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Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy
Research
Next Generation Exon Skipping Therapies Developed for the Treatment of Duchenne Muscular Dystrophy
Research
Insmed’s Gene Therapy (INS1201) Poised to Challenge Duchenne Muscular Dystrophy (DMD)
Approved Treatments
NICE Final Guidance for AGAMREE (Vamorolone) as a Treatment for Duchenne Muscular Dystrophy Is Positive for Santhera
Research
Dr. Liubov Gushchina’s Exon 17 Skipping Study Rewarded with Grant
Research
ImmunoForge Receives FDA IND Approval for Phase 2 Clinical Trial of ‘Pemziviptadil’ for DMD Cardiomyopathy
Press Releases
Sarepta Reiterated Total Net Product Revenue of $3.0 Billion in 2025
Press Releases
Wave Life Sciences Announces Plans for Exon 53 Skipping Study in 2025
Press Releases
Edgewise Therapeutics Announces Plans for 2025
DMD
Nutrition Guideline for Duchenne Muscular Dystrophy: Foods to Eat and Avoid
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Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
Must Read
Press Releases
Roche to Share Ongoing Work on Elevidys Gene Therapy at Muscular Dystrophy Association (MDA) 2025 Conference
Press Releases
Dyne Therapeutics Announces Unprecedented and Sustained Functional Improvement Through 18 Months from Phase 1/2 DELIVER Trial of DYNE-251 in Duchenne Muscular Dystrophy
Research
Researchers in Madrid Make Important Strides in the Cure of Duchenne Muscular Dystrophy with Nanoparticles