What is Deramiocel? What Does CAP-1002 Do?
Capricor Therapeutics, a biotechnology company developing transformative cell and exosome-based therapeutics for the treatment of rare diseases, today announced the completion of the submission...
Is Duchenne Gene Therapy a Suitable Treatment Despite its Immunogenic Class Effect?
Progressive muscle weakness and eventual mortality as a result of cardiomyopathy or respiratory complications are the hallmarks of Duchenne muscular dystrophy (DMD), a severe...
New Research on Duchenne Muscular Dystrophy Protein Interactions Lead to More Targeted Therapies
A pioneering discovery has shown the complicated relationships between dystrophin, a muscle stability protein, and its companion protein, dystrobrevin, opening new avenues for studying...
Zebrafish Modeling Shows Promise in Duchenne (DMD) Research
Zebrafish (Danio rerio) has emerged as a valuable model organism for investigating musculoskeletal development and the pathophysiology of associated diseases. Key genes and biological...
University of Miami Health System and Holtz Children’s Hospital Physicians Evaluated the Effectiveness of ELEVIDYS
University of Miami Health System and Holtz Children’s Hospital physicians are playing a major role in getting ELEVIDYS access.
The therapy delivers a functional micro-gene...