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PBGENE-DMD
PBGENE-DMD
Press Releases
The FDA Designates PBGENE-DMD as an Orphan Drug by Precision BioSciences to Treat Duchenne Muscular Dystrophy
Press Releases
Precision BioSciences Highlights New Preclinical Data for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy
Press Releases
Precision BioSciences Receives FDA Rare Pediatric Disease Designation for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy
Press Releases
Precision BioSciences PBGENE-DMD Restores Production of Nearly Full-Length Dystrophin Protein
Press Releases
Precision BioSciences Presents Preclinical Efficacy and Durability Data on PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy (DMD) at the 2025 Muscular Dystrophy Association...
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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
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Press Releases
Cumberland’s Ifetroban Demonstrated a 5.4% Improvement Compared to Placebo-Treated Patients
Approved Treatments
What is Duvyzat (Givinostat)?
Press Releases
Capricor Therapeutics Announces Positive 4-Year Data of Deramiocel (CAP-1002) in Duchenne Muscular Dystrophy