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Gene Therapy

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Givinostat EMA Approval: When Will Givinostat (Duvyzat) Be Approved in Europe?

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Givinostat has already received regulatory approval in the US...

Satellos SAT-3247 Stem Cell Approach May Restore Muscle Regeneration in Duchenne Muscular Dystrophy

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Genetic interventions such as exon skipping or gene therapy...

New Drug Submission for AGAMREE (vamorolone) Accepted for Priority Review by Health Canada for the Treatment of Duchenne Muscular Dystrophy

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Catalyst Pharmaceuticals has announced that Health Canada has accepted...

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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments 5
A genetic condition known as Duchenne muscular dystrophy (DMD)...

What is Duvyzat (Givinostat)?

Approved Treatments 1
For individuals with Duchenne muscular dystrophy (DMD), adults and...

In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?

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Elevidys is the only approved gene therapy in the...

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