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European Medicines Agency
European Medicines Agency
Approved Treatments
EMA Recommends EU Approval for Duvyzat (givinostat) to Treat Duchenne Muscular Dystrophy
Press Releases
Dyne Therapeutics Receives European Medicines Agency (EMA) Orphan Drug Designation for DYNE-251 in Duchenne Muscular Dystrophy
Editorials
Givinostat EMA Approval: Is Givinostat (Duvyzat) Approved by EMA?
Press Releases
Three Ongoing Clinical Trials of Elevidys Gene Therapy Temporarily Halted in Europe
Press Releases
European Clinical Trial Map Launched
Editorials
Call from Families to European Medicines Agency (EMA): Re-examine Ataluren (Translarna)
Editorials
Will Elevidys Receive Approval from the European Medicines Agency (EMA)?
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024
Must Read
Press Releases
Translarna (Ataluren) Rejected by EMA: Marketing Authorization Not Renewed
Editorials
DMD WarrioR’s Turkish Representative Shares His Views on Elevidys Gene Therapy: Is It Effective and Why Is It Expensive?
Research
Fn14 Protein May Protect Muscle Stem Cells, Offering Promise for Development of Duchenne Treatments