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European Medicines Agency
European Medicines Agency
Press Releases
MetrioPharm’s MP1032 Receives EMA Orphan Drug Designation in Duchenne Muscular Dystrophy
Press Releases
The European Medicines Agency (EMA) Issued a Negative Opinion on Elevidys
Approved Treatments
EMA Recommends EU Approval for Duvyzat (givinostat) to Treat Duchenne Muscular Dystrophy
Press Releases
Dyne Therapeutics Receives European Medicines Agency (EMA) Orphan Drug Designation for DYNE-251 in Duchenne Muscular Dystrophy
Editorials
Givinostat EMA Approval: Is Givinostat (Duvyzat) Approved by EMA?
Press Releases
Three Ongoing Clinical Trials of Elevidys Gene Therapy Temporarily Halted in Europe
Press Releases
European Clinical Trial Map Launched
Editorials
Call from Families to European Medicines Agency (EMA): Re-examine Ataluren (Translarna)
Editorials
Will Elevidys Receive Approval from the European Medicines Agency (EMA)?
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024
Must Read
Editorials
Accredited Duchenne Centers (ADC) Aims to Provide Uniform and Up-to-date Care for All People Living with Duchenne Muscular Dystrophy
Research
RGX-202 Gene Therapy Phase 3 Clinical Trial Begins
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies