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Dystrophin
Dystrophin
DMD
The Dystrophin Gene: Function, Disorders, and Therapeutic Advances
Research
Next Generation Lipid Nanoparticles (LNPs) for the Treatment of Duchenne
Research
The FDA Designates IPS HEART’s GIVI-MPC Stem Cell Therapy for Becker Muscular Dystrophy an Orphan Drug
Research
New Research on Duchenne Muscular Dystrophy Protein Interactions Lead to More Targeted Therapies
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024
Must Read
Editorials
Accredited Duchenne Centers (ADC) Aims to Provide Uniform and Up-to-date Care for All People Living with Duchenne Muscular Dystrophy
Research
RGX-202 Gene Therapy Phase 3 Clinical Trial Begins
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies