Home
Categories
DMD
Research
Press Releases
Approved Treatments
Editorials
Family Stories
Cures
WhatsApp Channel
About Us
Contact
Search
Home
Categories
DMD
Research
Press Releases
Approved Treatments
Editorials
Family Stories
Cures
WhatsApp Channel
About Us
Contact
More
Search
Research
Approved Treatments
DMD
Editorials
Family Stories
Press Releases
Research
Tevard Biosciences to Present Data Demonstrating tRNA-based Therapy Rescued Full-Length Dystrophin and Motor Function in Duchenne Muscular Dystrophy Model
Research
Satellos Prepares to Launch Phase 2 Clinical Study of SAT-3247 for the Treatment of Duchenne Muscular Dystrophy
Research
mRNA Studies in DMD Treatment: Future Therapeutic Candidates
Research
Miraculous Steroid Vamorolone (Agamree) Could Offer Safer Treatment for DMD
Cures of Duchenne (List of All Researches)
Research
DMD Warrior
-
September 20, 2024
Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene ReplacementGenethon (Sarepta)GNT-0004ClinicalMicro-dystrophin Gene ReplacementRegenxBioRGX-202ClinicalMicro-dystrophin Gene ReplacementSolid BiosciencesSGT-001ClinicalMicro-dystrophin Gene ReplacementSolid BiosciencesSGT-003ClinicalMicro-dystrophin Gene ReplacementBelief BioMedBBM-D101ClinicalMicro-dystrophin Gene ReplacementInsmedINS1201ClinicalMicro-dystrophin...
Load more
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024