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Sarepta
Sarepta
Press Releases
Russia-Based Circle of Kindness Foundation Announces 18% Price Cut for Elevidys Gene Therapy
Editorials
The Immune System May Be Decreasing the Effectiveness of Gene Therapy for Duchenne Muscular Dystrophy
Press Releases
Three Ongoing Clinical Trials of Elevidys Gene Therapy Temporarily Halted in Europe
Editorials
DMD WarrioR’s Turkish Representative Shares His Views on Elevidys Gene Therapy: Is It Effective and Why Is It Expensive?
DMD
What is Cytomegalovirus Infection (CMV)?
Press Releases
Sarepta, Reports 16 Years Old Boy Death After Elevidys Gene Therapy Treatment
Press Releases
Eteplirsen (Exondys 51) Treatment Significantly Slows Heart Function Decline in Duchenne Muscular Dystrophy
Editorials
Why Isn’t Roche Applying Marketing Authorization in Every Country for Elevidys Gene Therapy?
Editorials
Brazilian Children Over 7 and Their Families Demand Elevidys Gene Therapy from Anvisa
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Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
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Press Releases
Translarna (Ataluren) Rejected by EMA: Marketing Authorization Not Renewed
Editorials
DMD WarrioR’s Turkish Representative Shares His Views on Elevidys Gene Therapy: Is It Effective and Why Is It Expensive?
Research
Fn14 Protein May Protect Muscle Stem Cells, Offering Promise for Development of Duchenne Treatments