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Sarepta
Sarepta
Press Releases
High Anti-AAV Antibodies May No Longer Be a Barrier to Elevidys Administration
Press Releases
FDA: ‘Elevidys Gene Therapy Will Continue to Be Used in Ambulatory DMD Patients’
Press Releases
FDA Investigating Death of 8-Year-Old Brazilian Boy Who Received Elevidys
Editorials
Roche Suspends Shipments of Elevidys Gene Therapy Outside of the United States
Press Releases
Sarepta Therapeutics Announces Pause of ELEVIDYS Shipments in the USA
Press Releases
Sarepta to Lay Off About 500 Employees After Duchenne Gene Therapy Setbacks
Editorials
Vyondys 53: What Does FDA Rejection Letter Mean?
Press Releases
Sarepta Therapeutics Halts ELEVIDYS Shipments for Non-Ambulatory DMD Patients
Editorials
After Second Patient Death, Duchenne Muscular Dystrophy Communities Want Answers About Elevidys Gene Therapy
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Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
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Press Releases
Capricor Therapeutics Provides Regulatory Update on Deramiocel BLA for Duchenne Muscular Dystrophy
Press Releases
Cumberland’s Ifetroban Demonstrated a 5.4% Improvement Compared to Placebo-Treated Patients
Approved Treatments
What is Duvyzat (Givinostat)?