MHRA

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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

UK Approves Givinostat (Duvyzat) for Duchenne Muscular Dystrophy Treatment

Approved Treatments December 21, 2024 0

Givinostat conditionally approved to treat patients with Duchenne muscular...

Santhera Announces Approval in Hong Kong for AGAMREE® (Vamorolone) as a Treatment for Duchenne Muscular Dystrophy

Approved Treatments December 21, 2024 0

Santhera Pharmaceuticals announces that the Department of Health of...

Researchers Discover 18-Digit Code (Wnt7a) that Allows Proteins to Hitch a Ride Around the Body

Research December 12, 2024 0

Researchers from the University of Ottawa and The Ottawa...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

DMD October 13, 2024 0

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy

Research October 10, 2024 0

Capricor Therapeutics, a biotechnology company developing transformative cell and...

Cure of Duchenne (Research Overview)

Research September 20, 2024 0

Dystrophin Gene Therapy Mechanism Company Drug Status Micro-dystrophin Gene Replacement Sarepta Therapeutics Elevidys/SRP-9001 Approved Micro-dystrophin Gene Replacement Pfizer PF-06939926 Discontinued Micro-dystrophin Gene...

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