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Full-Length Dystrophin
Full-Length Dystrophin
Press Releases
Precision BioSciences Presents Preclinical Efficacy and Durability Data on PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy (DMD) at the 2025 Muscular Dystrophy Association...
Press Releases
SonoThera will Present New Data of Genetic Medicine Using Targeted, Ultrasound-Mediated Delivery (UMD) in Treating Duchenne Muscular Dystrophy
Research
What is Bobcat mRNA? How Does Bobcat mRNA Work for Duchenne Muscular Dystrophy?
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Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
Must Read
Editorials
After Second Patient Death, Duchenne Muscular Dystrophy Communities Want Answers About Elevidys Gene Therapy
Press Releases
Capricor Therapeutics Announces BMD Orphan Drug Designation and DMD Program Regulatory Development for Deramiocel (CAP-1002)
Press Releases
Sarepta Reported Elevidys Gene Therapy for Duchenne Muscular Dystrophy will not be used in non-ambulatory patients
ELEVIDYS