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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

How Does My Child Participate in Clinical Trials for Duchenne?

DMD September 6, 2025 0

If your child has been diagnosed with Duchenne muscular...

SQY Therapeutics Receives Orphan Drug Designation from the European Medicines Agency for Exon 51 Skipping Therapy SQY51 for Treatment of Duchenne Muscular Dystrophy

Press Releases September 4, 2025 0

SQY51 had already obtained Orphan Drug Designation from the...

Support World Duchenne Awareness Day 2025 with DMDWarrior

Editorials August 30, 2025 1

World Duchenne Awareness Day will be observed globally on...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments December 26, 2024 5

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research January 5, 2025 7

The results of new gene therapy studies for Duchenne...

Duchenne Muscular Dystrophy: Treatment & Cost

Editorials January 2, 2025 1

The excitement you feel until your child is born...

France

Must Read

JCR Pharmaceuticals Proprietary JUST-AAV Capsids May be Used in the Development of Duchenne Cures

Taiho Pharmaceutical Announced TAS-205 Phase 3 Clinical Study Did Not Meet Its Primary Endpoint

Accredited Duchenne Centers (ADC) Aims to Provide Uniform and Up-to-date Care for All People Living with Duchenne Muscular Dystrophy