Exon Skipping Therapies News, Researches and Articles

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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

UW Medicine Announces New Gene Therapy Research for Duchenne Muscular Dystrophy

Research July 18, 2025 0

For those who suffer from Duchenne muscular dystrophy (DMD),...

INS1201 Gene Therapy Phase 1 Clinical Trial Begins

Research July 17, 2025 0

Insmed was announced on the page published on ClinicalTrials.gov...

Sarepta to Lay Off About 500 Employees After Duchenne Gene Therapy Setbacks

Press Releases July 17, 2025 0

Sarepta stated that company intends to halt development on...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments December 26, 2024 5

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research January 5, 2025 5

The results of new gene therapy studies for Duchenne...

Duchenne Muscular Dystrophy: Treatment & Cost

Editorials January 2, 2025 1

The excitement you feel until your child is born...

Exon Skipping Therapies

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