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Exon Skipping Therapies
Exon Skipping Therapies
DMD
Mutations and Deletions Amenable to Exon 44 Skipping Therapies for Duchenne Muscular Dystrophy
DMD
Mutations Amenable to Exon 50 Skipping Therapies in Duchenne Muscular Dystrophy
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies
Research
Upcoming Exon 51 Skipping Therapies for the Treatment of Duchenne Muscular Dystrophy
DMD
Which Mutations are Amenable to Exon 45 Skipping?
Press Releases
Eteplirsen (Exondys 51) Treatment Significantly Slows Heart Function Decline in Duchenne Muscular Dystrophy
Research
Next Generation Exon Skipping Therapies Developed for the Treatment of Duchenne Muscular Dystrophy
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024
Must Read
Editorials
Accredited Duchenne Centers (ADC) Aims to Provide Uniform and Up-to-date Care for All People Living with Duchenne Muscular Dystrophy
Research
RGX-202 Gene Therapy Phase 3 Clinical Trial Begins
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies