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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

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Frequently Asked Questions About Solid Biosciences SGT-003 Gene Therapy

Editorials 0
Many research companies around the world are researching treatments...

Stitch RNA: New Method for Duchenne Gene Therapies

Research 0
The Stitch RNA (StitchR) method could accelerate the development...

Solid Biosciences Plans to Request a Meeting with the FDA in mid-2025 to Discuss Potential Accelerated Approval Pathways for SGT-003

Press Releases 0
Solid Biosciences, a life sciences company developing precision, next...

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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments 5
A genetic condition known as Duchenne muscular dystrophy (DMD)...

Cures of Duchenne (List of All Researches)

Research 12
Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene...

Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy

Research 0
Capricor Therapeutics, a biotechnology company developing transformative cell and...

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