We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

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UW Medicine Announces New Gene Therapy Research for Duchenne Muscular Dystrophy

Research July 18, 2025 0

For those who suffer from Duchenne muscular dystrophy (DMD),...

INS1201 Gene Therapy Phase 1 Clinical Trial Begins

Research July 17, 2025 0

Insmed was announced on the page published on ClinicalTrials.gov...

Sarepta to Lay Off About 500 Employees After Duchenne Gene Therapy Setbacks

Press Releases July 17, 2025 0

Sarepta stated that company intends to halt development on...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments December 26, 2024 5

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research January 5, 2025 5

The results of new gene therapy studies for Duchenne...

Duchenne Muscular Dystrophy: Treatment & Cost

Editorials January 2, 2025 1

The excitement you feel until your child is born...

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