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Research
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Approved Treatments
Editorials
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Duchenne
Duchenne
Press Releases
Plans for DYNE-101 in DM1 and DYNE-251 in DMD Are Announced by Dyne Therapeutics
Press Releases
Percheron Disappointed in Avicursen (ATL1102) Study For Duchenne (DMD)
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024
Must Read
Editorials
Accredited Duchenne Centers (ADC) Aims to Provide Uniform and Up-to-date Care for All People Living with Duchenne Muscular Dystrophy
Research
RGX-202 Gene Therapy Phase 3 Clinical Trial Begins
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies