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Delpacibart Zotadirsen

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FDA Designates Avidity Biosciences’ Delpacibart Zotadirsen (del-zota) as a Breakthrough Therapy for the Treatment of DMD in Individuals with Mutations That Allow for Exon...

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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

DMD Warrior - December 26, 2024

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Entrada Therapeutics Receives EU Authorization to Start Exon 45 Skipping Clinical Trial in Duchenne Muscular Dystrophy

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Entos Pharmaceuticals Develops Re-Dosable, Full-Length Dystrophin Gene Therapy: Fusogenix PLV Method

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Genethon Reports Results of GNT0004 Gene Therapy Clinical Trial: Permanent Decrease in CK Levels of More Than 75%

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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

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The European Medicines Agency (EMA) Issued a Negative Opinion on Elevidys

Press Releases July 25, 2025 0

Roche announced today that the Committee for Medicinal Products...

Brazil Suspends Use of ELEVIDYS (delandistrogene moxeparvovec)

Press Releases July 25, 2025 0

The Brazilian Health Regulatory Agency (Anvisa) announced that it...

Mutations and Deletions Amenable to Exon 44 Skipping Therapies for Duchenne Muscular Dystrophy

DMD July 24, 2025 0

Exon 44 skipping has emerged as a targeted treatment...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments December 26, 2024 5

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research January 5, 2025 5

The results of new gene therapy studies for Duchenne...

Duchenne Muscular Dystrophy: Treatment & Cost

Editorials January 2, 2025 1

The excitement you feel until your child is born...

Delpacibart Zotadirsen

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