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Avidity Biosciences
Avidity Biosciences
Press Releases
FDA Designates Avidity Biosciences’ Delpacibart Zotadirsen (del-zota) as a Breakthrough Therapy for the Treatment of DMD in Individuals with Mutations That Allow for Exon...
Editorials
Del-zota (EXPLORE44) Provides Nearly 30% Normal Dystrophin Production in Patients Amenable to Exon 44 Skipping
Press Releases
Avidity Biosciences Announces Positive Topline Del-zota Data Showing Consistent, Statistically Significant Improvements in Dystrophin
Research
5 DMD Researches You Should Follow up in 2025
Press Releases
Avidity Biosciences Prepares for Three Rare Muscle Disease Programs’ 2025 BLA Submission and Commercialization
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
Must Read
Editorials
Accredited Duchenne Centers (ADC) Aims to Provide Uniform and Up-to-date Care for All People Living with Duchenne Muscular Dystrophy
Research
RGX-202 Gene Therapy Phase 3 Clinical Trial Begins
Research
Entrada Therapeutics Begins Clinical Trials in Europe for Exon 44 and Exon 45 Skipping Therapies