Nippon Shinyaku Releases First Clinical Trial (First in Human) of Brogidirsen NS-089/NCNP-02 for the Treatment of Duchenne
The National Center of Neurology and Psychiatry is announced the publication of a research paper in Cell Reports Medicine detailing the results of an...
What is Ataluren (Translarna)? What is Ataluren Used For?
Ataluren (Translarna) is an investigational drug used to delay disease progression in outpatients with Duchenne muscular dystrophy (DMD), a progressive and fatal neuromuscular disease....
Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy
The results of new gene therapy studies for Duchenne muscular dystrophy disease will be watched by curious eyes in 2025. The trial phases of...
What is Deramiocel? What Does CAP-1002 Do?
Capricor Therapeutics, a biotechnology company developing transformative cell and exosome-based therapeutics for the treatment of rare diseases, today announced the completion of the submission...
Is Duchenne Gene Therapy a Suitable Treatment Despite its Immunogenic Class Effect?
Progressive muscle weakness and eventual mortality as a result of cardiomyopathy or respiratory complications are the hallmarks of Duchenne muscular dystrophy (DMD), a severe...