Toshifumi Yokota News, Researches and Articles

About us

We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

Hydrogel Delivery System Holds Potential for Cell-Based Therapy of Duchenne Muscular Dystrophy

Research March 12, 2025 0

In a mouse model of muscular dystrophy, researchers in...

OligomicsTx Gene Therapy Study Shows Promise in Treating Duchenne Muscular Dystrophy

Research March 11, 2025 0

The University of Alberta researchers develop a molecule that...

SonoThera will Present New Data of Genetic Medicine Using Targeted, Ultrasound-Mediated Delivery (UMD) in Treating Duchenne Muscular Dystrophy

Press Releases March 10, 2025 0

SonoThera will present new data at the 2025 MDA...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments December 26, 2024 5

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Cures of Duchenne (List of All Researches)

Research September 20, 2024 12

Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene...

Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy

Research October 10, 2024 0

Capricor Therapeutics, a biotechnology company developing transformative cell and...

Toshifumi Yokota

Must Read

A Novel “Mini-CRISPR” Could Be More Successful at Editing the Dystrophin Gene

Everything You Should Know About Genethon’s Gene Therapy GNT0004 for Duchenne Muscular Dystrophy

Sidra Medicine Establishes Gene Therapy Center for Rare Genetic Diseases in Qatar