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Sarepta
Sarepta
Research
Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy
Editorials
In Which Countries Is Elevidys Approved? Is Elevidys Approved In Europe?
Editorials
First Girl in the World to Receive Elevidys Gene Therapy: Raniya Scott
Approved Treatments
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
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December 26, 2024
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Press Releases
Capricor Therapeutics Provides Regulatory Update on Deramiocel BLA for Duchenne Muscular Dystrophy
Press Releases
Cumberland’s Ifetroban Demonstrated a 5.4% Improvement Compared to Placebo-Treated Patients
Approved Treatments
What is Duvyzat (Givinostat)?