Qatar News, Researches and Articles

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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

Keros Announces U.S. FDA Orphan Drug Designation Granted to KER-065 for the Treatment of Duchenne Muscular Dystrophy

Press Releases August 20, 2025 0

Keros Therapeutics today announced the U.S. Food and Drug...

ITF Therapeutics Launching A Study to Evaluate the Real-World Experience of Duvyzat (Givinostat) in Patients With Duchenne Muscular Dystrophy

Research August 19, 2025 0

The purpose of this prospective observational study (NCT07127978) is...

Agamree to be sold in United Arab Emirates, Saudi Arabia, Kuwait, Oman and Bahrain starting in 2026

Press Releases August 19, 2025 0

Santhera Pharmaceuticals announces the signing of an exclusive agreement...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments December 26, 2024 5

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research January 5, 2025 7

The results of new gene therapy studies for Duchenne...

Duchenne Muscular Dystrophy: Treatment & Cost

Editorials January 2, 2025 1

The excitement you feel until your child is born...

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Must Read

Wellcome Trust Donates £10 Million to Treat Rare Diseases

Edgewise Therapeutics Reports Positive Results on Sevasemten Program for Becker and Duchenne Muscular Dystrophies

Precision BioSciences Receives FDA Rare Pediatric Disease Designation for PBGENE-DMD for the Treatment of Duchenne Muscular Dystrophy