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Microdystrophin

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mRNA Studies in DMD Treatment: Future Therapeutic Candidates

Research 0
Given that FDA-approved exon skipping therapies and gene therapy...

Genethon CEO Frederic Revah Announces GNT0004 Gene Therapy Will Provide Amazing Results for DMD (Duchenne Muscular Dystrophy)

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The Chief Executive Officer of Genethon, Frederic Revah, made...

Miraculous Steroid Vamorolone (Agamree) Could Offer Safer Treatment for DMD

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A novel steroid medication that is used to treat...

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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments 5
A genetic condition known as Duchenne muscular dystrophy (DMD)...

What is Duvyzat (Givinostat)?

Approved Treatments 1
For individuals with Duchenne muscular dystrophy (DMD), adults and...

Cures of Duchenne (List of All Researches)

Research 14
Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene...

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