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Research

Shanghai Jiao Tong University School of Medicine Begins Clinical Trials of LE051 Exon 51 Skipping Therapy

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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

DMD Warrior - December 26, 2024

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Wave Life Sciences Announces Positive Data from FORWARD-53 Clinical Trial in DMD Including Significant Functional Benefit and Reversal of Muscle Damage after 48 Weeks...

Editorials

Chilean Health Ministry Says No Clinical Evidence of Improvement for Elevidys Gene Therapy

DMD

Which Mutations are Amenable to Exon 45 Skipping?

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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

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Precision BioSciences PBGENE-DMD Restores Production of Nearly Full-Length Dystrophin Protein

Press Releases May 15, 2025 0

Precision BioSciences, today announced the strategic prioritization and acceleration...

Satellos Reports SAT-3247 Q1 2025 Results, Highlights Recent Company Progress and Future Plans

Press Releases May 14, 2025 0

Satellos Bioscience, today announced its financial results and corporate...

Sarepta Therapeutics Announces Approval in Japan of ELEVIDYS, a Gene Therapy to Treat Duchenne Muscular Dystrophy

Press Releases May 13, 2025 1

People aged 3 to under 8 who do not...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments December 26, 2024 5

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research January 5, 2025 3

The results of new gene therapy studies for Duchenne...

What is Duvyzat (Givinostat)?

Approved Treatments October 13, 2024 1

For individuals with Duchenne muscular dystrophy (DMD), adults and...

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