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LE051
LE051
Research
Shanghai Jiao Tong University School of Medicine Begins Clinical Trials of LE051 Exon 51 Skipping Therapy
Popular
Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy
DMD Warrior
-
December 26, 2024
Must Read
Press Releases
SonoThera will Present New Data of Genetic Medicine Using Targeted, Ultrasound-Mediated Delivery (UMD) in Treating Duchenne Muscular Dystrophy
DMD
What Duchenne Muscular Dystrophy (DMD) Patients Who Need to Have Surgery Under Anesthesia Should Know
Editorials
Frequently Asked Questions About Solid Biosciences SGT-003 Gene Therapy