Germany News, Researches and Articles

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We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

New Positive Functional Data From The RGX-202 Affinity Duchenne® Trial Phase 1/2 Reported By Regenxbio

Regenxbio RGX-202 Press Releases June 6, 2025 0

The Regenxbio press statement stated that the findings, which...

PepGen Announces It Will Halt Clinical Trials of Exon 51 Skipping Study

Press Releases May 29, 2025 0

PepGen, a clinical-stage biotechnology company advancing the next generation...

Entrada Therapeutics Receives EU Authorization to Start Exon 45 Skipping Clinical Trial in Duchenne Muscular Dystrophy

Press Releases May 28, 2025 0

Entrada Therapeutics, today announced it has received authorization from...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments December 26, 2024 5

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research January 5, 2025 3

The results of new gene therapy studies for Duchenne...

Duchenne Muscular Dystrophy: Treatment & Cost

Editorials January 2, 2025 1

The excitement you feel until your child is born...

Germany

Must Read

Shanghai Jiao Tong University School of Medicine Begins Clinical Trials of LE051 Exon 51 Skipping Therapy

Translarna (Ataluren) Rejected by EMA: Marketing Authorization Not Renewed

DMD WarrioR’s Turkish Representative Shares His Views on Elevidys Gene Therapy: Is It Effective and Why Is It Expensive?