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Exon 50 Skipping Treatment

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Dyne Therapeutics Receives European Medicines Agency (EMA) Orphan Drug Designation for DYNE-251 in Duchenne Muscular Dystrophy

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Today, Dyne Therapeutics, a clinical-stage company dedicated to developing...

Agamree (vamorolone) will be Covered in Slovenia by the Slovenian Health Insurance Fund

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The Slovenian Health Insurance Institute (ZZZS) today added Agamree...

Russia-Based Circle of Kindness Foundation Announces 18% Price Cut for Elevidys Gene Therapy

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According to the Foundation's press office, "as a result...

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Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments 5
A genetic condition known as Duchenne muscular dystrophy (DMD)...

What is Duvyzat (Givinostat)?

Approved Treatments 1
For individuals with Duchenne muscular dystrophy (DMD), adults and...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research 2
The results of new gene therapy studies for Duchenne...

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