HomeTagsExon 50 Skipping

Exon 50 Skipping

Popular

Must Read

About us

We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

Dyne Therapeutics Receives European Medicines Agency (EMA) Orphan Drug Designation for DYNE-251 in Duchenne Muscular Dystrophy

Press Releases 0
Today, Dyne Therapeutics, a clinical-stage company dedicated to developing...

Agamree (vamorolone) will be Covered in Slovenia by the Slovenian Health Insurance Fund

Press Releases 0
The Slovenian Health Insurance Institute (ZZZS) today added Agamree...

Russia-Based Circle of Kindness Foundation Announces 18% Price Cut for Elevidys Gene Therapy

Press Releases 0
According to the Foundation's press office, "as a result...

Most Popular

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments 5
A genetic condition known as Duchenne muscular dystrophy (DMD)...

What is Duvyzat (Givinostat)?

Approved Treatments 1
For individuals with Duchenne muscular dystrophy (DMD), adults and...

Potential Upcoming New Gene Therapies for Duchenne Muscular Dystrophy

Research 2
The results of new gene therapy studies for Duchenne...

© 2024 - 2025 DMD Warrior. All rights reserved.