HomeTagsExon 50

Exon 50

spot_imgspot_img

Categories

Must Read

About us

We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

Frequently Asked Questions About Solid Biosciences SGT-003 Gene Therapy

Editorials 0
Many research companies around the world are researching treatments...

Stitch RNA: New Method for Duchenne Gene Therapies

Research 0
The Stitch RNA (StitchR) method could accelerate the development...

Solid Biosciences Plans to Request a Meeting with the FDA in mid-2025 to Discuss Potential Accelerated Approval Pathways for SGT-003

Press Releases 0
Solid Biosciences, a life sciences company developing precision, next...

Most Popular

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

Approved Treatments 5
A genetic condition known as Duchenne muscular dystrophy (DMD)...

Cures of Duchenne (List of All Researches)

Research 12
Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene...

Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy

Research 0
Capricor Therapeutics, a biotechnology company developing transformative cell and...

© 2024 - 2025 DMD Warrior. All rights reserved.