Ataluren

About us

We do not want children to die from a disease that can be cured. We want to give hope to families and ensure that all children with DMD are treated and regain their health.

Latest Articles

Nippon Shinyaku Releases First Clinical Trial (First in Human) of Brogidirsen NS-089/NCNP-02 for the Treatment of Duchenne

Research January 10, 2025 0

The National Center of Neurology and Psychiatry is announced...

What is Ataluren (Translarna)? What is Ataluren Used For?

Research January 9, 2025 0

Ataluren (Translarna) is an investigational drug used to delay...

Avidity Biosciences Prepares for Three Rare Muscle Disease Programs’ 2025 BLA Submission and Commercialization

DMD January 8, 2025 0

A biopharmaceutical firm dedicated to developing a novel class...

Frequently Asked Questions About Elevidys Used for Duchenne Muscular Dystrophy

DMD December 26, 2024 1

A genetic condition known as Duchenne muscular dystrophy (DMD)...

Capricor Therapeutics Submits Application for Treatment of DMD Cardiomyopathy

Research October 10, 2024 0

Capricor Therapeutics, a biotechnology company developing transformative cell and...

Cures of Duchenne (List of All Researches)

Research September 20, 2024 2

Dystrophin Gene Therapy MechanismCompanyDrugStatus Micro-dystrophin Gene Replacement Sarepta TherapeuticsElevidys/SRP-9001ApprovedMicro-dystrophin Gene ReplacementPfizerPF-06939926DiscontinuedMicro-dystrophin Gene...

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Must Read

CRISPR-Cas13 Could Accelerate Studies on RNA-Targeted Therapies

New Gene Therapy Study at Indiana University Offers Hope for Duchenne Muscular Dystrophy

The Story of Aziz, DMD Warrior from Turkey