{"id":8726,"date":"2026-09-09T14:19:54","date_gmt":"2026-09-09T11:19:54","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8726"},"modified":"2026-09-09T14:19:57","modified_gmt":"2026-09-09T11:19:57","slug":"sat-3247-renamed-forazapadin-dmd","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/sat-3247-renamed-forazapadin-dmd\/","title":{"rendered":"\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u836f\u7269 Satellos&#039; \u548c SAT-3247 \u83b7\u5f97\u4e16\u754c\u536b\u751f\u7ec4\u7ec7\u6b63\u5f0f\u540d\u79f0\uff1a\u798f\u62c9\u624e\u5e15\u5b9a"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>Satellos Bioscience \u5ba3\u5e03\uff0c\u5176\u5728\u7814\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u6cbb\u7597\u836f\u7269 SAT-3247 \u5df2\u6b63\u5f0f\u83b7\u5f97\u4e16\u754c\u536b\u751f\u7ec4\u7ec7 (WHO) \u9881\u53d1\u7684\u56fd\u9645\u975e\u4e13\u5229\u540d\u79f0 (INN) Forazapadin\u3002.<\/strong> \u547d\u540d\u8fd9\u4e00\u91cc\u7a0b\u7891\u662f\u8be5\u836f\u7269\u5168\u7403\u4e34\u5e8a\u5f00\u53d1\u548c\u672a\u6765\u76d1\u7ba1\u8def\u5f84\u4e2d\u7684\u91cd\u8981\u4e00\u6b65\u3002.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u76ee\u5f55<\/h2><nav><ul><li><a href=\"#what-is-forazapadin\">\u4ec0\u4e48\u662f\u798f\u62c9\u624e\u5e15\u5b9a\uff1f<\/a><\/li><li><a href=\"#why-the-who-name-matters\">\u4e3a\u4ec0\u4e48\u4e16\u536b\u7ec4\u7ec7\u7684\u540d\u79f0\u5f88\u91cd\u8981<\/a><\/li><li><a href=\"#phase-2-clinical-trials-continue\">\u4e8c\u671f\u4e34\u5e8a\u8bd5\u9a8c\u7ee7\u7eed\u8fdb\u884c<\/a><\/li><li><a href=\"#why-this-could-be-important-for-the-dmd-community\">\u4e3a\u4ec0\u4e48\u8fd9\u5bf9DMD\u793e\u7fa4\u6765\u8bf4\u53ef\u80fd\u5f88\u91cd\u8981<\/a><\/li><li><a href=\"#dmd-warriors-take\">DMDWarrior\u7684\u89c2\u70b9<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 id=\"what-is-forazapadin\" class=\"wp-block-heading\">\u4ec0\u4e48\u662f\u798f\u62c9\u624e\u5e15\u5b9a\uff1f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Forazapadin \u662f\u4e00\u79cd\u53e3\u670d\u5c0f\u5206\u5b50\u836f\u7269\uff0c\u76ee\u524d\u6b63\u5728\u7814\u53d1\u4e2d\uff0c\u65e8\u5728\u6539\u5584\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u808c\u8089\u518d\u751f\u3002.<\/strong> \u4e0e\u57fa\u56e0\u7597\u6cd5\u6216\u5916\u663e\u5b50\u8df3\u8dc3\u7597\u6cd5\u4e0d\u540c\uff0c\u798f\u62c9\u624e\u5e15\u4e01\u901a\u8fc7\u4e00\u79cd\u4e0d\u4f9d\u8d56\u4e8e\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u7684\u673a\u5236\u53d1\u6325\u4f5c\u7528\uff0c\u8fd9\u610f\u5473\u7740\u65e0\u8bba\u60a3\u8005\u7684\u5916\u663e\u5b50\u7a81\u53d8\u6216\u57fa\u56e0\u4e9a\u578b\u5982\u4f55\uff0c\u5b83\u90fd\u53ef\u4ee5\u4f7f\u7528\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u836f\u7269\u9776\u5411\u4e00\u79cd\u540d\u4e3aAAK1\u7684\u86cb\u767d\u8d28\uff0c\u8fd9\u79cd\u86cb\u767d\u8d28\u5728\u4eba\u4f53\u81ea\u7136\u7684\u808c\u8089\u4fee\u590d\u8fc7\u7a0b\u4e2d\u53d1\u6325\u4f5c\u7528\u3002Satellos\u516c\u53f8\u8ba4\u4e3a\uff0c\u963b\u65adAAK1\u53ef\u80fd\u6709\u52a9\u4e8e\u6062\u590d\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u53d7\u635f\u7684\u808c\u8089\u518d\u751f\u80fd\u529b\u3002.<\/p>\n\n\n\n<h2 id=\"why-the-who-name-matters\" class=\"wp-block-heading\">\u4e3a\u4ec0\u4e48\u4e16\u536b\u7ec4\u7ec7\u7684\u540d\u79f0\u5f88\u91cd\u8981<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u56fd\u9645\u975e\u4e13\u5229\u540d\u79f0 (INN) \u662f\u901a\u8fc7\u4e16\u754c\u536b\u751f\u7ec4\u7ec7 (WHO) \u547d\u540d\u6d41\u7a0b\u5206\u914d\u7684\u5b98\u65b9\u901a\u7528\u540d\u79f0\u3002\u83b7\u5f97 INN \u8868\u660e\u4e00\u79cd\u7597\u6cd5\u5df2\u8fdb\u5165\u66f4\u9ad8\u7ea7\u7684\u7814\u53d1\u9636\u6bb5\uff0c\u5e76\u63d0\u4f9b\u4e86\u4e00\u4e2a\u5168\u7403\u8ba4\u53ef\u7684\u540d\u79f0\uff0c\u8be5\u540d\u79f0\u53ef\u5728\u79d1\u5b66\u51fa\u7248\u7269\u3001\u4e34\u5e8a\u8bd5\u9a8c\u3001\u76d1\u7ba1\u7533\u62a5\u548c\u672a\u6765\u7684\u5546\u4e1a\u5316\u8fc7\u7a0b\u4e2d\u4e00\u81f4\u4f7f\u7528\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Satellos \u8868\u793a\uff0c\u4eca\u540e\u5c06\u5728\u5176\u79d1\u5b66\u548c\u76d1\u7ba1\u6c9f\u901a\u4e2d\u9010\u6b65\u7528 Forazapadin \u53d6\u4ee3 SAT-3247 \u8fd9\u4e2a\u540d\u79f0\u3002.<\/p>\n\n\n\n<h2 id=\"phase-2-clinical-trials-continue\" class=\"wp-block-heading\">\u4e8c\u671f\u4e34\u5e8a\u8bd5\u9a8c\u7ee7\u7eed\u8fdb\u884c<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u76ee\u524d\uff0cForazapadin \u6b63\u5728\u4e24\u9879\u9488\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684 II \u671f\u4e34\u5e8a\u7814\u7a76\u4e2d\u8fdb\u884c\u8bc4\u4f30\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u5927\u672c\u8425<\/strong> \u2014 \u4e00\u9879\u9488\u5bf9\u60a3\u6709 DMD \u7684\u513f\u7ae5\u7684\u968f\u673a\u3001\u5b89\u6170\u5242\u5bf9\u7167\u7684\u5168\u7403\u7814\u7a76\u3002.<\/li>\n\n\n\n<li><strong>\u6b65\u9053\u8d77\u70b9<\/strong> \u2014 \u4e00\u9879\u9488\u5bf9\u60a3\u6709 DMD \u7684\u6210\u5e74\u4eba\u7684\u5f00\u653e\u6807\u7b7e 2 \u671f\u7814\u7a76\u3002.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u636e Satellos \u79f0\uff0cBASECAMP \u8bd5\u9a8c\u7684\u53d7\u8bd5\u8005\u62db\u52df\u9884\u8ba1\u5c06\u5728\u672c\u5b63\u5ea6\u5b8c\u6210\uff0c\u800c\u8be5\u7814\u7a76\u7684\u9996\u6279\u4e34\u5e8a\u6570\u636e\u9884\u8ba1\u5c06\u4e8e 2026 \u5e74\u7b2c\u56db\u5b63\u5ea6\u516c\u5e03\u3002\u4e86\u89e3\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/clinical-trials\/\" target=\"_blank\" rel=\"noopener\">\u63a2\u7d22\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u516c\u53f8\u8fd8\u8ba1\u5212\u5728 2026 \u5e74\u5e95\u524d\u542f\u52a8 Forazapadin \u6cbb\u7597\u9762\u80a9\u80b1\u578b\u808c\u8425\u517b\u4e0d\u826f\u75c7 (FSHD) \u7684 2 \u671f\u4e34\u5e8a\u8bd5\u9a8c\u3002.<\/p>\n\n\n\n<h2 id=\"why-this-could-be-important-for-the-dmd-community\" class=\"wp-block-heading\">\u4e3a\u4ec0\u4e48\u8fd9\u5bf9DMD\u793e\u7fa4\u6765\u8bf4\u53ef\u80fd\u5f88\u91cd\u8981<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u76ee\u524d\u5927\u591a\u6570\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u7597\u6cd5\u90fd\u9488\u5bf9\u7279\u5b9a\u7684\u57fa\u56e0\u7a81\u53d8\u6216\u7740\u91cd\u4e8e\u6062\u590d\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u3002\u800c\u798f\u62c9\u624e\u5e15\u4e01\u7684\u7814\u53d1\u76ee\u6807\u5219\u6709\u6240\u4e0d\u540c\uff1a\u5b83\u65e8\u5728\u652f\u6301\u4eba\u4f53\u81ea\u8eab\u518d\u751f\u9aa8\u9abc\u808c\u7684\u80fd\u529b\uff0c\u800c\u65e0\u9700\u4f9d\u8d56\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u7684\u4ea7\u751f\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u5982\u679c\u4e34\u5e8a\u8bd5\u9a8c\u6210\u529f\uff0c\u8fd9\u79cd\u65b9\u6cd5\u6709\u53ef\u80fd\u5f97\u5230\u5e94\u7528\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u6db5\u76d6\u4e0d\u540c\u7c7b\u578b\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7a81\u53d8\u3002.<\/li>\n\n\n\n<li>\u4e0e\u5176\u4ed6\u5df2\u83b7\u6279\u51c6\u7684DMD\u7597\u6cd5\u4e00\u8d77\u3002.<\/li>\n\n\n\n<li>\u4f5c\u4e3a\u4e00\u79cd\u65e8\u5728\u7ef4\u62a4\u808c\u8089\u5065\u5eb7\u7684\u72ec\u7acb\u6cbb\u7597\u65b9\u6cd5\u3002.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u7136\u800c\uff0c\u503c\u5f97\u6ce8\u610f\u7684\u662f\uff0c\u798f\u62c9\u624e\u5e15\u5b9a\u4ecd\u662f\u4e00\u79cd\u7814\u7a76\u6027\u836f\u7269\u3002\u5176\u5b89\u5168\u6027\u548c\u6709\u6548\u6027\u4ecd\u5728\u8fdb\u884c\u4e2d\u7684\u4e34\u5e8a\u8bd5\u9a8c\u4e2d\u8bc4\u4f30\uff0c\u5c1a\u672a\u83b7\u5f97\u76d1\u7ba1\u90e8\u95e8\u6279\u51c6\u7528\u4e8e\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u3002.<\/p>\n\n\n\n<h2 id=\"dmd-warriors-take\" class=\"wp-block-heading\">DMDWarrior\u7684\u89c2\u70b9<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Forazapadin \u7684\u547d\u540d\u5e76\u975e\u83b7\u5f97\u6279\u51c6\uff0c\u4f46\u5b83\u662f\u4e00\u4e2a\u610f\u4e49\u91cd\u5927\u7684\u91cc\u7a0b\u7891\uff0c\u4f53\u73b0\u4e86 Satellos&#039; \u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7814\u53d1\u9879\u76ee\u7684\u6210\u719f\u3002DMDWarrior \u5c06\u7ee7\u7eed\u5bc6\u5207\u5173\u6ce8 BASECAMP \u548c TRAILHEAD \u4e34\u5e8a\u8bd5\u9a8c\uff0c\u5e76\u5728\u83b7\u5f97\u65b0\u7684\u7597\u6548\u3001\u5b89\u5168\u6027\u548c\u751f\u7269\u6807\u5fd7\u7269\u6570\u636e\u540e\u53ca\u65f6\u62a5\u9053\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong><a href=\"https:\/\/dmdwarrior.com\/zh\/duchenne-exon-deletion-tool\/\" target=\"_blank\" data-type=\"link\" data-id=\"https:\/\/dmdwarrior.com\/duchenne-exon-deletion-tool\/\" rel=\"noreferrer noopener\">\u60a8\u7b26\u5408\u4f7f\u7528\u798f\u62c9\u624e\u5e15\u5b9a\uff08Forazapadin\uff09\u7684\u6761\u4ef6\u5417\uff1f<\/a><\/strong> \u7acb\u5373\u67e5\u770b\uff01<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>Satellos Bioscience has announced that its investigational Duchenne muscular dystrophy (DMD) treatment SAT-3247 has officially received the International Nonproprietary Name (INN) Forazapadin from the World Health Organization (WHO). The naming milestone is an important step in the drug\u2019s global clinical development and future regulatory pathway. What is Forazapadin? Forazapadin is an oral small-molecule medicine being [&hellip;]<\/p>\n","protected":false},"author":8,"featured_media":8729,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[903,251,252,253],"class_list":["post-8726","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-forazapadin","tag-sat-3247","tag-satellos","tag-satellos-bioscience"],"subtitle":"\u7528\u4e8e\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u836f\u7269 Satellos' SAT-3247 \u6709\u4e86\u65b0\u540d\u79f0\uff1a\u798f\u62c9\u624e\u5e15\u5b9a (Forazapadin)\u3002\u4e16\u754c\u536b\u751f\u7ec4\u7ec7\u7684\u6279\u51c6\u6807\u5fd7\u7740\u8be5\u836f\u7269\u7814\u53d1\u8fdb\u7a0b\u4e2d\u7684\u5173\u952e\u4e00\u6b65\u3002\u4f46\u8fd9\u79cd\u65b0\u7684\u53e3\u670d\u7597\u6cd5\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u672a\u6765\u6cbb\u7597\u610f\u5473\u7740\u4ec0\u4e48\u5462\uff1f","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/8726","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/8"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=8726"}],"version-history":[{"count":2,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/8726\/revisions"}],"predecessor-version":[{"id":8730,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/8726\/revisions\/8730"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/8729"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=8726"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=8726"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=8726"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}