{"id":7974,"date":"2026-05-27T17:33:34","date_gmt":"2026-05-27T14:33:34","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=7974"},"modified":"2026-05-27T17:33:35","modified_gmt":"2026-05-27T14:33:35","slug":"dyne-251-z-rostudirsen-phase-3-forzetto-clinical-trial","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/dyne-251-z-rostudirsen-phase-3-forzetto-clinical-trial\/","title":{"rendered":"Z-Rostudirsen\u6cbb\u7597DMD\u7684DYNE-251\u548cFORZETTO III\u671f\u4e34\u5e8a\u8bd5\u9a8c\u6b63\u5f0f\u542f\u52a8\u3002"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>Dyne Therapeutics \u5ba3\u5e03\u542f\u52a8 Z-Rostudirsen \u6cbb\u7597 DMD \u7684 Dyne Therapeutics 3 \u671f FORZETTO \u8bd5\u9a8c (NCT07608432)\uff0c\u8fd9\u6807\u5fd7\u7740\u53d7\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u5f71\u54cd\u7684\u5bb6\u5ead\u53c8\u5411\u524d\u8fc8\u51fa\u4e86\u4e00\u5927\u6b65\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u9879\u5168\u7403\u6027 III \u671f\u7814\u7a76\u5c06\u8bc4\u4f30 z-rostudirsen (DYNE-251) \u5728\u9002\u5408\u63a5\u53d7 51 \u53f7\u5916\u663e\u5b50\u8df3\u8dc3\u624b\u672f\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u60a3\u8005\u4e2d\u7684\u7597\u6548\u3002\u8be5\u516c\u53f8\u8fd8\u8ba1\u5212\u5728\u672c\u5b63\u5ea6\u665a\u4e9b\u65f6\u5019\u5411\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40 (FDA) \u63d0\u4ea4\u751f\u7269\u5236\u54c1\u8bb8\u53ef\u7533\u8bf7 (BLA)\uff0c\u4ee5\u5bfb\u6c42\u52a0\u901f\u5ba1\u6279\u3002\u4e86\u89e3\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/biologics-license-application-bla\/\" target=\"_blank\" data-type=\"post\" data-id=\"5027\" rel=\"noreferrer noopener\">BLA\u662f\u4ec0\u4e48\u610f\u601d\uff1f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">FORZETTO \u8bd5\u9a8c\u8bbe\u8ba1\u5c06\u5728\u610f\u5927\u5229\u4f5b\u7f57\u4f26\u8428\u4e3e\u884c\u7684\u7b2c 19 \u5c4a\u56fd\u9645\u795e\u7ecf\u808c\u8089\u75be\u75c5\u5927\u4f1a (ICNMD) \u4e0a\u8fdb\u884c\u5c55\u793a\u3002.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u76ee\u5f55<\/h2><nav><ul><li><a href=\"#what-is-z-rostudirsen-dyne-251\">\u4ec0\u4e48\u662f Z-Rostudirsen (DYNE-251)\uff1f<\/a><\/li><li><a href=\"#how-the-forzetto-phase-3-trial-will-work\">FORZETTO \u4e09\u671f\u4e34\u5e8a\u8bd5\u9a8c\u5c06\u5982\u4f55\u8fdb\u884c<\/a><\/li><li><a href=\"#primary-endpoint-focuses-on-muscle-function\">\u4e3b\u8981\u7ec8\u70b9\u6307\u6807\u4fa7\u91cd\u4e8e\u808c\u8089\u529f\u80fd<\/a><\/li><li><a href=\"#additional-secondary-endpoints-in-the-forzetto-study\">FORZETTO \u7814\u7a76\u4e2d\u7684\u5176\u4ed6\u6b21\u8981\u7ec8\u70b9<\/a><\/li><li><a href=\"#fda-alignment-and-accelerated-approval-plans\">FDA \u5bf9\u9f50\u548c\u52a0\u901f\u5ba1\u6279\u8ba1\u5212<\/a><\/li><li><a href=\"#why-the-dyne-therapeutics-phase-3-forzetto-trial-of-z-rostudirsen-for-dmd-matters\">\u4e3a\u4ec0\u4e48 Z-Rostudirsen \u6cbb\u7597 DMD \u7684 Dyne Therapeutics \u548c FORZETTO \u4e09\u671f\u4e34\u5e8a\u8bd5\u9a8c\u5982\u6b64\u91cd\u8981\uff1f<\/a><\/li><li><a href=\"#contact-information\">\u8054\u7cfb\u4fe1\u606f<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"what-is-z-rostudirsen-dyne-251\" class=\"wp-block-heading\">\u4ec0\u4e48\u662f Z-Rostudirsen (DYNE-251)\uff1f<\/h2>\n\n\n\n<h3 id=\"a-next-generation-exon-51-skipping-therapy\" class=\"wp-block-heading\">\u65b0\u4e00\u4ee3\u5916\u663e\u5b5051\u8df3\u8dc3\u7597\u6cd5<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Z-rostudirsen\uff0c\u53c8\u540d DYNE-251\uff0c\u662f\u4e00\u79cd\u7814\u7a76\u6027\u7597\u6cd5\uff0c\u65e8\u5728\u4e3a\u60a3\u6709 DMD \u7a81\u53d8\u3001\u53ef\u4ece\u5916\u663e\u5b50 51 \u8df3\u8dc3\u4e2d\u83b7\u76ca\u7684\u60a3\u8005\u63d0\u4f9b\u6cbb\u7597\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u7597\u6cd5\u65e8\u5728\u5e2e\u52a9\u4eba\u4f53\u5728\u808c\u8089\u7ec4\u7ec7\u548c\u4e2d\u67a2\u795e\u7ecf\u7cfb\u7edf\u4e2d\u4ea7\u751f\u63a5\u8fd1\u5168\u957f\u7684\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u3002\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u5bf9\u4e8e\u4fdd\u62a4\u808c\u8089\u514d\u53d7\u635f\u4f24\u81f3\u5173\u91cd\u8981\uff0c\u5176\u7f3a\u4e4f\u4f1a\u5bfc\u81f4\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u60a3\u8005\u51fa\u73b0\u8fdb\u884c\u6027\u808c\u8089\u65e0\u529b\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u6839\u636e Dyne Therapeutics \u7684\u7814\u7a76\uff0c\u6cbb\u7597\u7684\u76ee\u6807\u4e0d\u4ec5\u662f\u6539\u5584\u5b9e\u9a8c\u5ba4\u751f\u7269\u6807\u5fd7\u7269\uff0c\u8fd8\u8981\u5e2e\u52a9\u60a3\u8005\u66f4\u597d\u5730\u6d3b\u52a8\u3001\u66f4\u597d\u5730\u547c\u5438\uff0c\u5e76\u63d0\u9ad8\u65e5\u5e38\u751f\u6d3b\u8d28\u91cf\u3002.<\/p>\n\n\n\n<figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"847\" height=\"1024\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-847x1024.jpg\" alt=\"\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u53ef\u901a\u8fc7\u5916\u663e\u5b50 51 \u8df3\u8dc3\u7597\u6cd5\u6cbb\u7597\u7684\u7a81\u53d8\u548c\u7f3a\u5931\" class=\"wp-image-4526\" title=\"\" srcset=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-847x1024.jpg 847w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-248x300.jpg 248w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-768x929.jpg 768w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-1270x1536.jpg 1270w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-1693x2048.jpg 1693w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-10x12.jpg 10w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-347x420.jpg 347w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-150x181.jpg 150w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-300x363.jpg 300w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-696x842.jpg 696w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-1068x1292.jpg 1068w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-1920x2323.jpg 1920w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping.jpg 1984w\" sizes=\"auto, (max-width: 847px) 100vw, 847px\" \/><figcaption class=\"wp-element-caption\"><a href=\"https:\/\/dmdwarrior.com\/zh\/mutations-and-deletions-amenable-to-exon-51-skipping-therapies-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u9002\u5408\u5916\u663e\u5b50 51 \u8df3\u8dc3\u7597\u6cd5\u7684\u7a81\u53d8\u548c\u7f3a\u5931<\/a><\/figcaption><\/figure>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7acb\u5373\u5c1d\u8bd5\uff1a<\/strong> <strong><a href=\"https:\/\/dmdwarrior.com\/zh\/duchenne-exon-deletion-tool\/\" target=\"_blank\" rel=\"noreferrer noopener\">DMD \u8fd8\u662f BMD\uff1f\u5916\u663e\u5b50\u68c0\u67e5\u5de5\u5177<\/a><\/strong><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"how-the-forzetto-phase-3-trial-will-work\" class=\"wp-block-heading\">FORZETTO \u4e09\u671f\u4e34\u5e8a\u8bd5\u9a8c\u5c06\u5982\u4f55\u8fdb\u884c<\/h2>\n\n\n\n<h3 id=\"global-randomized-placebo-controlled-study\" class=\"wp-block-heading\">\u5168\u7403\u968f\u673a\u5b89\u6170\u5242\u5bf9\u7167\u7814\u7a76<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>DYNE-251 3 \u671f FORZETTO \u8bd5\u9a8c\u662f\u4e00\u9879\u5168\u7403\u6027\u3001\u968f\u673a\u3001\u53cc\u76f2\u3001\u5b89\u6170\u5242\u5bf9\u7167\u7814\u7a76\uff0c\u65e8\u5728\u8bc4\u4f30 z-rostudirsen \u7684\u5b89\u5168\u6027\u548c\u6709\u6548\u6027\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u7814\u7a76\u7684\u5173\u952e\u7ec6\u8282\u5305\u62ec\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u7ea690\u540d\u53ef\u72ec\u7acb\u884c\u8d70\u7684\u7537\u6027\u53c2\u4e0e\u8005<\/li>\n\n\n\n<li>4\u81f318\u5c81<\/li>\n\n\n\n<li>\u53c2\u4e0e\u8005\u5fc5\u987b\u540c\u610f\u8df3\u8fc7\u7b2c51\u53f7\u5916\u663e\u5b50\u3002<\/li>\n\n\n\n<li>\u60a3\u8005\u5c06\u63a5\u53d7\u4ee5\u4e0b\u4e24\u79cd\u6cbb\u7597\u4e4b\u4e00\uff1a\n<ul class=\"wp-block-list\">\n<li>20 mg\/kg z-rostudirsen<\/li>\n\n\n\n<li>\u6216\u5b89\u6170\u5242<\/li>\n<\/ul>\n<\/li>\n\n\n\n<li>\u6cbb\u7597\u5c06\u6bcf\u56db\u5468\u8fdb\u884c\u4e00\u6b21\uff08Q4W\uff09\u3002<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u7b2c\u4e00\u4e2a\u4e34\u5e8a\u8bd5\u9a8c\u70b9\u5df2\u7ecf\u542f\u7528\uff0c\u73b0\u5728\u5f00\u59cb\u62db\u52df\u53d7\u8bd5\u8005\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"primary-endpoint-focuses-on-muscle-function\" class=\"wp-block-heading\">\u4e3b\u8981\u7ec8\u70b9\u6307\u6807\u4fa7\u91cd\u4e8e\u808c\u8089\u529f\u80fd<\/h2>\n\n\n\n<h3 id=\"rise-from-floor-velocity-will-be-measured\" class=\"wp-block-heading\">\u5c06\u6d4b\u91cf\u4ece\u5730\u9762\u4e0a\u5347\u7684\u901f\u5ea6<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u8be5\u7814\u7a76\u7684\u4e3b\u8981\u76ee\u6807\u662f\u6d4b\u91cf\u7b2c 73 \u5468\u65f6\u4ece\u5730\u9762\u8d77\u7acb (RFF) \u901f\u5ea6\uff08\u4e5f\u79f0\u4e3a\u8d77\u7acb\u65f6\u95f4 (TTR) \u901f\u5ea6\uff09\u7684\u53d8\u5316\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u6d4b\u8bd5\u6d4b\u91cf\u60a3\u8005\u4ece\u5730\u677f\u4e0a\u7ad9\u8d77\u6765\u7684\u901f\u5ea6\uff0c\u88ab\u8ba4\u4e3a\u662f DMD \u4e34\u5e8a\u8bd5\u9a8c\u4e2d\u808c\u8089\u529b\u91cf\u548c\u8fd0\u52a8\u534f\u8c03\u6027\u7684\u91cd\u8981\u6307\u6807\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u5728\u65e9\u671f\u7684 1\/2 \u671f DELIVER \u7814\u7a76\u4e2d\uff0c\u63a5\u53d7 z-rostudirsen \u6cbb\u7597\u7684\u60a3\u8005\u5728\u516d\u4e2a\u6708\u540e RFF \u901f\u5ea6\u8f83\u63a5\u53d7\u5b89\u6170\u5242\u6cbb\u7597\u7684\u53c2\u4e0e\u8005\u6709\u663e\u8457\u6539\u5584\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"additional-secondary-endpoints-in-the-forzetto-study\" class=\"wp-block-heading\">FORZETTO \u7814\u7a76\u4e2d\u7684\u5176\u4ed6\u6b21\u8981\u7ec8\u70b9<\/h2>\n\n\n\n<h3 id=\"researchers-will-track-mobility-and-lung-function\" class=\"wp-block-heading\">\u7814\u7a76\u4eba\u5458\u5c06\u8ffd\u8e2a\u6d3b\u52a8\u80fd\u529b\u548c\u80ba\u529f\u80fd<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u7814\u7a76\u8fd8\u5c06\u8bc4\u4f30\u51e0\u9879\u5176\u4ed6\u529f\u80fd\u6027\u7ed3\u679c\uff0c\u5305\u62ec\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u6b65\u901f\u7b2c 95 \u767e\u5206\u4f4d (SV95C)<\/li>\n\n\n\n<li><a href=\"https:\/\/dmdwarrior.com\/zh\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" target=\"_blank\" data-type=\"post\" data-id=\"4959\" rel=\"noreferrer noopener\">\u5317\u6781\u661f\u52a8\u6001\u8bc4\u4f30 (NSAA)<\/a><\/li>\n\n\n\n<li>10\u7c73\u6b65\u884c\/\u8dd1\u6b65\uff0810MWR\uff09<\/li>\n\n\n\n<li>\u56db\u7ea7\u53f0\u9636\u6500\u767b (4SC)<\/li>\n\n\n\n<li>\u7528\u529b\u80ba\u6d3b\u91cf\u5360\u9884\u8ba1\u503c\u7684\u767e\u5206\u6bd4 (FVC%p)<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u7814\u7a76\u4eba\u5458\u8fd8\u5c06\u6536\u96c6\u60a3\u8005\u62a5\u544a\u7684\u7ed3\u679c\uff0c\u4ee5\u66f4\u597d\u5730\u4e86\u89e3\u6cbb\u7597\u53ef\u80fd\u5bf9\u65e5\u5e38\u751f\u6d3b\u4ea7\u751f\u7684\u5f71\u54cd\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5728\u6700\u521d\u7684 72 \u5468\u5b89\u6170\u5242\u5bf9\u7167\u671f\u7ed3\u675f\u540e\uff0c\u7b26\u5408\u6761\u4ef6\u7684\u53c2\u4e0e\u8005\u53ef\u4ee5\u7ee7\u7eed\u53c2\u52a0\u4e3a\u671f 96 \u5468\u7684\u5f00\u653e\u6807\u7b7e\u6269\u5c55\u7814\u7a76\u3002.<\/strong><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"fda-alignment-and-accelerated-approval-plans\" class=\"wp-block-heading\">FDA \u5bf9\u9f50\u548c\u52a0\u901f\u5ba1\u6279\u8ba1\u5212<\/h2>\n\n\n\n<h3 id=\"forzetto-could-support-full-traditional-approval\" class=\"wp-block-heading\">FORZETTO \u53ef\u652f\u6301\u5b8c\u6574\u7684\u4f20\u7edf\u8ba4\u8bc1<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">Dyne Therapeutics \u8868\u793a\uff0c\u8be5\u516c\u53f8\u5df2\u4e0e\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40 (FDA) \u5c31 FORZETTO 3 \u671f\u8bd5\u9a8c\u8bbe\u8ba1\u548c\u65b9\u6848\u8fbe\u6210\u4e00\u81f4\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u9879\u7814\u7a76\u65e8\u5728\u4f5c\u4e3a\u4e00\u9879\u786e\u8bc1\u6027\u8bd5\u9a8c\uff0c\u4ee5\u671f\u5c06\u7f8e\u56fd\u52a0\u901f\u5ba1\u6279\u8f6c\u5316\u4e3a\u5b8c\u5168\u5e38\u89c4\u5ba1\u6279\u3002\u8be5\u8bd5\u9a8c\u4e5f\u53ef\u80fd\u4e3a\u672a\u6765\u5728\u7f8e\u56fd\u4ee5\u5916\u5730\u533a\u7684\u76d1\u7ba1\u7533\u8bf7\u63d0\u4f9b\u652f\u6301\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"why-the-dyne-therapeutics-phase-3-forzetto-trial-of-z-rostudirsen-for-dmd-matters\" class=\"wp-block-heading\">\u4e3a\u4ec0\u4e48 Z-Rostudirsen \u6cbb\u7597 DMD \u7684 Dyne Therapeutics \u548c FORZETTO \u4e09\u671f\u4e34\u5e8a\u8bd5\u9a8c\u5982\u6b64\u91cd\u8981\uff1f<\/h2>\n\n\n\n<h3 id=\"a-potentially-important-development-for-the-dmd-community\" class=\"wp-block-heading\">\u5bf9DMD\u793e\u7fa4\u800c\u8a00\uff0c\u4e00\u9879\u53ef\u80fd\u5177\u6709\u91cd\u8981\u610f\u4e49\u7684\u8fdb\u5c55<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Z-Rostudirsen \u6cbb\u7597 DMD \u7684 Dyne Therapeutics 3 \u671f FORZETTO \u8bd5\u9a8c\u7684\u542f\u52a8\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7fa4\u4f53\u6765\u8bf4\u662f\u4e00\u4e2a\u91cd\u8981\u7684\u91cc\u7a0b\u7891\uff0c\u7279\u522b\u662f\u5bf9\u4e8e\u7b26\u5408\u5916\u663e\u5b50 51 \u8df3\u8dc3\u7597\u6cd5\u6761\u4ef6\u7684\u60a3\u8005\u800c\u8a00\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u9274\u4e8e\u65e9\u671f\u4e34\u5e8a\u6570\u636e\u4ee4\u4eba\u9f13\u821e\uff0c\u76ee\u524d\u4e00\u9879\u5927\u578b\u9a8c\u8bc1\u6027\u7814\u7a76\u6b63\u5728\u8fdb\u884c\u4e2d\uff0c\u7814\u7a76\u4eba\u5458\u548c\u60a3\u8005\u5bb6\u5c5e\u5c06\u5bc6\u5207\u5173\u6ce8 DYNE-251 \u662f\u5426\u80fd\u4e3a\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4eba\u4eec\u5e26\u6765\u6709\u610f\u4e49\u7684\u529f\u80fd\u6539\u5584\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"contact-information\" class=\"wp-block-heading\">\u8054\u7cfb\u4fe1\u606f<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u540d\u79f0\uff1aDyne\u4e34\u5e8a\u8bd5\u9a8c<\/li>\n\n\n\n<li>\u7535\u8bdd\u53f7\u7801\uff1a+1-781-317-1919<\/li>\n\n\n\n<li>\u7535\u5b50\u90ae\u4ef6\uff1aclinicaltrials@dyne-tx.com<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5173\u6ce8\u6b64\u9875\u9762<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u6240\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Dyne Therapeutics has announced the start of the Dyne Therapeutics Phase 3 FORZETTO Trial (NCT07608432) of Z-Rostudirsen for DMD, marking another major step forward for families affected by Duchenne muscular dystrophy (DMD). The global Phase 3 study will evaluate z-rostudirsen (DYNE-251) in people living with DMD who are amenable to exon 51 skipping. The company [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":8013,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[137,143,208,145,122,193,421,194,780,460],"class_list":["post-7974","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-clinical-trial","tag-dyne","tag-dyne-therapeutics","tag-dyne-251","tag-exon-51","tag-exon-51-skipping","tag-exon-51-skipping-therapy","tag-exon-51-treatment","tag-forzetto","tag-z-rostudirsen"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/7974","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=7974"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/7974\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/8013"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=7974"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=7974"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=7974"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}