{"id":6720,"date":"2026-03-11T13:24:08","date_gmt":"2026-03-11T10:24:08","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6720"},"modified":"2026-03-11T13:31:48","modified_gmt":"2026-03-11T10:31:48","slug":"genethon-gnt0004-creatine-kinase-ck-levels-and-nsaa-scores","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/genethon-gnt0004-creatine-kinase-ck-levels-and-nsaa-scores\/","title":{"rendered":"Genethon \u8bc1\u5b9e GNT0004 \u57fa\u56e0\u7597\u6cd5\u4e24\u5e74\u7597\u6548\u663e\u8457\uff0c\u808c\u9178\u6fc0\u9176 (CK) \u6c34\u5e73\u548c NSAA \u8bc4\u5206\u5747\u6709\u6240\u6539\u5584"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u7684\u57fa\u56e0\u6cbb\u7597\u7814\u7a76\u4e0d\u65ad\u53d6\u5f97\u8fdb\u5c55\u3002. <strong>\u5728\u5965\u5170\u591a\u4e3e\u884c\u7684 MDA \u4e34\u5e8a\u4e0e\u79d1\u5b66\u4f1a\u8bae\u4e0a\uff0c\u6cd5\u56fd\u57fa\u56e0\u6cbb\u7597\u7ec4\u7ec7 Genethon \u516c\u5e03\u4e86\u65b0\u7684\u957f\u671f\u6570\u636e\uff0c\u8868\u660e\u5176\u5728\u7814\u7597\u6cd5 GNT0004 \u5728\u6cbb\u7597\u4e24\u5e74\u540e\u4ecd\u80fd\u4fdd\u6301\u4e34\u5e8a\u7597\u6548\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u7814\u7a76\u7ed3\u679c\u663e\u793a\uff0c\u5728\u4e34\u5e8a\u8bd5\u9a8c\u7684\u7b2c\u4e00\u9636\u6bb5\u63a5\u53d7\u6cbb\u7597\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7537\u5b69\u7684\u8fd0\u52a8\u529f\u80fd\u5f97\u5230\u6539\u5584\uff0c\u808c\u8089\u635f\u4f24\u751f\u7269\u6807\u5fd7\u7269\u51cf\u5c11\uff0c\u4e14\u5b89\u5168\u6027\u826f\u597d\u3002.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u76ee\u5f55<\/h2><nav><ul><li><a href=\"#two-year-results-from-the-gnt-0004-clinical-trial\">GNT0004\u4e34\u5e8a\u8bd5\u9a8c\u4e24\u5e74\u7ed3\u679c<\/a><\/li><li><a href=\"#significant-improvement-in-nsaa-motor-function-scores\">NSAA\u8fd0\u52a8\u529f\u80fd\u8bc4\u5206\u663e\u8457\u63d0\u9ad8<\/a><\/li><li><a href=\"#improvements-in-walking-tests\">\u6b65\u884c\u6d4b\u8bd5\u7684\u6539\u8fdb<\/a><\/li><li><a href=\"#large-reduction-in-creatine-kinase-ck-levels\">\u808c\u9178\u6fc0\u9176\uff08CK\uff09\u6c34\u5e73\u5927\u5e45\u964d\u4f4e<\/a><\/li><li><a href=\"#mri-imaging-shows-slower-disease-progression\">\u6838\u78c1\u5171\u632f\u6210\u50cf\u663e\u793a\u75be\u75c5\u8fdb\u5c55\u8f83\u6162<\/a><\/li><li><a href=\"#favorable-safety-profile\">\u826f\u597d\u7684\u5b89\u5168\u6027<\/a><\/li><li><a href=\"#pivotal-phase-of-the-trial-now-underway\">\u7814\u7a76\u7684\u5173\u952e\u9636\u6bb5\u6b63\u5728\u8fdb\u884c\u4e2d<\/a><\/li><li><a href=\"#why-these-results-matter\">\u8fd9\u4e9b\u7ed3\u679c\u4e3a\u4f55\u91cd\u8981<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"two-year-results-from-the-gnt-0004-clinical-trial\">GNT0004\u4e34\u5e8a\u8bd5\u9a8c\u4e24\u5e74\u7ed3\u679c<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u8fd9\u9879\u56fd\u9645\u591a\u4e2d\u5fc3\u7814\u7a76\u62db\u52df\u4e86 6 \u81f3 10 \u5c81\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e14\u80fd\u591f\u884c\u8d70\u7684\u7537\u5b69\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u5728\u5242\u91cf\u9012\u589e\u9636\u6bb5\uff0c\u4e94\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u6cbb\u7597\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u6cd5\u56fd\u6709\u56db\u540d\u60a3\u8005<\/li>\n\n\n\n<li>\u82f1\u56fd\u4e00\u540d\u60a3\u8005<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e09\u540d\u60a3\u8005\u63a5\u53d7\u4e86 3\u00d710\u00b9\u00b3 vg\/kg \u7684\u6cbb\u7597\u5242\u91cf\uff0c\u4ed6\u4eec\u7684\u957f\u671f\u968f\u8bbf\u6570\u636e\u6784\u6210\u4e86\u65b0\u5206\u6790\u7684\u57fa\u7840\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e24\u5e74\u540e\uff0c\u7814\u7a76\u7ed3\u679c\u663e\u793a\uff1a<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u8fd0\u52a8\u529f\u80fd\u6301\u7eed\u6539\u5584<\/li>\n\n\n\n<li>\u808c\u8089\u635f\u4f24\u751f\u7269\u6807\u5fd7\u7269\u51cf\u5c11<\/li>\n\n\n\n<li>\u75be\u75c5\u8fdb\u5c55\u8f83\u6162<\/li>\n\n\n\n<li>\u6ca1\u6709\u4e25\u91cd\u7684\u5b89\u5168\u9690\u60a3<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"significant-improvement-in-nsaa-motor-function-scores\">NSAA\u8fd0\u52a8\u529f\u80fd\u8bc4\u5206\u663e\u8457\u63d0\u9ad8<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u91c7\u7528\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\u91cf\u8868\uff08NSAA\uff09\u8bc4\u4f30\u8fd0\u52a8\u529f\u80fd\uff0c\u8be5\u91cf\u8868\u662f\u5e7f\u6cdb\u7528\u4e8e\u8bc4\u4f30\u53ef\u6b65\u884c\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u60a3\u8005\u7684\u4e34\u5e8a\u91cf\u8868\u3002\u4e86\u89e3\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u5317\u6781\u661f\u52a8\u6001\u8bc4\u4f30\uff08NSAA\uff09<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4e3b\u8981\u7814\u7a76\u7ed3\u679c\u5305\u62ec\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u4e24\u5e74\u540eNSAA\u8bc4\u5206\u63d0\u9ad8\u4e869\u5206<\/strong><\/li>\n\n\n\n<li>\u4e0e\u901a\u8fc7\u503e\u5411\u8bc4\u5206\u5206\u6790\u5339\u914d\u7684\u672a\u6cbb\u7597\u60a3\u8005\u76f8\u6bd4<\/li>\n\n\n\n<li><strong>\u8fdc\u9ad8\u4e8e\u88ab\u8ba4\u4e3a\u5177\u6709\u4e34\u5e8a\u610f\u4e49\u7684 2.5 \u5206\u9608\u503c\u3002<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u4e9b\u7ed3\u679c\u8868\u660e\uff0cGNT0004 \u53ef\u4ee5\u663e\u8457\u6539\u5584\u6216\u7a33\u5b9a\u63a5\u53d7\u6cbb\u7597\u60a3\u8005\u7684\u8fd0\u52a8\u80fd\u529b\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"improvements-in-walking-tests\">\u6b65\u884c\u6d4b\u8bd5\u7684\u6539\u8fdb<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u63a5\u53d7 GNT0004 \u6cbb\u7597\u7684\u60a3\u8005\u5728\u5b9a\u65f6\u6b65\u884c\u8bc4\u4f30\u4e2d\u4e5f\u8868\u73b0\u51fa\u53ef\u8861\u91cf\u7684\u8fdb\u6b65\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u4e0e\u672a\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u76f8\u6bd4\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u57286\u5206\u949f\u6b65\u884c\u6d4b\u8bd5\u4e2d\u5e73\u5747\u591a\u8d70\u4e86173\u7c73\u3002<\/strong><\/li>\n\n\n\n<li><strong>10\u7c73\u6b65\u884c\u6d4b\u8bd5\u901f\u5ea6\u63d0\u9ad80.95\u7c73\/\u79d2<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u4e9b\u529f\u80fd\u4e0a\u7684\u6539\u5584\u8868\u660e\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u513f\u7ae5\u5728\u4e00\u6bb5\u65f6\u95f4\u5185\u4fdd\u6301\u4e86\u66f4\u597d\u7684\u6d3b\u52a8\u80fd\u529b\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"large-reduction-in-creatine-kinase-ck-levels\">\u808c\u9178\u6fc0\u9176\uff08CK\uff09\u6c34\u5e73\u5927\u5e45\u964d\u4f4e<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7814\u7a76\u4eba\u5458\u8fd8\u62a5\u544a\u79f0\uff0c\u808c\u9178\u6fc0\u9176 (CK) \u6c34\u5e73\u5927\u5e45\u4e0b\u964d\uff0c\u808c\u9178\u6fc0\u9176\u662f\u808c\u8089\u635f\u4f24\u7684\u91cd\u8981\u751f\u7269\u6807\u5fd7\u7269\u3002.<\/strong> \u9605\u8bfb\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/what-is-creatine-kinase-ck\/\" data-type=\"post\" data-id=\"2167\" target=\"_blank\" rel=\"noreferrer noopener\">\u4ec0\u4e48\u662f\u808c\u9178\u6fc0\u9176\uff08CK\uff09\uff1f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u7ed3\u679c\u663e\u793a\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u4e24\u5e74\u540e CK \u5e73\u5747\u964d\u4f4e\u7ea6 70%<\/strong><\/li>\n\n\n\n<li>\u4e0e\u6bcf\u4f4d\u60a3\u8005\u6cbb\u7597\u524d\u7684\u57fa\u7ebf\u6c34\u5e73\u76f8\u6bd4<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e00\u540d\u63a5\u53d7\u4e09\u5e74\u968f\u8bbf\u7684\u60a3\u8005 CK \u6c34\u5e73\u4fdd\u6301\u7a33\u5b9a\uff0c\u8fd9\u8868\u660e\u8be5\u7597\u6cd5\u53ef\u80fd\u5bf9\u808c\u8089\u7ec6\u80de\u819c\u7a33\u5b9a\u6027\u4ea7\u751f\u6301\u4e45\u5f71\u54cd\u3002.<\/strong><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"mri-imaging-shows-slower-disease-progression\">\u6838\u78c1\u5171\u632f\u6210\u50cf\u663e\u793a\u75be\u75c5\u8fdb\u5c55\u8f83\u6162<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u5b9a\u91cf\u78c1\u5171\u632f\u6210\u50cf\u663e\u793a\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u808c\u8089\u9000\u5316\u901f\u5ea6\u8f83\u6162\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u7814\u7a76\u4eba\u5458\u89c2\u5bdf\u5230\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u808c\u8089\u8102\u80aa\u542b\u91cf\u5dee\u5f02\u8d85\u8fc7 18%<\/strong><\/li>\n\n\n\n<li>\u4e0e\u81ea\u7136\u53f2\u961f\u5217\u4e2d\u672a\u7ecf\u6cbb\u7597\u7684\u60a3\u8005\u76f8\u6bd4<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u5728\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e2d\uff0c\u8102\u80aa\u6d78\u6da6\u7a0b\u5ea6\u8d8a\u9ad8\u901a\u5e38\u53cd\u6620\u75be\u75c5\u8fdb\u5c55\u8d8a\u4e25\u91cd\u3002\u8102\u80aa\u6d78\u6da6\u7a0b\u5ea6\u8d8a\u4f4e\u5219\u8868\u660e\u808c\u8089\u7ec4\u7ec7\u4fdd\u5b58\u5b8c\u597d\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"favorable-safety-profile\">\u826f\u597d\u7684\u5b89\u5168\u6027<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u8be5\u7814\u7a76\u62a5\u544a\u672a\u53d1\u73b0\u4e25\u91cd\u4e0d\u826f\u4e8b\u4ef6\uff0c\u8bc1\u5b9e\u8be5\u7597\u6cd5\u8010\u53d7\u6027\u826f\u597d\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u60a3\u8005\u63a5\u53d7\u4e86\u6682\u65f6\u7684\u9884\u9632\u6027\u514d\u75ab\u6291\u5236\u6cbb\u7597\uff0c\u8fd9\u6709\u52a9\u4e8e\u6700\u5927\u9650\u5ea6\u5730\u51cf\u5c11\u5bf9\u57fa\u56e0\u6cbb\u7597\u8f7d\u4f53\u7684\u514d\u75ab\u53cd\u5e94\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"pivotal-phase-of-the-trial-now-underway\">\u7814\u7a76\u7684\u5173\u952e\u9636\u6bb5\u6b63\u5728\u8fdb\u884c\u4e2d<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u8be5\u4e34\u5e8a\u8bd5\u9a8c\u7684\u5173\u952e\u9636\u6bb5\u5df2\u83b7\u5f97\u4ee5\u4e0b\u673a\u6784\u7684\u6279\u51c6\uff1a<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u6b27\u6d32\u836f\u54c1\u7ba1\u7406\u5c40\uff08EMA\uff09<\/li>\n\n\n\n<li>\u836f\u54c1\u548c\u4fdd\u5065\u4ea7\u54c1\u76d1\u7ba1\u5c40\uff08MHRA\uff09<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u6b64\u9636\u6bb5\u5c06\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u62db\u52df 64 \u540d 6-10 \u5c81\u53ef\u72ec\u7acb\u884c\u8d70\u7684\u7537\u5b69<\/strong><\/li>\n\n\n\n<li>\u91c7\u7528\u968f\u673a\u3001\u53cc\u76f2\u3001\u5b89\u6170\u5242\u5bf9\u7167\u8bbe\u8ba1<\/li>\n\n\n\n<li><strong>\u6d4b\u8bd5\u9009\u5b9a\u7684\u5242\u91cf 3\u00d710\u00b9\u00b3 vg\/kg<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u503c\u5f97\u6ce8\u610f\u7684\u662f\uff0c\u8be5\u5242\u91cf\u4f4e\u4e8e\u5176\u4ed6\u4e00\u4e9b\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u57fa\u56e0\u6cbb\u7597\u8bd5\u9a8c\u4e2d\u4f7f\u7528\u7684\u5242\u91cf\uff0c\u8fd9\u53ef\u80fd\u5e26\u6765\u5b89\u5168\u4f18\u52bf\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4e86\u89e3\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u6f5c\u5728\u65b0\u57fa\u56e0\u7597\u6cd5<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"why-these-results-matter\">\u8fd9\u4e9b\u7ed3\u679c\u4e3a\u4f55\u91cd\u8981<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u662f\u4e00\u79cd\u4e25\u91cd\u7684\u9057\u4f20\u6027\u75be\u75c5\uff0c\u7531\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u57fa\u56e0\u7a81\u53d8\u5f15\u8d77\u3002\u8be5\u75be\u75c5\u4f1a\u5bfc\u81f4\u8fdb\u884c\u6027\u808c\u8089\u9000\u5316\u548c\u6d3b\u52a8\u80fd\u529b\u4e27\u5931\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u57fa\u56e0\u7597\u6cd5\uff08\u4f8b\u5982 GNT0004\uff09\u65e8\u5728\u5c06\u529f\u80fd\u6027\u9057\u4f20\u7269\u8d28\u8f93\u9001\u5230\u808c\u8089\u7ec6\u80de\uff0c\u4ece\u800c\u6709\u53ef\u80fd\u89e3\u51b3\u75be\u75c5\u7684\u6839\u672c\u539f\u56e0\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e24\u5e74\u7684\u7ed3\u679c\u8868\u660e\uff0cGNT0004 \u53ef\u80fd\uff1a<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u6539\u5584\u8fd0\u52a8\u529f\u80fd<\/li>\n\n\n\n<li>\u51cf\u5c11\u808c\u8089\u635f\u4f24<\/li>\n\n\n\n<li>\u75be\u75c5\u8fdb\u5c55\u7f13\u6162<\/li>\n\n\n\n<li>\u4fdd\u6301\u53ef\u63a7\u7684\u5b89\u5168\u72b6\u51b5<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u9879\u5173\u952e\u7814\u7a76\u7684\u8fdb\u4e00\u6b65\u7ed3\u679c\u5c06\u51b3\u5b9a\u8be5\u7597\u6cd5\u6700\u7ec8\u662f\u5426\u80fd\u6210\u4e3a\u4e00\u79cd\u83b7\u6279\u7684\u6cbb\u7597\u65b9\u6848\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5173\u6ce8\u6b64\u9875\u9762<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u6240\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Gene therapy research for Duchenne muscular dystrophy (DMD) continues to advance. At the MDA Clinical &amp; Scientific Conference in Orlando, the French gene therapy organization Genethon presented new long-term data showing that its investigational therapy GNT0004 maintains clinical benefits two years after treatment. The findings highlight improvements in motor function, reductions in muscle damage biomarkers, [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6722,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[68,61,105,220,434,449],"class_list":["post-6720","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-creatine-kinase","tag-gene-therapy","tag-genethon","tag-gnt0004","tag-gnt0004-gene-therapy","tag-nsaa"],"subtitle":"Genethon\u516c\u53f8\u62a5\u544a\u79f0\uff0c\u5176\u5728\u7814\u57fa\u56e0\u7597\u6cd5GNT0004\u5728\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u4e2d\u53d6\u5f97\u4e86\u4ee4\u4eba\u9f13\u821e\u7684\u4e24\u5e74\u7597\u6548\u3002\u8be5\u7597\u6cd5\u663e\u793a\uff0c\u60a3\u8005\u7684NSAA\u8fd0\u52a8\u8bc4\u5206\u6301\u7eed\u6539\u5584\uff0c\u808c\u9178\u6fc0\u9176\uff08CK\uff09\u6c34\u5e73\u663e\u8457\u964d\u4f4e\uff0c\u8868\u660e\u5176\u53ef\u80fd\u5ef6\u7f13\u75be\u75c5\u8fdb\u5c55\u3002.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/6720","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=6720"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/6720\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/6722"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=6720"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=6720"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=6720"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}