{"id":6701,"date":"2026-03-09T18:17:40","date_gmt":"2026-03-09T15:17:40","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6701"},"modified":"2026-03-09T18:34:31","modified_gmt":"2026-03-09T15:34:31","slug":"vamorolone-agamree-in-dmd-real-world-experience","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/vamorolone-agamree-in-dmd-real-world-experience\/","title":{"rendered":"Vamorolone\uff08Agamree\uff09\u5728DMD\u4e2d\u7684\u5e94\u7528\uff1a\u771f\u5b9e\u4e16\u754c\u4f53\u9a8c"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Santhera Pharmaceuticals\u5ba3\u5e03\uff0c\u5728\u4f5b\u7f57\u91cc\u8fbe\u5dde\u5965\u5170\u591a\u4e3e\u884c\u76842026\u5e74\u808c\u8089\u840e\u7f29\u75c7\u534f\u4f1a\uff08MDA\uff09\u4e34\u5e8a\u4e0e\u79d1\u5b66\u5927\u4f1a\u4e0a\uff0c\u516c\u5e03\u4e86AGAMREE\uff08vamorolone\uff09\u6b63\u5728\u8fdb\u884c\u7684GUARDIAN\u7814\u7a76\u7684\u957f\u671f\u771f\u5b9e\u4e16\u754c\u5bf9\u6bd4\u5206\u6790\u7684\u5b8c\u6574\u7ed3\u679c\uff0c\u5176\u4e2d\u5305\u62ec\u57fa\u7ebf\u6570\u636e\u3002\u4e86\u89e3\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/what-is-agamree-vamorolone-what-is-agamree-used-for\/\" data-type=\"post\" data-id=\"2333\">\u4ec0\u4e48\u662f Agamree (Vamorolone)\uff1f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u6570\u636e\u96c6\u5305\u542b\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u7537\u5b69\u63a5\u53d7 AGAMREE \u6cbb\u7597\u957f\u8fbe\u516b\u5e74\uff08\u4e2d\u4f4d\u6570\u4e3a\u4e94\u5e74\uff09\u7684\u6570\u636e\u3002\u5206\u6790\u7eb3\u5165\u4e86\u901a\u8fc7\u5404\u79cd\u51c6\u5165\u9879\u76ee\u7ee7\u7eed\u63a5\u53d7\u6cbb\u7597\u7684\u4e34\u5e8a\u7814\u7a76\u53c2\u4e0e\u8005\u7684\u6570\u636e\uff0c\u4ee5\u53ca GUARDIAN \u56db\u671f\u7814\u7a76 (NCT06713135) \u7684\u6570\u636e\u3002\u5c06\u5305\u62ec GUARDIAN \u7814\u7a76\u57fa\u7ebf\u7ed3\u679c\u5728\u5185\u7684\u957f\u671f\u6570\u636e\u4e0e\u63a5\u53d7\u5730\u592b\u53ef\u7279\u6216\u6cfc\u5c3c\u677e\u6cbb\u7597\u7684\u503e\u5411\u6027\u5339\u914d\u7684\u5386\u53f2\u5bf9\u7167\u961f\u5217\u8fdb\u884c\u4e86\u6bd4\u8f83\u3002<a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06713135\" target=\"_blank\" rel=\"noreferrer noopener\">NCT06713135<\/a>)<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u7efc\u5408\u6570\u636e\u8868\u660e\uff0cvamorolone \u80fd\u591f\u7ef4\u6301\u4e0e\u4f20\u7edf\u76ae\u8d28\u7c7b\u56fa\u9187\u76f8\u5f53\u7684\u957f\u671f\u7597\u6548\uff0c\u540c\u65f6\u63d0\u9ad8\u8010\u53d7\u6027\uff0c\u5e76\u663e\u8457\u51cf\u5c11\u4e0e\u7c7b\u56fa\u9187\u76f8\u5173\u7684\u5173\u952e\u526f\u4f5c\u7528\uff0c\u8fd9\u4e9b\u526f\u4f5c\u7528\u901a\u5e38\u4f1a\u5bfc\u81f4\u5242\u91cf\u51cf\u5c11\u6216\u505c\u836f\uff0c\u4ece\u800c\u5f71\u54cd\u60a3\u8005\u7684\u957f\u671f\u7597\u6548\u3002\u4e86\u89e3\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/pros-and-cons-of-steroids-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" data-type=\"post\" data-id=\"6244\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u4f7f\u7528\u7c7b\u56fa\u9187\uff08\u53ef\u7684\u677e\uff09\u7684\u5229\u5f0a\u662f\u4ec0\u4e48\uff1f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5173\u6ce8\u6b64\u9875\u9762<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u6240\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Santhera Pharmaceuticals announced that full results from long-term real-world comparative analyses, including baseline data from the ongoing GUARDIAN study of AGAMREE (vamorolone), were presented at the Muscular Dystrophy Association (MDA) Clinical &amp; Scientific Conference 2026 in Orlando, Florida. Learn More: What is Agamree (Vamorolone)? The dataset includes up to eight years of AGAMREE exposure (median [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6703,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[42,41,43],"class_list":["post-6701","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-agamree","tag-santhera","tag-vamorolone"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/6701","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=6701"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/6701\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/6703"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=6701"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=6701"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=6701"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}