{"id":6207,"date":"2026-02-12T16:04:10","date_gmt":"2026-02-12T13:04:10","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6207"},"modified":"2026-02-12T16:11:13","modified_gmt":"2026-02-12T13:11:13","slug":"satellos-first-participant-dosed-in-phase-2-study-of-sat-3247-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/satellos-first-participant-dosed-in-phase-2-study-of-sat-3247-duchenne-muscular-dystrophy\/","title":{"rendered":"Satellos\u516c\u53f8\u5ba3\u5e03\uff0c\u9996\u4f4d\u53d7\u8bd5\u8005\u5df2\u5728\u9488\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684SAT-3247\u836f\u7269\u76842\u671f\u513f\u79d1\u7814\u7a76\u4e2d\u63a5\u53d7\u7ed9\u836f\u3002"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Satellos Bioscience \u5ba3\u5e03\uff0cBASECAMP \u7684\u9996\u4f4d\u53c2\u4e0e\u8005\u5df2\u63a5\u53d7\u7ed9\u836f\u3002BASECAMP \u662f\u4e00\u9879\u4e3a\u671f\u4e09\u4e2a\u6708\u7684\u968f\u673a\u3001\u53cc\u76f2\u3001\u5b89\u6170\u5242\u5bf9\u7167\u3001\u6982\u5ff5\u9a8c\u8bc1\u7684 2 \u671f\u513f\u79d1\u7814\u7a76\uff0c\u65e8\u5728\u8bc4\u4f30 SAT-3247 \u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08\u201c\u675c\u6c0f\u201d\u6216\u201cDMD\u201d\uff09\u7684\u7597\u6548\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u672c\u7814\u7a76\u5c06\u8bc4\u4f30 SAT-3247 \u5bf9 51 \u540d\u5e74\u9f84\u5728 7\u30018 \u6216 9 \u5c81\u4e4b\u95f4\u3001\u80fd\u591f\u72ec\u7acb\u884c\u8d70\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u513f\u7ae5\u7684\u7597\u6548\u3002\u4e3b\u8981\u7ec8\u70b9\u5305\u62ec\u5b89\u5168\u6027\u3001\u8010\u53d7\u6027\u548c\u5bf9\u808c\u8089\u529b\u91cf\u7684\u5f71\u54cd\u3002\u6b21\u8981\u7ec8\u70b9\u5c06\u8bc4\u4f30 SAT-3247 \u5bf9\u808c\u8089\u8d28\u91cf\u3001\u529f\u80fd\u548c\u518d\u751f\u80fd\u529b\u7684\u5f71\u54cd\u3002. <strong>\u4e86\u89e3\u66f4\u591a\uff1a<\/strong> <a href=\"https:\/\/dmdwarrior.com\/zh\/potential-of-sat-3247-to-restore-muscle-regeneration-in-duchenne-published-in-nature\/\" target=\"_blank\" rel=\"noreferrer noopener\">SAT-3247 \u5177\u6709\u6062\u590d\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u808c\u8089\u518d\u751f\u7684\u6f5c\u529b\uff0c\u76f8\u5173\u7814\u7a76\u53d1\u8868\u4e8e\u300a\u81ea\u7136\u300b\u6742\u5fd7\u3002<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201cBASECAMP\u8bd5\u9a8c\u65e8\u5728\u4f5c\u4e3a\u4e00\u9879\u6f5c\u5728\u7684\u5173\u952e\u6027\u8bd5\u9a8c\uff0c\u6807\u5fd7\u7740Satellos\u5728\u8bc4\u4f30SAT-3247\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u513f\u7684\u6f5c\u529b\u65b9\u9762\u8fc8\u51fa\u4e86\u91cd\u8981\u4e00\u6b65\uff0c\u201dSatellos\u8054\u5408\u521b\u59cb\u4eba\u517c\u9996\u5e2d\u6267\u884c\u5b98\u5f17\u5170\u514b\u00b7\u683c\u91cc\u68ee\u8868\u793a\u3002\u201cBASECAMP\u8bd5\u9a8c\u4ea7\u751f\u7684\u6570\u636e\u53ef\u80fd\u5728\u52a0\u901fSAT-3247\u4f5c\u4e3a\u8be5\u75be\u75c5\u65b0\u578b\u7597\u6cd5\u7684\u5f00\u53d1\u8fc7\u7a0b\u4e2d\u53d1\u6325\u91cd\u8981\u4f5c\u7528\u3002\u201d<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">SAT-3247\u4e34\u5e8a\u8bd5\u9a8c\u5c06\u5728\u54ea\u4e9b\u56fd\u5bb6\u5f00\u59cb\uff1f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>BASECAMP \u8bd5\u9a8c\u6b63\u5728\u79ef\u6781\u62db\u52df\u53d7\u8bd5\u8005\uff0cSatellos \u8ba1\u5212\u5728\u7f8e\u56fd\u3001\u6b27\u6d32\u3001\u82f1\u56fd\u3001\u6fb3\u5927\u5229\u4e9a\u3001\u52a0\u62ff\u5927\u548c\u585e\u5c14\u7ef4\u4e9a\u7684\u4e34\u5e8a\u4e2d\u5fc3\u8bbe\u7acb 25 \u4e2a\u7814\u7a76\u5730\u70b9\u3002.<\/strong> \u9605\u8bfb\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/how-to-participate-in-clinical-trials-for-duchenne\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u6211\u7684\u5b69\u5b50\u5982\u4f55\u53c2\u52a0\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c\uff1f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201cBASECAMP \u5c06\u91cd\u70b9\u5173\u6ce8\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e00\u4e2a\u91cd\u8981\u65f6\u671f\uff0c\u5373\u808c\u8089\u5065\u5eb7\u548c\u529f\u80fd\u5f00\u59cb\u5feb\u901f\u4e0b\u964d\u7684\u65f6\u671f\uff0c\u201dSatellos \u9996\u5e2d\u533b\u7597\u5b98 Wildon Farwell \u533b\u5b66\u535a\u58eb\u8868\u793a\uff0c\u201c\u5bf9\u4e8e\u8fd9\u79cd\u6bc1\u706d\u6027\u75be\u75c5\uff0c\u6cbb\u7597\u9009\u62e9\u4ecd\u7136\u6709\u9650\uff0c\u8fd9\u9879\u7814\u7a76\u5c06\u8bc4\u4f30\u4e00\u79cd\u53ef\u80fd\u589e\u52a0\u808c\u8089\u518d\u751f\u5e76\u6539\u5584\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u513f\u529f\u80fd\u7684\u65b0\u65b9\u6cd5\u3002\u201d<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u4ec0\u4e48\u662f SAT-3247\uff1f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">SAT-3247 \u662f\u4e00\u79cd\u4e13\u6709\u7684\u53e3\u670d\u5c0f\u5206\u5b50\u836f\u7269\uff0c\u7531 Satellos \u516c\u53f8\u5f00\u53d1\uff0c\u65e8\u5728\u4e3a\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u53ca\u5176\u4ed6\u9000\u884c\u6027\u6216\u635f\u4f24\u6027\u75be\u75c5\u4e2d\u53d7\u635f\u7684\u9aa8\u9abc\u808c\u518d\u751f\u63d0\u4f9b\u4e00\u79cd\u65b0\u578b\u7597\u6cd5\u3002Satellos \u516c\u53f8\u6b63\u81f4\u529b\u4e8e\u63a8\u8fdb SAT-3247 \u7684\u7814\u53d1\uff0c\u4f7f\u5176\u6210\u4e3a\u4e00\u79cd\u6f5c\u5728\u7684 DMD \u6cbb\u7597\u65b9\u6cd5\uff0c\u5176\u7597\u6548\u72ec\u7acb\u4e8e\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\uff0c\u4e14\u4e0d\u53d7\u5916\u663e\u5b50\u7a81\u53d8\u72b6\u6001\u7684\u5f71\u54cd\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5173\u6ce8\u6b64\u9875\u9762<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u6240\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Satellos Bioscience announced that the first participant has been dosed in BASECAMP, a three-month, randomized, double-blind, placebo-controlled, proof-of-concept, Phase 2 pediatric study of SAT-3247 for Duchenne muscular dystrophy (\u201cDuchenne\u201d or \u201cDMD\u201d). The study will evaluate SAT-3247 in 51 ambulatory children with DMD aged 7, 8 or 9 years of age. Primary endpoints include safety, tolerability [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6208,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[303,137,242,254,251,252,253],"class_list":["post-6207","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-cell-therapy","tag-clinical-trial","tag-clinical-trials","tag-frank-gleeson","tag-sat-3247","tag-satellos","tag-satellos-bioscience"],"subtitle":"BASECAMP \u662f\u4e00\u9879\u4e3a\u671f\u4e09\u4e2a\u6708\u7684\u968f\u673a\u3001\u53cc\u76f2\u3001\u5b89\u6170\u5242\u5bf9\u7167\u7814\u7a76\uff0c\u65e8\u5728\u8bc4\u4f30 SAT-3247 \u7684\u5b89\u5168\u6027\u548c\u8010\u53d7\u6027\uff0c\u4ee5\u53ca\u5176\u5bf9\u808c\u8089\u529b\u91cf\u3001\u808c\u8089\u8d28\u91cf\u548c\u808c\u8089\u518d\u751f\u7684\u5f71\u54cd\u3002","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/6207","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=6207"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/6207\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/6208"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=6207"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=6207"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=6207"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}