{"id":5378,"date":"2025-12-17T22:22:32","date_gmt":"2025-12-17T19:22:32","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=5378"},"modified":"2025-12-17T22:33:23","modified_gmt":"2025-12-17T19:33:23","slug":"satellos-sat-3247-phase-2-basecamp-clinical-trial-nct07287189","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/satellos-sat-3247-phase-2-basecamp-clinical-trial-nct07287189\/","title":{"rendered":"Satellos\u516c\u53f8\u5ba3\u5e03\u542f\u52a8\u9488\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u95e8\u8bca\u60a3\u8005\u7684SAT-3247\u836f\u7269\u76842A\u671f\uff08BASECAMP\uff09\u7814\u7a76\u3002"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Satellos\u516c\u53f8\u5ba3\u5e03\u542f\u52a8\u4e00\u9879\u9488\u5bf97\u81f310\u5c81\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u95e8\u8bca\u60a3\u8005\u7684SAT-3247\uff08NCT07287189\uff09\u7684IIA\u671f\u4e34\u5e8a\u8bd5\u9a8c\u3002\u8be5\u8bd5\u9a8c\u5c06\u91c7\u7528\u968f\u673a\u3001\u53cc\u76f2\u3001\u5b89\u6170\u5242\u5bf9\u7167\u3001\u5468\u5185\u7ed9\u836f\u65b9\u6848\uff0c\u572812\u5468\u5185\u7814\u7a76\u4e24\u79cd\u5242\u91cf\u7684SAT-3247\uff0c\u4ee5\u786e\u5b9a\u6700\u4f73\u5242\u91cf\u3001\u5b89\u5168\u6027\u3001\u8010\u53d7\u6027\u548c\u521d\u6b65\u7597\u6548\u3002. <strong>\u4e86\u89e3\u66f4\u591a<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/zh\/satellos-receives-fda-and-international-clearance-to-commence-pediatric-phase-2-testing-of-sat-3247-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Satellos \u83b7\u5f97 FDA \u548c\u56fd\u9645\u6279\u51c6\uff0c\u5f00\u59cb\u5bf9 SAT-3247 \u8fdb\u884c\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u513f\u79d1 II \u671f\u8bd5\u9a8c<\/a><\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u76ee\u5f55<\/h2><nav><ul><li><a href=\"#what-is-sat-3247-phase-2-a-clinical-trial\">SAT-3247 2A\u671f\u4e34\u5e8a\u8bd5\u9a8c\u662f\u4ec0\u4e48\uff1f<\/a><\/li><li><a href=\"#rag-18-sa-rna-early-phase-1-nct-07282652\">SAT-3247 2A \u76f8 \u2013 NCT07287189<\/a><\/li><li><a href=\"#how-to-participate-in-the-wve-n-531-clinical-trial\">\u5982\u4f55\u53c2\u4e0e SAT-3247 IIA \u671f\u4e34\u5e8a\u8bd5\u9a8c<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-is-sat-3247-phase-2-a-clinical-trial\">SAT-3247 2A\u671f\u4e34\u5e8a\u8bd5\u9a8c\u662f\u4ec0\u4e48\uff1f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u662f\u4e00\u9879\u9488\u5bf97\u5c81\u81f310\u5c81\u53ef\u72ec\u7acb\u884c\u8d70\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u60a3\u8005\u7684\u5168\u7403\u6027IIa\u671f\u4e34\u5e8a\u8bd5\u9a8c\uff0c\u7814\u7a76\u836f\u7269SAT-3247\u3002\u8be5\u8bd5\u9a8c\u5c06\u91c7\u7528\u968f\u673a\u3001\u53cc\u76f2\u3001\u5b89\u6170\u5242\u5bf9\u7167\u7684\u5e73\u65e5\u7ed9\u836f\u65b9\u6848\uff0c\u4e3a\u671f12\u5468\uff0c\u7814\u7a76\u4e24\u79cd\u5242\u91cf\u7684SAT-3247\uff0c\u4ee5\u786e\u5b9a\u6700\u4f73\u5242\u91cf\u3001\u5b89\u5168\u6027\u3001\u8010\u53d7\u6027\u548c\u521d\u6b65\u7597\u6548\u3002\u5176\u4e2d\uff0c\u7f8e\u56fd\u548c\u52a0\u62ff\u5927\u5c06\u7814\u7a76\u4e00\u79cd\u5242\u91cf\u7684SAT-3247\u548c\u5b89\u6170\u5242\uff1b\u82f1\u56fd\u3001\u6b27\u76df\u3001\u585e\u5c14\u7ef4\u4e9a\u548c\u6fb3\u5927\u5229\u4e9a\u5c06\u7814\u7a76\u4e24\u79cd\u5242\u91cf\u7684SAT-3247\u548c\u5b89\u6170\u5242\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8ba1\u5212\u5728\u5168\u7403\u8303\u56f4\u5185\u62db\u52df\u81f3\u591a 51 \u540d\u5e74\u9f84\u5728 7 \u5c81\u81f3 10 \u5c81\u4e4b\u95f4\u7684\u53ef\u72ec\u7acb\u884c\u8d70\u7684 DMD \u60a3\u8005\u3002\u968f\u673a\u5206\u7ec4\u5c06\u6839\u636e\u57fa\u7ebf\u76ae\u8d28\u7c7b\u56fa\u9187\u6cbb\u7597\u65b9\u6848\u548c\u65e2\u5f80 DMD \u4f34\u968f\u7528\u836f\u60c5\u51b5\u8fdb\u884c\u5206\u5c42\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u6bcf\u4f4d\u53c2\u4e0e\u8005\u5c06\u6bcf\u5929\u63a5\u53d7\u4e00\u6b21 SAT-3247 \u6216\u5339\u914d\u7684\u5b89\u6170\u5242\uff0c\u6301\u7eed 12 \u5468\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u53d7\u8bd5\u8005\u5c06\u5728\u5f00\u59cb\u63a5\u53d7\u7814\u7a76\u836f\u7269\u57fa\u7ebf\u7ed9\u836f\u524d 28 \u5929\u5185\u63a5\u53d7\u7b5b\u9009\u3002\u7b5b\u9009\u671f\u7ed3\u675f\u540e\uff0c\u53d7\u8bd5\u8005\u5c06\u5b8c\u6210\u57fa\u7ebf\u8bbf\u89c6\uff08\u8bbf\u89c6 2\uff09\u3001\u7b2c 1 \u5468\u7684\u968f\u8bbf\u7535\u8bdd\uff0c\u4ee5\u53ca\u7b2c 4 \u5468\uff08\u8bbf\u89c6 3\uff09\u3001\u7b2c 8 \u5468\uff08\u8bbf\u89c6 4\uff09\u548c\u7b2c 12 \u5468\uff08\u8bbf\u89c6 5\uff09\u7684\u8bbf\u89c6\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"rag-18-sa-rna-early-phase-1-nct-07282652\">SAT-3247 2A \u76f8 \u2013 NCT07287189<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u4e00\u9879\u9488\u5bf9\u53ef\u6d3b\u52a8 DMD \u60a3\u8005\u7684\u53e3\u670d SAT-3247 \u7684 2a \u671f\u968f\u673a\u3001\u53cc\u76f2\u3001\u5b89\u6170\u5242\u5bf9\u7167\u5242\u91cf\u6bd4\u8f83\u548c\u63a2\u7d22\u6027\u7597\u6548\u7814\u7a76\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong><strong>\u5b66\u4e60\u5f00\u59cb\u65f6\u95f4\uff08\u5b9e\u9645\uff09<\/strong><\/strong>: 2025-12-08<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5c0f\u5b66\u5b8c\u6210\u60c5\u51b5\uff08\u9884\u8ba1\uff09<\/strong>: 2026-03-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7814\u7a76\u5b8c\u6210\u60c5\u51b5\uff08\u9884\u8ba1\uff09<\/strong>: 2026-06-30<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u53c2\u4e0e\u4eba\u6570\uff08\u9884\u8ba1\uff09<\/strong>: 51<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5b66\u4e60\u7c7b\u578b<\/strong>\uff1a\u4ecb\u5165<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5730\u70b9<\/strong>\u7f8e\u56fd\u3001\u6fb3\u5927\u5229\u4e9a\u3001\u52a0\u62ff\u5927\u3001\u585e\u5c14\u7ef4\u4e9a\u3001\u82f1\u56fd<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9002\u5408\u5b66\u4e60\u7684\u5e74\u9f84<\/strong>7\u5c81\u81f39\u5c81\uff08\u7537\u7ae5\uff09<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4e3b\u8981\u7eb3\u5165\u548c\u6392\u9664\u6807\u51c6\u3002\u2013\u00a0<a href=\"https:\/\/clinicaltrials.gov\/study\/NCT07287189\" target=\"_blank\" rel=\"noreferrer noopener\">NCT07287189<\/a>\u00a0\u2013<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"how-to-participate-in-the-wve-n-531-clinical-trial\">\u5982\u4f55\u53c2\u4e0e SAT-3247 IIA \u671f\u4e34\u5e8a\u8bd5\u9a8c<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u8981\u53c2\u4e0e SAT-3247 2A \u671f\u4e34\u5e8a\u8bd5\u9a8c\uff0c\u60a8\u53ef\u4ee5\u4f7f\u7528\u4ee5\u4e0b\u8054\u7cfb\u4fe1\u606f\u3002.\u00a0<strong>\u4e86\u89e3\u66f4\u591a<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/zh\/how-to-participate-in-clinical-trials-for-duchenne\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u5982\u4f55\u53c2\u52a0\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u4e34\u5e8a\u8bd5\u9a8c\uff1f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u6211\u4eec\u5c06\u516c\u5e03\u80fd\u591f\u56de\u7b54\u6709\u5173\u53c2\u4e0e\u7814\u7a76\u7684\u95ee\u9898\u7684\u4e2a\u4eba\u7684\u8054\u7cfb\u65b9\u5f0f\uff0c\u4ee5\u53ca\u6709\u5173\u7814\u7a76\u8fdb\u884c\u5730\u70b9\u7684\u4fe1\u606f\u3002.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a<\/strong>:&nbsp;<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c\uff08\u6240\u6709\u7814\u7a76\u5217\u8868\uff09<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Satellos announced the commencement of a Phase 2A trial of SAT-3247 (NCT07287189) in ambulatory patients with Duchenne aged 7 to 10 years. In this trial, two doses of SAT-3247 will be studied over 12 weeks in a randomized, double-blind, placebo-controlled, intraweek regimen to determine the optimal dose, safety, tolerance, and preliminary efficacy. Learn More: Satellos [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":5381,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[171,303,137,242,470,251,252,253],"class_list":["post-5378","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-canada","tag-cell-therapy","tag-clinical-trial","tag-clinical-trials","tag-nct07287189","tag-sat-3247","tag-satellos","tag-satellos-bioscience"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/5378","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=5378"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/5378\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/5381"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=5378"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=5378"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=5378"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}