{"id":4964,"date":"2025-10-30T15:41:35","date_gmt":"2025-10-30T12:41:35","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4964"},"modified":"2025-11-03T19:56:20","modified_gmt":"2025-11-03T16:56:20","slug":"regenxbio-announces-completion-pivotal-enrollment-and-initiates","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/regenxbio-announces-completion-pivotal-enrollment-and-initiates\/","title":{"rendered":"REGENXBIO\u5ba3\u5e03RGX-202\u5173\u952e\u6027\u60a3\u8005\u62db\u52df\u5b8c\u6210\uff0c\u5e76\u542f\u52a8\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u57fa\u56e0\u6cbb\u7597\u9879\u76ee\u7684\u5546\u4e1a\u5316\u751f\u4ea7\u3002"},"content":{"rendered":"<p class=\"wp-block-paragraph\">REGENXBIO \u5ba3\u5e03\u5df2\u5b8c\u6210 RGX-202\uff08\u4e00\u79cd\u7528\u4e8e\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u5728\u7814\u57fa\u56e0\u7597\u6cd5\uff09\u7684 AFFINITY DUCHENNE \u5173\u952e\u6027\u8bd5\u9a8c\u7684\u60a3\u8005\u62db\u52df\uff0c\u5e76\u6210\u529f\u751f\u4ea7\u4e86\u9996\u6279\u7528\u4e8e\u5546\u4e1a\u4f9b\u5e94\u7684\u4ea7\u54c1\u3002. <strong>\u9605\u8bfb\u66f4\u591a<\/strong>: <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT05693142\" target=\"_blank\" rel=\"noreferrer noopener\">NCT05693142<\/a>.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7fa4\u4f53\u8feb\u5207\u9700\u8981\u65b0\u7684\u6cbb\u7597\u65b9\u6848\uff0c\u8fd9\u4e9b\u65b9\u6848\u80fd\u591f\u63d0\u4f9b\u6301\u4e45\u3001\u5b89\u5168\u7684\u7597\u6548\uff0c\u5e76\u80fd\u5207\u5b9e\u6539\u53d8\u8fd9\u79cd\u9000\u884c\u6027\u75be\u75c5\u7684\u8fdb\u7a0b\u3002. <strong>REGENXBIO \u603b\u88c1\u517c\u9996\u5e2d\u6267\u884c\u5b98 Curran Simpson \u8868\u793a\uff1a\u201d\u5b8c\u6210\u8fd9\u4e00\u5173\u952e\u6027\u8bd5\u9a8c\u91cc\u7a0b\u7891\u5e76\u81ea\u4e3b\u751f\u4ea7\u9996\u6279\u7528\u4e8e\u5546\u4e1a\u7528\u9014\u7684\u5242\u91cf\uff0c\u4f7f\u6211\u4eec\u79bb\u5c06 RGX-202 \u63a8\u5411\u5e02\u573a\u66f4\u8fd1\u4e86\u4e00\u6b65\uff0c\u4f7f\u5176\u6210\u4e3a\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\uff08\u6cbb\u7597\u9009\u62e9\u6709\u9650\uff09\u6f5c\u5728\u7684\u6700\u4f73\u57fa\u56e0\u7597\u6cd5\u3002\u201d.<\/strong> \u201cRGX-202 \u80cc\u540e\u7684\u5dee\u5f02\u5316\u6cbb\u7597\u65b9\u6cd5\uff0c\u5305\u62ec\u6211\u4eec\u884c\u4e1a\u9886\u5148\u7684\u4ea7\u54c1\u7eaf\u5ea6\u6c34\u5e73\u548c\u5e26\u6709 C \u7aef\u7ed3\u6784\u57df\u7684\u65b0\u578b\u7ed3\u6784\uff0c\u5df2\u7ecf\u53d6\u5f97\u4e86\u79ef\u6781\u7684\u5b89\u5168\u6027\u548c\u6709\u6548\u6027\uff0c\u5e76\u5728 I\/II \u671f\u4e34\u5e8a\u8bd5\u9a8c\u4e2d\u89c2\u5bdf\u5230\u4e86\u6301\u7eed\u7684\u529f\u80fd\u6027\u83b7\u76ca\u3002. <strong>\u9274\u4e8e\u8fd9\u4e9b\u4ee4\u4eba\u9f13\u821e\u7684\u7ed3\u679c\uff0c\u6211\u4eec\u81f4\u529b\u4e8e\u6269\u5927\u5546\u4e1a\u4f9b\u5e94\uff0c\u5e76\u5c06\u5728\u660e\u5e74\u7b2c\u4e8c\u5b63\u5ea6\u521d\u5206\u4eab\u5173\u952e\u6570\u636e\u3002\u201d<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e86\u89e3\u66f4\u591a<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/zh\/rgx-202-gene-therapy-phase-3-clinical-trial-nct05693142\/\">RGX-202\u57fa\u56e0\u7597\u6cd53\u671f\u4e34\u5e8a\u8bd5\u9a8c\u5f00\u59cb<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">RGX-202 \u7684\u4e3b\u8981\u7ed3\u679c<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u5728 AFFINITY DUCHENNE \u8bd5\u9a8c\u7684 I\/II \u671f\u90e8\u5206\u4e2d\uff0c\u63a5\u53d7 RGX-202 \u6cbb\u7597\u7684\u60a3\u8005\u4e0e\u81ea\u7136\u75c5\u7a0b\u76f8\u6bd4\uff0c\u8868\u73b0\u51fa\u6301\u7eed\u3001\u663e\u8457\u7684\u5fae\u578b\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u8868\u8fbe\u548c\u529f\u80fd\u6539\u5584\uff0c\u8fd9\u652f\u6301\u4e86\u901a\u8fc7\u52a0\u901f\u5ba1\u6279\u9014\u5f84\u83b7\u5f97\u6279\u51c6\u7684\u53ef\u80fd\u6027\u3002<\/li>\n\n\n\n<li>REGENXBIO \u7ee7\u7eed\u62db\u52df\u60a3\u8005\u53c2\u4e0e\u9a8c\u8bc1\u6027\u8bd5\u9a8c<\/li>\n\n\n\n<li>\u9996\u6279\u7528\u4e8e\u5546\u4e1a\u4f9b\u5e94\u7684\u6279\u6b21\u4ea7\u54c1\u7531\u516c\u53f8\u5185\u90e8\u5236\u9020\u521b\u65b0\u4e2d\u5fc3\u751f\u4ea7\u3002\n<ul class=\"wp-block-list\">\n<li>\u6bcf\u5e74\u6700\u591a\u53ef\u751f\u4ea7 2,500 \u5242 RGX-202<\/li>\n<\/ul>\n<\/li>\n\n\n\n<li>\u9884\u8ba1\u5c06\u4e8e 2026 \u5e74\u7b2c\u4e8c\u5b63\u5ea6\u521d\u516c\u5e03\u5173\u952e\u6027\u6570\u636e\uff0c\u5e76\u4e8e 2026 \u5e74\u5e74\u4e2d\u63d0\u4ea4\u751f\u7269\u5236\u54c1\u8bb8\u53ef\u7533\u8bf7 (BLA)\u3002<\/li>\n<\/ul>\n\n\n\n<h2 class=\"wp-block-heading\">RGX-202 \u4f5c\u7528\u673a\u5236<\/h2>\n\n\n\n<figure class=\"wp-block-embed is-type-video is-provider-vimeo wp-block-embed-vimeo\"><div class=\"wp-block-embed__wrapper\">\n<iframe loading=\"lazy\" title=\"\u6700\u7ec8\u60a3\u8005\u89c6\u9891 2025\u5e745\u670821\u65e5 (1080p)\" src=\"https:\/\/player.vimeo.com\/video\/1092247292?dnt=1&amp;app_id=122963\" width=\"696\" height=\"392\" frameborder=\"0\" allow=\"autoplay; fullscreen; picture-in-picture; clipboard-write; encrypted-media; web-share\" referrerpolicy=\"strict-origin-when-cross-origin\"><\/iframe>\n<\/div><\/figure>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c\uff08\u6240\u6709\u7814\u7a76\u5217\u8868\uff09<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>REGENXBIO announced the completion of enrollment in the AFFINITY DUCHENNE pivotal trial of RGX-202, an investigational gene therapy for the treatment of Duchenne muscular dystrophy, as well as the successful production of the first batches intended for commercial supply. Read More: NCT05693142. &#8220;The Duchenne community urgently needs new treatment options that provide durable, safe outcomes [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4965,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[61,107,108],"class_list":["post-4964","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-gene-therapy","tag-regenxbio","tag-rgx-202"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4964","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=4964"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4964\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/4965"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=4964"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=4964"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=4964"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}