{"id":4959,"date":"2025-11-01T15:17:45","date_gmt":"2025-11-01T12:17:45","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4959"},"modified":"2025-11-03T14:12:47","modified_gmt":"2025-11-03T11:12:47","slug":"north-star-ambulatory-assessment-nsaa-in-duchenne-dmd","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/","title":{"rendered":"\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u7684\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30 (NSAA)"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30 (NSAA) \u662f\u4e00\u79cd\u6807\u51c6\u5316\u7684\u3001\u7531\u4e34\u5e8a\u533b\u751f\u7ba1\u7406\u7684\u5de5\u5177\uff0c\u65e8\u5728\u8bc4\u4f30\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u7684\u53ef\u884c\u8d70\u7537\u5b69\u7684\u8fd0\u52a8\u8868\u73b0\u3002.<\/strong> \u8be5\u5de5\u5177\u7531\u5317\u6781\u661f\u795e\u7ecf\u808c\u8089\u75be\u75c5\u4e34\u5e8a\u7f51\u7edc\u5f00\u53d1\uff0c\u4e3a\u5728\u4e34\u5e8a\u5b9e\u8df5\u548c\u7814\u7a76\u73af\u5883\u4e2d\u8ddf\u8e2a\u75be\u75c5\u8fdb\u5c55\u548c\u8bc4\u4f30\u6cbb\u7597\u7ed3\u679c\u63d0\u4f9b\u4e86\u4e00\u79cd\u53ef\u9760\u7684\u65b9\u6cd5\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u662f\u4e00\u79cd\u8fdb\u884c\u6027\u795e\u7ecf\u808c\u8089\u75be\u75c5\uff0c\u7531DMD\u57fa\u56e0\u7a81\u53d8\u5f15\u8d77\uff0c\u5bfc\u81f4\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\uff08\u4e00\u79cd\u5bf9\u808c\u8089\u7a33\u5b9a\u6027\u81f3\u5173\u91cd\u8981\u7684\u86cb\u767d\u8d28\uff09\u7f3a\u5931\u3002\u968f\u7740\u65f6\u95f4\u7684\u63a8\u79fb\uff0c\u8fd9\u4f1a\u5bfc\u81f4\u808c\u8089\u65e0\u529b\u3001\u4e27\u5931\u884c\u8d70\u80fd\u529b\u548c\u529f\u80fd\u8870\u9000\u3002. <strong>\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\u901a\u8fc7\u4e00\u7cfb\u5217\u53ef\u6d4b\u91cf\u7684\u8fd0\u52a8\u4efb\u52a1\u6765\u91cf\u5316\u8fd9\u4e00\u8fdb\u5c55\u3002.<\/strong><\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u76ee\u5f55<\/h2><nav><ul><li><a href=\"#purpose-and-importance-of-the-nsaa-in-dmd\">NSAA\u5728DMD\u4e2d\u7684\u76ee\u7684\u548c\u91cd\u8981\u6027<\/a><\/li><li><a href=\"#structure-and-scoring-of-the-nsaa\">NSAA\u7684\u7ed3\u6784\u548c\u8bc4\u5206<\/a><\/li><li><a href=\"#nsaa-assessed-skills\">NSAA\u8bc4\u4f30\u6280\u80fd<\/a><\/li><li><a href=\"#interpreting-nsaa-scores\">NSAA\u8bc4\u5206\u89e3\u8bfb<\/a><\/li><li><a href=\"#use-of-the-nsaa-in-clinical-trials\">NSAA\u5728\u4e34\u5e8a\u8bd5\u9a8c\u4e2d\u7684\u5e94\u7528<\/a><\/li><li><a href=\"#limitations-of-the-nsaa\">NSAA\u7684\u5c40\u9650\u6027<\/a><\/li><li><a href=\"#most-common-question-about-north-star-ambulatory-assessment-nsaa\">\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\uff1a\u95ee\u7b54<\/a><ul><li><a href=\"#faq-question-1761824999344\">\u4ec0\u4e48\u662f\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825035673\">\u4e3a\u4ec0\u4e48\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u4f1a\u4f7f\u7528NSAA\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825143662\">\u8c01\u53ef\u4ee5\u8fdb\u884cNSAA\u6d4b\u8bd5\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825159756\">NSAA\u662f\u5982\u4f55\u8bc4\u5206\u7684\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825213163\">\u5b8c\u6210NSAA\u9700\u8981\u591a\u957f\u65f6\u95f4\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825239921\">NSAA\u5177\u4f53\u8861\u91cf\u7684\u662f\u4ec0\u4e48\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825277811\">NSAA \u9002\u7528\u4e8e\u591a\u5927\u5e74\u9f84\u6bb5\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825294335\">NSAA \u5e94\u8be5\u591a\u4e45\u8fdb\u884c\u4e00\u6b21\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825309981\">NSAA\u662f\u5982\u4f55\u7528\u4e8e\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c\u7684\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825328456\">NSAA\u6709\u54ea\u4e9b\u5c40\u9650\u6027\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825354752\">\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u7537\u5b69\u5982\u679c\u4e27\u5931\u884c\u8d70\u80fd\u529b\u4f1a\u53d1\u751f\u4ec0\u4e48\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825371612\">NSAA\u80fd\u5426\u9884\u6d4bDMD\u60a3\u8005\u7684\u884c\u8d70\u80fd\u529b\u4e27\u5931\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825393528\">NSAA\u662f\u5426\u53ef\u9760\u4e14\u7ecf\u8fc7\u9a8c\u8bc1\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825415116\">\u5bb6\u957f\u5982\u4f55\u5e2e\u52a9\u5b69\u5b50\u51c6\u5907NSAA\u8003\u8bd5\uff1f<\/a><\/li><li><a href=\"#faq-question-1761825442589\">NSAA\u8868\u683c\u6216\u8bc4\u5206\u8868\u5728\u54ea\u91cc\u53ef\u4ee5\u627e\u5230\uff1f<\/a><\/li><\/ul><\/li><li><a href=\"#conclusion\">\u7ed3\u8bba<\/a><ul><li><a href=\"#key-takeaways\">\u8981\u70b9\u603b\u7ed3<\/a><\/li><\/ul><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"purpose-and-importance-of-the-nsaa-in-dmd\"><strong>NSAA\u5728DMD\u4e2d\u7684\u76ee\u7684\u548c\u91cd\u8981\u6027<\/strong><\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u5317\u6781\u661f\u52a8\u6001\u8bc4\u4f30\u5728\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u7ba1\u7406\u4e2d\u53d1\u6325\u7740\u51e0\u4e2a\u91cd\u8981\u4f5c\u7528\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u76d1\u6d4b\u75be\u75c5\u8fdb\u5c55\uff1a<\/strong> \u5b83\u4e3a\u4e34\u5e8a\u533b\u751f\u63d0\u4f9b\u4e86\u4e00\u79cd\u5ba2\u89c2\u7684\u8861\u91cf\u6807\u51c6\uff0c\u7528\u4e8e\u8bc4\u4f30\u529f\u80fd\u80fd\u529b\u968f\u65f6\u95f4\u7684\u53d8\u5316\u3002.<\/li>\n\n\n\n<li><strong>\u8bc4\u4f30\u6cbb\u7597\u6548\u679c\uff1a<\/strong> \u5b83\u5e7f\u6cdb\u7528\u4e8e\u4e34\u5e8a\u8bd5\u9a8c\u4e2d\uff0c\u4ee5\u8bc4\u4f30\u76ae\u8d28\u7c7b\u56fa\u9187\u3001\u5916\u663e\u5b50\u8df3\u8dc3\u836f\u7269\u6216\u57fa\u56e0\u7597\u6cd5\u7b49\u7597\u6cd5\u7684\u6548\u679c\u3002.<\/li>\n\n\n\n<li><strong>\u652f\u6301\u4e34\u5e8a\u51b3\u7b56\uff1a<\/strong> \u5b9a\u671f\u8fdb\u884c NSAA \u6d4b\u8bd5\u6709\u52a9\u4e8e\u6307\u5bfc\u6709\u5173\u5e72\u9884\u63aa\u65bd\u3001\u7269\u7406\u6cbb\u7597\u548c\u8f85\u52a9\u8bbe\u5907\u7684\u51b3\u7b56\u3002.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u7531\u4e8e NSAA \u4fa7\u91cd\u4e8e\u6b65\u884c\u529f\u80fd\uff0c\u56e0\u6b64\u901a\u5e38\u7528\u4e8e 4 \u81f3 18 \u5c81\u7684\u7537\u5b69\uff0c\u5728\u4ed6\u4eec\u5931\u53bb\u72ec\u7acb\u884c\u8d70\u80fd\u529b\u4e4b\u524d\u8fdb\u884c\u8bc4\u4f30\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"structure-and-scoring-of-the-nsaa\"><strong>NSAA\u7684\u7ed3\u6784\u548c\u8bc4\u5206<\/strong><\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u5317\u6781\u661f\u6b65\u884c\u80fd\u529b\u8bc4\u4f30\u5305\u542b17\u9879\u529f\u80fd\u6027\u4efb\u52a1\uff0c\u7528\u4e8e\u8bc4\u4f30\u7ad9\u7acb\u3001\u884c\u8d70\u3001\u8dd1\u6b65\u548c\u6500\u722c\u7b49\u80fd\u529b\u3002\u6bcf\u9879\u4efb\u52a1\u5747\u91c7\u75283\u5206\u5236\u8bc4\u5206\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>2 = \u6b63\u5e38\u6267\u884c\u4efb\u52a1<\/strong><\/li>\n\n\n\n<li><strong>1 = \u5728\u4fee\u6539\u6216\u534f\u52a9\u4e0b\u5b8c\u6210\u4efb\u52a1<\/strong><\/li>\n\n\n\n<li><strong>0 = \u65e0\u6cd5\u6267\u884c\u4efb\u52a1<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u603b\u5206\u6700\u9ad8\u4e3a 34 \u5206\uff0c\u4ee3\u8868\u8fd0\u52a8\u529f\u80fd\u5b8c\u5168\u6b63\u5e38\uff1b\u5206\u6570\u8d8a\u4f4e\uff0c\u8868\u793a\u529f\u80fd\u969c\u788d\u8d8a\u4e25\u91cd\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"nsaa-assessed-skills\">NSAA\u8bc4\u4f30\u6280\u80fd<\/h2>\n\n\n\n<ol class=\"wp-block-list\">\n<li><strong>\u5e38\u8bbe<\/strong>\uff1a\u8d64\u811a\u7ad9\u7acb\uff0c\u5c3d\u53ef\u80fd\u957f\u65f6\u95f4\u4fdd\u6301\u9759\u6b62\uff0c\u4e0d\u8981\u6709\u5916\u90e8\u652f\u6491\u3002.<\/li>\n\n\n\n<li><strong>\u6b65\u884c<\/strong>\uff1a\u4ee5\u7a33\u5b9a\u7684\u811a\u8ddf\u5230\u811a\u5c16\u7684\u6b65\u6001\u5411\u524d\u8d70\u81f3\u5c11 10 \u6b65\u3002.<\/li>\n\n\n\n<li><strong>\u4ece\u6905\u5b50\u4e0a\u7ad9\u8d77\u6765<\/strong>\uff1a\u5f00\u59cb\u65f6\u53cc\u81c2\u4ea4\u53c9\u62b1\u4e8e\u80f8\u524d\uff0c\u7136\u540e\u4ece\u6905\u5b50\u4e0a\u7ad9\u8d77\u6765\uff0c\u53cc\u81c2\u4e0d\u8981\u677e\u5f00\u3002.<\/li>\n\n\n\n<li><strong>\u722c\u5761\u6b65\uff08\u53f3\u817f\uff09<\/strong>\u7528\u53f3\u811a\uff08\u6216\u60ef\u7528\u811a\uff09\u8e0f\u4e0a\u81f3\u5c11 15 \u5398\u7c73\u9ad8\u7684\u7bb1\u5f62\u53f0\u9636\u3002.<\/li>\n\n\n\n<li><strong>\u722c\u5761\u6b65\uff08\u5de6\u817f\uff09<\/strong>\u7528\u5de6\u811a\uff08\u6216\u975e\u60ef\u7528\u811a\uff09\u8e29\u4e0a\u81f3\u5c11 15 \u5398\u7c73\u9ad8\u7684\u7bb1\u5f62\u53f0\u9636\uff0c\u4e0e\u53e6\u4e00\u53ea\u811a\u5e76\u62e2\u3002.<\/li>\n\n\n\n<li><strong>\u5750\u4e0b<\/strong>\u5e73\u8eba\u5728\u5730\u677f\u4e0a\uff0c\u53cc\u81c2\u653e\u5728\u8eab\u4f53\u4e24\u4fa7\uff0c\u7136\u540e\u8d77\u8eab\u5750\u597d\uff0c\u8fc7\u7a0b\u4e2d\u8eab\u4f53\u4e0d\u80fd\u671d\u5411\u5730\u677f\uff0c\u4e5f\u4e0d\u80fd\u7528\u53cc\u624b\u652f\u6491\u3002\u4e3a\u4e86\u83b7\u5f97\u6700\u9ad8\u5206\uff0c\u5141\u8bb8\u4f7f\u7528\u4e00\u53ea\u624b\u3002.<\/li>\n\n\n\n<li><strong>\u8df3<\/strong>\u53cc\u811a\u5e76\u62e2\u7ad9\u5728\u5730\u677f\u4e0a\uff0c\u5c3d\u53ef\u80fd\u9ad8\u5730\u8df3\u8d77\uff0c\u5c3d\u91cf\u51cf\u5c11\u5411\u524d\u79fb\u52a8\u7684\u5e45\u5ea6\u3002.<\/li>\n\n\n\n<li><strong>\u8dd1\u6b65<\/strong>\u5c3d\u53ef\u80fd\u5feb\u5730\u8dd1\u5927\u7ea6 32 \u82f1\u5c3a\u3002\u8981\u83b7\u5f97\u6700\u9ad8\u5206\uff0c\u5954\u8dd1\u65f6\u53cc\u811a\u90fd\u5fc5\u987b\u79bb\u5730\u3002.<\/li>\n\n\n\n<li><strong>\u5355\u817f\u7ad9\u7acb<\/strong>\u5355\u817f\u7ad9\u7acb\uff0c\u53cc\u81c2\u81ea\u7136\u4e0b\u5782\uff0c\u5c3d\u53ef\u80fd\u957f\u65f6\u95f4\u4fdd\u6301\u8fd9\u4e2a\u59ff\u52bf\u3002.<\/li>\n\n\n\n<li><strong>\u5355\u817f\u7ad9\u7acb<\/strong>\u5355\u817f\u7ad9\u7acb\uff0c\u53cc\u81c2\u81ea\u7136\u4e0b\u5782\uff0c\u5c3d\u53ef\u80fd\u957f\u65f6\u95f4\u4fdd\u6301\u8fd9\u4e2a\u59ff\u52bf\u3002.<\/li>\n\n\n\n<li><strong>\u4e0b\u7bb1\u6b65\uff08\u53f3\u817f\uff09<\/strong>\u9762\u5411\u524d\u65b9\uff0c\u7528\u53f3\u811a\uff08\u6216\u60ef\u7528\u811a\uff09\u4ece\u7bb1\u5b50\u4e0a\u8d70\u4e0b\u6765\u3002.<\/li>\n\n\n\n<li><strong>\u4e0b\u7bb1\u6b65\uff08\u5de6\u817f\uff09<\/strong>\u9762\u5411\u524d\u65b9\uff0c\u7528\u5de6\u811a\uff08\u6216\u975e\u60ef\u7528\u811a\uff09\u4ece\u7bb1\u5b50\u4e0a\u4e0b\u6765\uff0c\u4e0e\u53e6\u4e00\u53ea\u811a\u6c47\u5408\u3002.<\/li>\n\n\n\n<li><strong>\u7ad9\u76f4\u811a\u8ddf<\/strong>\u8d64\u811a\u540e\u8ddf\u5411\u540e\u503e\u659c\uff0c\u4fdd\u6301\u4e09\u79d2\u949f\u3002\u8981\u83b7\u5f97\u6700\u9ad8\u5206\uff0c\u53cc\u811a\u5fc5\u987b\u540c\u65f6\u62ac\u8d77\uff0c\u5e76\u5145\u5206\u80cc\u5c48\uff08\u5c06\u811a\u62ac\u5411\u5c0f\u817f\uff09\u3002.<\/li>\n\n\n\n<li><strong>\u4ece\u5730\u677f\u8d77\u8eab<\/strong>\u5e73\u8eba\u5728\u5730\u4e0a\uff0c\u5c3d\u5feb\u7ad9\u8d77\u6765\uff0c\u4e0d\u8981\u7ffb\u8eab\u6210\u56db\u70b9\u8dea\u59ff\u6216\u4fef\u5367\u59ff\u52bf\uff08\u6208\u5c14\u6c0f\u52a8\u4f5c\uff09\u3002.<\/li>\n\n\n\n<li><strong>\u62ac\u5934<\/strong>\u5e73\u8eba\u5728\u5730\u677f\u4e0a\uff0c\u53cc\u81c2\u4ea4\u53c9\u62b1\u5728\u80f8\u524d\uff0c\u53cc\u624b\u653e\u5728\u80a9\u8180\u4e0b\u65b9\u3002\u7136\u540e\uff0c\u62ac\u8d77\u5934\uff0c\u4e0b\u5df4\u8d34\u8fd1\u80f8\u90e8\uff0c\u540c\u65f6\u4fdd\u6301\u53cc\u81c2\u4ea4\u53c9\u62b1\u5728\u80f8\u524d\u3002.<\/li>\n\n\n\n<li><strong>\u5355\u817f\u8df3<\/strong>\uff1a\u5355\u817f\u7ad9\u7acb\uff0c\u5355\u811a\u8df3\uff0c\u53cc\u811a\u4e0d\u80fd\u540c\u65f6\u843d\u5730\u3002.<\/li>\n\n\n\n<li><strong>\u5355\u817f\u8df3<\/strong>\u5355\u817f\u7ad9\u7acb\uff0c\u5de6\u811a\u8df3\uff0c\u53cc\u811a\u4e0d\u8981\u540c\u65f6\u843d\u5730<\/li>\n<\/ol>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u6d4b\u8bd5\u64cd\u4f5c\u7b80\u4fbf\u5feb\u6377\uff08\u901a\u5e38\u53ea\u9700 10-15 \u5206\u949f\uff09\uff0c\u6240\u9700\u8bbe\u5907\u6781\u5c11\uff0c\u56e0\u6b64\u975e\u5e38\u9002\u5408\u65e5\u5e38\u8bca\u6240\u5c31\u8bca\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"interpreting-nsaa-scores\"><strong>NSAA\u8bc4\u5206\u89e3\u8bfb<\/strong><\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\u8bc4\u5206\u5f80\u5f80\u9075\u5faa\u53ef\u9884\u6d4b\u7684\u8f68\u8ff9\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u5e7c\u513f\u671f\uff084-7\u5c81\uff09\uff1a<\/strong> \u968f\u7740\u8fd0\u52a8\u6280\u80fd\u7684\u53d1\u5c55\uff0c\u5206\u6570\u901a\u5e38\u4f1a\u63d0\u9ad8\u3002.<\/li>\n\n\n\n<li><strong>\u513f\u7ae5\u4e2d\u671f\uff087-10\u5c81\uff09\uff1a<\/strong> \u5206\u6570\u8d8b\u4e8e\u7a33\u5b9a\uff0c\u53cd\u6620\u51fa\u8fd0\u52a8\u5b66\u4e60\u548c\u808c\u8089\u65e0\u529b\u4e4b\u95f4\u7684\u5e73\u8861\u3002.<\/li>\n\n\n\n<li><strong>\u513f\u7ae5\u665a\u671f\uff0810\u5c81\u4ee5\u4e0a\uff09\uff1a<\/strong> \u968f\u7740\u808c\u8089\u9010\u6e10\u9000\u5316\u5bfc\u81f4\u7279\u5b9a\u80fd\u529b\u4e27\u5931\uff0c\u8bc4\u5206\u4e5f\u4f1a\u4e0b\u964d\u3002.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u8ffd\u8e2aNSAA\u968f\u65f6\u95f4\u7684\u53d8\u5316\u6709\u52a9\u4e8e\u4e34\u5e8a\u533b\u751f\u53d1\u73b0\u5177\u6709\u4e34\u5e8a\u610f\u4e49\u7684\u5dee\u5f02\uff08CMD\uff09\u2014\u2014\u901a\u5e38\u5728\u4e34\u5e8a\u8bd5\u9a8c\u4e2d\uff0c\u22652\u5206\u7684\u53d8\u5316\u88ab\u8ba4\u4e3a\u5177\u6709\u4e34\u5e8a\u610f\u4e49\u3002\u89c2\u770b\u89c6\u9891\uff1a <a href=\"https:\/\/www.youtube.com\/watch?v=dgzDd5_fsDY\" target=\"_blank\" rel=\"noopener\">\u8bc4\u4f30\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u8fd0\u52a8\u529f\u80fd<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"use-of-the-nsaa-in-clinical-trials\"><strong>NSAA\u5728\u4e34\u5e8a\u8bd5\u9a8c\u4e2d\u7684\u5e94\u7528<\/strong><\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">NSAA \u662f\u8bb8\u591a\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c\u7684\u4e3b\u8981\u6216\u6b21\u8981\u7ec8\u70b9\u3002\u5b83\u63d0\u4f9b\u4e86\u4e00\u79cd\u5ba2\u89c2\u4e14\u53ef\u91cd\u590d\u7684\u8fd0\u52a8\u529f\u80fd\u6d4b\u91cf\u65b9\u6cd5\uff0c\u4e0e\u5176\u4ed6\u7ed3\u679c\uff08\u5982 6 \u5206\u949f\u6b65\u884c\u8ddd\u79bb (6MWD) \u548c\u8ba1\u65f6\u529f\u80fd\u6d4b\u8bd5\uff08\u4f8b\u5982\uff0c\u7ad9\u7acb\u65f6\u95f4\u6216\u722c\u697c\u68af\u65f6\u95f4\uff09\uff09\u5bc6\u5207\u76f8\u5173\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u56e0\u4e3a\u5b83\u80fd\u591f\u6355\u6349\u4e0e\u65e5\u5e38\u751f\u6d3b\u76f8\u5173\u7684\u529f\u80fd\u6027\u4efb\u52a1\uff0c\u4ece\u800c\u53cd\u6620\u51fa\u5bf9\u60a3\u8005\u53ca\u5176\u5bb6\u5ead\u6709\u610f\u4e49\u7684\u6539\u5584\uff0c\u56e0\u6b64\u5728\u5bf9\u65b0\u7597\u6cd5\u8fdb\u884c\u76d1\u7ba1\u8bc4\u4f30\u65f6\u5177\u6709\u6781\u9ad8\u7684\u4ef7\u503c\u3002\u4e86\u89e3\u66f4\u591a\uff1a <a href=\"https:\/\/dmdwarrior.com\/zh\/how-to-participate-in-clinical-trials-for-duchenne\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u6211\u7684\u5b69\u5b50\u5982\u4f55\u53c2\u52a0\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c\uff1f<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"limitations-of-the-nsaa\"><strong>NSAA\u7684\u5c40\u9650\u6027<\/strong><\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u867d\u7136\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\u662f\u4e00\u79cd\u5f3a\u5927\u7684\u8bc4\u4f30\u5de5\u5177\uff0c\u4f46\u5b83\u4e5f\u5b58\u5728\u4e00\u4e9b\u5c40\u9650\u6027\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u5b83\u4ec5\u9002\u7528\u4e8e\u80fd\u591f\u884c\u8d70\u7684\u60a3\u8005\u2014\u2014\u4e0d\u80fd\u884c\u8d70\u7684\u7537\u5b69\u9700\u8981\u5176\u4ed6\u91cf\u8868\uff0c\u4f8b\u5982\u4e0a\u80a2\u529f\u80fd (PUL) \u6d4b\u8bd5\u3002.<\/li>\n\n\n\n<li>\u8bc4\u5206\u7cfb\u7edf\u867d\u7136\u5ba2\u89c2\uff0c\u4f46\u8bc4\u5206\u8005\u4e4b\u95f4\u53ef\u80fd\u5b58\u5728\u5dee\u5f02\uff0c\u8fd9\u51f8\u663e\u4e86\u8bad\u7ec3\u6709\u7d20\u7684\u7406\u7597\u5e08\u7684\u5fc5\u8981\u6027\u3002.<\/li>\n\n\n\n<li>\u73af\u5883\u56e0\u7d20\u548c\u52a8\u673a\u90fd\u4f1a\u5f71\u54cd\u8003\u8bd5\u5f53\u5929\u7684\u8868\u73b0\u3002.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u5c3d\u7ba1\u5982\u6b64\uff0cNSAA \u4ecd\u7136\u662f\u8bc4\u4f30\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u884c\u8d70\u529f\u80fd\u7684\u9ec4\u91d1\u6807\u51c6\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"most-common-question-about-north-star-ambulatory-assessment-nsaa\"><strong>\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\uff1a\u95ee\u7b54<\/strong><\/h2>\n\n\n<div id=\"rank-math-faq\" class=\"rank-math-block\">\n<div class=\"rank-math-list\">\n<div id=\"faq-question-1761824999344\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u4ec0\u4e48\u662f\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n<img loading=\"lazy\" decoding=\"async\" width=\"1080\" height=\"1080\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/11\/North-Star-Ambulatory-Assessment-NSAA.jpg\" class=\"alignright\" alt=\"\u4ec0\u4e48\u662f\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\uff1f\" title=\"\">\n<p>\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30 (NSAA) \u662f\u4e00\u9879\u5305\u542b 17 \u4e2a\u9879\u76ee\u7684\u529f\u80fd\u91cf\u8868\uff0c\u65e8\u5728\u6d4b\u91cf\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u7684\u53ef\u884c\u8d70\u7537\u5b69\u7684\u8fd0\u52a8\u80fd\u529b\u3002.<\/p>\n<p>\u5b83\u8bc4\u4f30\u7ad9\u7acb\u3001\u884c\u8d70\u3001\u8dd1\u6b65\u3001\u722c\u697c\u68af\u548c\u8df3\u8dc3\u7b49\u6d3b\u52a8\uff0c\u8fd9\u4e9b\u6d3b\u52a8\u5bf9\u4e8e\u65e5\u5e38\u6d3b\u52a8\u81f3\u5173\u91cd\u8981\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825035673\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u4e3a\u4ec0\u4e48\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u4f1a\u4f7f\u7528NSAA\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u4e4b\u6240\u4ee5\u4f7f\u7528 NSAA\uff0c\u662f\u56e0\u4e3a\u5b83\u80fd\u591f\u5bf9\u60a3\u6709 DMD \u7684\u7537\u5b69\u7684\u529f\u80fd\u80fd\u529b\u548c\u75be\u75c5\u8fdb\u5c55\u8fdb\u884c\u5b9a\u91cf\u6d4b\u91cf\u3002.<\/p>\n<p>\u4e34\u5e8a\u533b\u751f\u548c\u7814\u7a76\u4eba\u5458\u7528\u5b83\u6765\uff1a<\/p>\n<p>\u2022 \u8ddf\u8e2a\u8fd0\u52a8\u6027\u80fd\u968f\u65f6\u95f4\u7684\u53d8\u5316<br \/>\u2022 \u8bc4\u4f30\u65b0\u7597\u6cd5\u6216\u6cbb\u7597\u65b9\u6848\u7684\u6709\u6548\u6027<br \/>\u2022 \u76d1\u6d4b\u76ae\u8d28\u7c7b\u56fa\u9187\u4f7f\u7528\u548c\u7269\u7406\u6cbb\u7597\u5e72\u9884\u7684\u6548\u679c<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825143662\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u8c01\u53ef\u4ee5\u8fdb\u884cNSAA\u6d4b\u8bd5\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>NSAA\u901a\u5e38\u7531\u53d7\u8fc7\u4e13\u95e8\u7814\u7a76\u795e\u7ecf\u808c\u8089\u75be\u75c5\u7684\u7406\u7597\u5e08\u6216\u4e34\u5e8a\u533b\u751f\u8fdb\u884c\u3002\u9002\u5f53\u7684\u57f9\u8bad\u53ef\u786e\u4fdd\u4e0d\u540c\u8bc4\u4f30\u8005\u548c\u7814\u7a76\u4e2d\u5fc3\u4e4b\u95f4\u7684\u8bc4\u5206\u5177\u6709\u4e00\u81f4\u6027\u548c\u53ef\u9760\u6027\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825159756\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA\u662f\u5982\u4f55\u8bc4\u5206\u7684\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>17 \u4e2a\u9879\u76ee\u4e2d\u7684\u6bcf\u4e00\u9879\u90fd\u6309\u4ee5\u4e0b\u65b9\u5f0f\u8bc4\u5206\uff1a<\/p>\n<p>\u2022 2 \u5206 \u2013 \u53ef\u4ee5\u6b63\u5e38\u5b8c\u6210\u8be5\u6d3b\u52a8<br \/>\u2022 1 \u5206 \u2013 \u53ef\u4ee5\u5b8c\u6210\u8be5\u6d3b\u52a8\uff0c\u4f46\u6709\u4e00\u5b9a\u96be\u5ea6\u6216\u9700\u8981\u8865\u507f\u3002<br \/>\u2022 0 \u5206 \u2013 \u65e0\u6cd5\u5b8c\u6210\u8be5\u6d3b\u52a8<\/p>\n<p>\u603b\u5206\u6700\u9ad8\u4e3a 34 \u5206\uff0c\u5206\u6570\u8d8a\u9ad8\u8868\u793a\u8fd0\u52a8\u529f\u80fd\u8d8a\u597d\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825213163\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u5b8c\u6210NSAA\u9700\u8981\u591a\u957f\u65f6\u95f4\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u8bc4\u4f30\u901a\u5e38\u9700\u8981 10-15 \u5206\u949f\u624d\u80fd\u5b8c\u6210\uff0c\u5177\u4f53\u65f6\u95f4\u53d6\u51b3\u4e8e\u5b69\u5b50\u7684\u914d\u5408\u7a0b\u5ea6\u548c\u75b2\u52b3\u7a0b\u5ea6\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825239921\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA\u5177\u4f53\u8861\u91cf\u7684\u662f\u4ec0\u4e48\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u5317\u6781\u661f\u6b65\u884c\u80fd\u529b\u8bc4\u4f30\uff08NSAA\uff09\u7528\u4e8e\u6d4b\u91cf\u7c97\u5927\u8fd0\u52a8\u6280\u80fd\u548c\u6b65\u884c\u529f\u80fd\uff0c\u5305\u62ec\uff1a<\/p>\n<p>\u2022 \u7ad9\u7acb\u5e73\u8861<br \/>\u2022 \u4ece\u5730\u677f\u4e0a\u5347\u8d77<br \/>\u2022 \u6b65\u884c\u548c\u8dd1\u6b65\u80fd\u529b<br \/>\u2022 \u722c\u697c\u68af<br \/>\u2022 \u8df3\u8dc3\u548c\u5355\u811a\u8df3<\/p>\n<p>\u8fd9\u4e9b\u4efb\u52a1\u53cd\u6620\u4e86\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u6700\u5e38\u5f71\u54cd\u7684\u65e5\u5e38\u8fd0\u52a8\u80fd\u529b\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825277811\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA \u9002\u7528\u4e8e\u591a\u5927\u5e74\u9f84\u6bb5\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>NSAA\u6d4b\u8bd5\u901a\u5e38\u9002\u7528\u4e8e4\u81f318\u5c81\u4ecd\u80fd\u884c\u8d70\u7684\u7537\u5b69\u3002\u7136\u800c\uff0c\u8be5\u6d4b\u8bd5\u57285\u81f312\u5c81\u4e4b\u95f4\u6700\u5177\u53c2\u8003\u4ef7\u503c\uff0c\u56e0\u4e3aDMD\u60a3\u8005\u7684\u8fd0\u52a8\u6280\u80fd\u901a\u5e38\u5728\u8fd9\u4e2a\u5e74\u9f84\u6bb5\u8fbe\u5230\u9876\u5cf0\uff0c\u7136\u540e\u9010\u6e10\u4e0b\u964d\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825294335\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA \u5e94\u8be5\u591a\u4e45\u8fdb\u884c\u4e00\u6b21\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u5728\u4e34\u5e8a\u5b9e\u8df5\u548c\u7814\u7a76\u4e2d\uff0c\u901a\u5e38\u6bcf 6 \u81f3 12 \u4e2a\u6708\u8fdb\u884c\u4e00\u6b21 NSAA \u68c0\u67e5\uff0c\u4ee5\u76d1\u6d4b\u75be\u75c5\u8fdb\u5c55\u548c\u6cbb\u7597\u53cd\u5e94\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825309981\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA\u662f\u5982\u4f55\u7528\u4e8e\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c\u7684\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\u662f\u8bb8\u591a\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u4e34\u5e8a\u8bd5\u9a8c\u7684\u4e3b\u8981\u6216\u6b21\u8981\u7ec8\u70b9\u6307\u6807\u3002\u5b83\u6709\u52a9\u4e8e\u786e\u5b9a\u4e00\u79cd\u65b0\u836f\u3001\u57fa\u56e0\u7597\u6cd5\u6216\u5916\u663e\u5b50\u8df3\u8dc3\u7597\u6cd5\u662f\u5426\u80fd\u6709\u6548\u5ef6\u7f13\u8fd0\u52a8\u529f\u80fd\u7684\u8870\u9000\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825328456\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA\u6709\u54ea\u4e9b\u5c40\u9650\u6027\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u867d\u7136\u5317\u6781\u661f\u52a8\u6001\u8bc4\u4f30\u662f\u4e00\u4e2a\u5f88\u6709\u4ef7\u503c\u7684\u5de5\u5177\uff0c\u4f46\u5b83\u4e5f\u5b58\u5728\u4e00\u4e9b\u5c40\u9650\u6027\uff1a<\/p>\n<p>\u2022 \u4ec5\u9002\u7528\u4e8e\u53ef\u81ea\u4e3b\u884c\u8d70\u7684\u60a3\u8005\uff08\u4ecd\u80fd\u884c\u8d70\u7684\u60a3\u8005\uff09\u3002.<br \/>\u2022 \u5b83\u53ef\u80fd\u65e0\u6cd5\u68c0\u6d4b\u5230\u75be\u75c5\u8fdb\u5c55\u65e9\u671f\u6216\u665a\u671f\u8fd0\u52a8\u529f\u80fd\u7684\u7ec6\u5fae\u53d8\u5316\u3002.<br \/>\u2022 \u9700\u8981\u7ecf\u8fc7\u57f9\u8bad\u7684\u8bc4\u4f30\u4eba\u5458\u624d\u80fd\u83b7\u5f97\u4e00\u81f4\u7684\u7ed3\u679c\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825354752\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u7537\u5b69\u5982\u679c\u4e27\u5931\u884c\u8d70\u80fd\u529b\u4f1a\u53d1\u751f\u4ec0\u4e48\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u5f53\u60a3\u8005\u4e27\u5931\u884c\u8d70\u80fd\u529b\u65f6\uff0cNSAA \u5c31\u4e0d\u518d\u9002\u7528\u3002\u4e34\u5e8a\u533b\u751f\u4f1a\u4f7f\u7528\u5176\u4ed6\u91cf\u8868\uff0c\u4f8b\u5982\u4e0a\u80a2\u529f\u80fd\u8bc4\u4f30 (PUL)\uff0c\u6765\u76d1\u6d4b\u624b\u81c2\u548c\u4e0a\u534a\u8eab\u529f\u80fd\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825371612\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA\u80fd\u5426\u9884\u6d4bDMD\u60a3\u8005\u7684\u884c\u8d70\u80fd\u529b\u4e27\u5931\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u662f\u7684\u3002\u7814\u7a76\u8868\u660e\uff0c\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\uff08NSAA\uff09\u8bc4\u5206\u968f\u65f6\u95f4\u63a8\u79fb\u800c\u4e0b\u964d\u4e0e\u4e27\u5931\u884c\u8d70\u80fd\u529b\u7684\u65f6\u95f4\u76f8\u5173\u3002\u4f8b\u5982\uff0cNSAA\u8bc4\u5206\u4f4e\u4e8e18\u5206\u7684\u7537\u5b69\u901a\u5e38\u6709\u5728\u672a\u67652-3\u5e74\u5185\u4e27\u5931\u884c\u8d70\u80fd\u529b\u7684\u98ce\u9669\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825393528\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA\u662f\u5426\u53ef\u9760\u4e14\u7ecf\u8fc7\u9a8c\u8bc1\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u662f\u7684\u3002NSAA \u5df2\u901a\u8fc7\u4e34\u5e8a\u9a8c\u8bc1\uff0c\u5e76\u663e\u793a\u51fa\u6781\u4f73\u7684\u8bc4\u5206\u8005\u95f4\u4fe1\u5ea6\u548c\u91cd\u6d4b\u4fe1\u5ea6\u3002\u5b83\u5df2\u88ab\u5e7f\u6cdb\u63a5\u53d7\u7528\u4e8e\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bca\u7597\u548c\u56fd\u9645\u7814\u7a76\u8bd5\u9a8c\u4e2d\u3002.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825415116\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u5bb6\u957f\u5982\u4f55\u5e2e\u52a9\u5b69\u5b50\u51c6\u5907NSAA\u8003\u8bd5\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u5bb6\u957f\u53ef\u4ee5\u8fd9\u6837\u63d0\u4f9b\u5e2e\u52a9\uff1a<\/p>\n<p>\u2022 \u786e\u4fdd\u5b69\u5b50\u7a7f\u7740\u8212\u9002\u7684\u8863\u670d\u548c\u978b\u5b50<br \/>\u2022 \u9f13\u52b1\u5b69\u5b50\u5728\u8003\u8bd5\u524d\u4f11\u606f\uff0c\u4ee5\u907f\u514d\u75b2\u52b3<br \/>\u2022 \u63d0\u4f9b\u9f13\u52b1\uff0c\u5e2e\u52a9\u5b69\u5b50\u81ea\u4fe1\u5730\u5b8c\u6210\u6bcf\u4e00\u9879\u4efb\u52a1<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1761825442589\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">NSAA\u8868\u683c\u6216\u8bc4\u5206\u8868\u5728\u54ea\u91cc\u53ef\u4ee5\u627e\u5230\uff1f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>NSAA\u5b98\u65b9\u8868\u683c\u548c\u8be6\u7ec6\u8bc4\u5206\u6307\u5357\u53ef\u901a\u8fc7\u4ee5\u4e0b\u65b9\u5f0f\u83b7\u53d6\uff1a<\/p>\n<p>\u2022 \u5317\u6781\u661f\u795e\u7ecf\u808c\u8089\u75be\u75c5\u4e34\u5e8a\u7f51\u7edc (NSCN)<br \/>\u2022 \u5728\u795e\u7ecf\u808c\u8089\u671f\u520a\u4e0a\u53d1\u8868\u4e34\u5e8a\u7814\u7a76<br \/>\u2022 \u5df2\u6388\u6743\u7684\u4e34\u5e8a\u8bd5\u9a8c\u6587\u4ef6<\/p>\n\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n\n\n<h2 class=\"wp-block-heading\" id=\"conclusion\"><strong>\u7ed3\u8bba<\/strong><\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30 (NSAA) \u662f\u8bc4\u4f30\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7537\u5b69\u8fd0\u52a8\u529f\u80fd\u7684\u91cd\u8981\u5de5\u5177\u3002.<\/strong> \u5176\u7b80\u4fbf\u6027\u3001\u53ef\u9760\u6027\u548c\u7075\u654f\u5ea6\u4f7f\u5176\u6210\u4e3a\u4e34\u5e8a\u7ba1\u7406\u548c\u7814\u7a76\u8bd5\u9a8c\u4e2d\u4e0d\u53ef\u6216\u7f3a\u7684\u5de5\u5177\u3002\u901a\u8fc7\u7cfb\u7edf\u5730\u8ffd\u8e2a\u8fd0\u52a8\u80fd\u529b\u7684\u53d8\u5316\uff0cNSAA \u4f7f\u4e34\u5e8a\u533b\u751f\u548c\u7814\u7a76\u4eba\u5458\u80fd\u591f\u66f4\u597d\u5730\u4e86\u89e3\u75be\u75c5\u8fdb\u5c55\uff0c\u5e76\u8bc4\u4f30\u65b0\u5174\u7597\u6cd5\u5728\u5b9e\u9645\u5e94\u7528\u4e2d\u7684\u6548\u679c\u3002.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"key-takeaways\"><strong>\u8981\u70b9\u603b\u7ed3<\/strong><\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>NSAA \u901a\u8fc7 17 \u9879\u4efb\u52a1\u6765\u6d4b\u91cf DMD \u60a3\u8005\u7684\u6b65\u884c\u8fd0\u52a8\u529f\u80fd\u3002.<\/li>\n\n\n\n<li>\u8bc4\u5206\u8303\u56f4\u4e3a 0 \u5230 34 \u5206\uff0c\u5206\u6570\u8d8a\u9ad8\u8868\u793a\u529f\u80fd\u8d8a\u597d\u3002.<\/li>\n\n\n\n<li>\u5b83\u5e7f\u6cdb\u7528\u4e8e\u4e34\u5e8a\u8bd5\u9a8c\u4e2d\uff0c\u4ee5\u76d1\u6d4b\u6cbb\u7597\u6548\u679c\u3002.<\/li>\n\n\n\n<li>\u5b9a\u671f\u8fdb\u884c NSAA \u68c0\u6d4b\u6709\u52a9\u4e8e\u4e2a\u6027\u5316\u62a4\u7406\u548c\u65e9\u671f\u5e72\u9884\u3002.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" data-type=\"page\" data-id=\"4611\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c\uff08\u6240\u6709\u7814\u7a76\u5217\u8868\uff09<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The North Star Ambulatory Assessment (NSAA) is a standardized, clinician-administered tool designed to evaluate motor performance in ambulant boys with Duchenne muscular dystrophy (DMD). Developed by the North Star Clinical Network for Neuromuscular Diseases, it provides a reliable way to track disease progression and assess treatment outcomes in both clinical practice and research settings. 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