{"id":4799,"date":"2025-10-14T10:10:06","date_gmt":"2025-10-14T07:10:06","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4799"},"modified":"2025-10-14T10:17:10","modified_gmt":"2025-10-14T07:17:10","slug":"brogidirsen-ns-089-ncnp-02-has-the-potential-to-slow-disease-progression-in-dmd-patients-amenable-to-exon-44-skipping","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/brogidirsen-ns-089-ncnp-02-has-the-potential-to-slow-disease-progression-in-dmd-patients-amenable-to-exon-44-skipping\/","title":{"rendered":"Brogidirsen (NS-089\/NCNP-02) \u6709\u671b\u51cf\u7f13\u63a5\u53d7\u5916\u663e\u5b50 44 \u8df3\u8dc3\u7597\u6cd5\u6cbb\u7597\u7684 DMD \u60a3\u8005\u7684\u75c5\u60c5\u8fdb\u5c55"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Nippon Shinyaku \u516c\u5e03\u4e86\u57fa\u4e8e\u5f00\u653e\u6807\u7b7e\u6269\u5c55\u7814\u7a76\u7684 3.5 \u5e74\u5e94\u7528\u7684\u7597\u6548\u548c\u5b89\u5168\u6027\u6570\u636e\uff0c\u5176\u4e2d\u8fd8\u5305\u62ec\u542f\u52a8 brogidirsen \u7684\u4e34\u5e8a\u8bd5\u9a8c (NS-089\/NCNP-02)\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u4e9b\u6570\u636e\u7531\u65e5\u672c\u56fd\u5bb6\u795e\u7ecf\u75c5\u5b66\u548c\u7cbe\u795e\u75c5\u5b66\u4e2d\u5fc3\uff08NCNP\uff0c\u4e1c\u4eac\u5c0f\u5e73\u5e02\uff1b\u4e3b\u5e2d\uff0c\u4e2d\u8fbc\u548c\u4e4b\uff09\u5728 2025 \u5e74 10 \u6708 7 \u65e5\u81f3 11 \u65e5\u5728\u5965\u5730\u5229\u4e3e\u884c\u7684\u7b2c 30 \u5c4a\u4e16\u754c\u808c\u8089\u5b66\u4f1a\u56fd\u9645\u5927\u4f1a\u4e0a\u4ee5\u6d77\u62a5\u5f62\u5f0f\u5c55\u793a\u3002<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Brogidirsen \u662f\u4ec0\u4e48\uff1f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Brogidirsen \u662f\u7531 Nippon Shinyaku \u548c NCNP \u5171\u540c\u53d1\u73b0\u7684\u53cd\u4e49\u5be1\u6838\u82f7\u9178\uff0c\u7528\u4e8e\u6cbb\u7597\u60a3\u6709\u53ef\u8fdb\u884c\u5916\u663e\u5b50 44 \u8df3\u8dc3\u7684\u6297\u808c\u840e\u7f29\u86cb\u767d\u57fa\u56e0\u7a81\u53d8\u7684 DMD \u60a3\u8005\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u672c\u6587\u6570\u636e\u57fa\u4e8eNCNP\u5f00\u5c55\u7684\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e34\u5e8a\u8bd5\u9a8c\u53ca\u5176Nippon Shinyaku\u5f00\u5c55\u7684\u6269\u5c55\u7814\u7a76\u3002\u8fd9\u4e9b\u7814\u7a76\u8bc4\u4f30\u4e866\u4f8b\u63a5\u53d7\u6bcf\u5468\u9759\u8109\u6ce8\u5c04\u5e03\u7f57\u5409\u5b9a\u7684\u60a3\u8005\u4e2d\u7684\u7597\u6548\u548c\u5b89\u5168\u6027\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/zh\/upcoming-exon-44-skipping-therapies-for-dmd\/\">\u5373\u5c06\u63a8\u51fa\u7684\u5916\u663e\u5b50 44 \u8df3\u8dc3\u7597\u6cd5<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u5b89\u5168\u7ed3\u679c<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u7ed3\u679c\u663e\u793a\uff0c\u5728\u7b2c25\/26\u5468\u548c\u7b2c99\/100\u5468\uff0c\u6d3b\u68c0\u808c\u8089\u4e2d\u7684\u5916\u663e\u5b50\u8df3\u8dc3\u6548\u7387\u548c\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u8868\u8fbe\u6c34\u5e73\u5448\u9ad8\u8d8b\u52bf\u3002\u6b64\u5916\uff0c\u957f\u671f\u670d\u7528\u5e03\u7f57\u5409\u5b9a\u540e\u4ecd\u80fd\u884c\u8d70\u7684\u53d7\u8bd5\u8005\u5728\u5305\u62ec\u5317\u6781\u661f\u6b65\u884c\u8bc4\u4f30\u5728\u5185\u7684\u8bc4\u4f30\u4e2d\u4fdd\u6301\u4e86\u8fd0\u52a8\u529f\u80fd\u3002\u5b89\u5168\u6027\u8bc4\u4f30\u7ed3\u679c\u663e\u793a\uff0c\u672a\u89c2\u5bdf\u5230\u4e0e\u5e03\u7f57\u5409\u5b9a\u76f8\u5173\u7684\u4e25\u91cd\u6216\u91cd\u5ea6\u4e0d\u826f\u4e8b\u4ef6\uff0c\u4e5f\u672a\u89c2\u5bdf\u5230\u4e0e\u8f93\u6ce8\u76f8\u5173\u53cd\u5e94\uff08\u4f8b\u5982\u8fc7\u654f\u53cd\u5e94\uff09\u76f8\u5173\u7684\u4e0d\u826f\u4e8b\u4ef6\uff0c\u4e5f\u672a\u89c2\u5bdf\u5230\u56e0\u4e0d\u826f\u4e8b\u4ef6\u800c\u505c\u836f\u7684\u60c5\u51b5\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7ed3\u679c\u8868\u660e\uff0cbrogidirsen \u6709\u53ef\u80fd\u51cf\u7f13\u9002\u5408\u8fdb\u884c\u5916\u663e\u5b50 44 \u8df3\u8dc3\u7684 DMD \u60a3\u8005\u7684\u75c5\u60c5\u8fdb\u5c55\u3002<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u9879\u957f\u671f\u5ef6\u957f\u8bd5\u9a8c\u6b63\u5728\u8fdb\u884c\u4e2d\uff0c\u65e8\u5728\u63a2\u7a76\u957f\u671f\u7ed9\u836f\u7684\u6709\u6548\u6027\u548c\u5b89\u5168\u6027\u3002\u6b64\u5916\uff0cNippon Shinyaku \u53ca\u5176\u5b50\u516c\u53f8 NS Pharma, Inc. \u6b63\u5728\u5f00\u5c55\u4e00\u9879\u5173\u4e8e Brogidirsen \u7684\u5168\u7403 II \u671f\u7814\u7a76\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e86\u89e3\u66f4\u591a<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/zh\/mutations-and-deletions-amenable-to-exon-44-skipping-therapies-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u9002\u5408\u5916\u663e\u5b5044\u8df3\u8dc3\u7597\u6cd5\u7684\u7a81\u53d8\u548c\u7f3a\u5931<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Nippon Shinyaku announced efficacy and safety data from a 3.5-year application based on an open-label extension study that also included the initiation of a clinical trial for brogidirsen (NS-089\/NCNP-02). These data were presented as a poster by the National Center of Neurology and Psychiatry (NCNP, Kodaira City, Tokyo; President, Kazuyuki Nakagome) at the 30th annual [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4800,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[138,141,127,246,136,140],"class_list":["post-4799","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-brogidirsen","tag-exon-44","tag-exon-44-skipping","tag-exon-44-skipping-therapies","tag-nippon-shinyaku","tag-ns-089-ncnp-02"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4799","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=4799"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4799\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/4800"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=4799"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=4799"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=4799"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}