{"id":4776,"date":"2025-10-10T17:06:47","date_gmt":"2025-10-10T14:06:47","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4776"},"modified":"2025-10-10T17:17:25","modified_gmt":"2025-10-10T14:17:25","slug":"new-data-of-sat-3247-in-first-in-human-trial-of-adults-with-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/new-data-of-sat-3247-in-first-in-human-trial-of-adults-with-duchenne-muscular-dystrophy\/","title":{"rendered":"Satellos \u516c\u5e03\u65b0\u6570\u636e\uff0c\u8fdb\u4e00\u6b65\u8bc1\u660e SAT-3247 \u5728\u6210\u4eba\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u9996\u6b21\u4eba\u4f53\u8bd5\u9a8c\u4e2d\u7684\u5b89\u5168\u6027\u3001\u8010\u53d7\u6027\u548c\u529f\u80fd\u5f71\u54cd"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Satellos Bioscience \u5728\u5965\u5730\u5229\u7ef4\u4e5f\u7eb3\u4e3e\u884c\u7684\u7b2c 30 \u5c4a\u4e16\u754c\u808c\u8089\u534f\u4f1a\u5e74\u4f1a\u4e0a\u516c\u5e03\u4e86\u65b0\u6570\u636e\uff0c\u8fdb\u4e00\u6b65\u8bc1\u660e\u4e86 SAT-3247 \u5bf9\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (Duchenne \u6216 DMD) \u7684\u6210\u5e74\u4eba (20-27 \u5c81) \u7684\u8010\u53d7\u6027\u548c\u521d\u6b65\u7597\u6548\u3002<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u76ee\u5f55<\/h2><nav><ul><li><a href=\"#key-findings\">\u4e3b\u8981\u53d1\u73b0<\/a><\/li><li><a href=\"#increase-in-grip-strength\">\u589e\u52a0\u63e1\u529b<\/a><\/li><li><a href=\"#regardless-specific-dystrophin-mutation\">\u72ec\u7acb\u4e8e\u7279\u5b9a\u5916\u663e\u5b50\u7a81\u53d8<\/a><\/li><li><a href=\"#future-clinical-trial-plans\">\u672a\u6765\u7684\u4e34\u5e8a\u8bd5\u9a8c\u8ba1\u5212<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"key-findings\">\u4e3b\u8981\u53d1\u73b0<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u63a5\u53d7 SAT-3247 \u6cbb\u7597 28 \u5929\u540e\uff0c\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u6210\u5e74\u4eba\u8868\u73b0\u51fa\u8d85\u8d8a\u81ea\u7136\u75c5\u7a0b\u7684\u529f\u80fd\u6539\u5584<\/strong><\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u63e1\u529b\u589e\u52a0 118.6%\uff0c\u9884\u8ba1\u7528\u529b\u80ba\u6d3b\u91cf\u589e\u52a0 5.8%\uff1b\u7136\u800c\uff0c\u81ea\u7136\u53f2\u4e2d\u4e24\u8005\u90fd\u4e0b\u964d<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>SAT-3247 \u5728 1 \u671f a\/b \u671f\u7814\u7a76\u7684\u6240\u6709\u90e8\u5206\u5747\u8868\u73b0\u51fa\u5b89\u5168\u6027\u3001\u8010\u53d7\u6027\u548c\u9884\u671f\u836f\u4ee3\u52a8\u529b\u5b66 (PK)<\/strong><\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u4e16\u754c\u808c\u8089\u5b66\u4f1a\u7b2c 30 \u5c4a\u5e74\u4f1a\u6700\u65b0\u6d77\u62a5\u5c55\u793a\u65b0\u6570\u636e<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">Satellos\u8054\u5408\u521b\u59cb\u4eba\u517c\u9996\u5e2d\u6267\u884c\u5b98\u5f17\u5170\u514b\u00b7\u683c\u91cc\u68ee\u8868\u793a\uff1a\u201cSatellos\u5728\u6210\u4eba\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u4e2d\u5f00\u5c55\u768428\u5929\u4e34\u5e8a\u7814\u7a76\u4e2d\uff0c\u6700\u65b0\u4e34\u5e8a\u7ed3\u679c\u4e3aSAT-3247\u6210\u4e3a\u5b89\u5168\u4e14\u5177\u6709\u4e34\u5e8a\u610f\u4e49\u7684\u6cbb\u7597\u65b9\u6cd5\u7684\u6f5c\u529b\u63d0\u4f9b\u4e86\u91cd\u8981\u9a8c\u8bc1\u3002\u6211\u4eec\u975e\u5e38\u5174\u594b\uff0c\u5e76\u5145\u6ee1\u4fe1\u5fc3\u5730\u63a8\u8fdb\u4e0b\u4e00\u9636\u6bb5\u7684\u4e34\u5e8a\u7814\u7a76\uff0c\u76ee\u6807\u662f\u5411\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7fa4\u4f53\u5c55\u793aSAT-3247\u7684\u53d8\u9769\u6f5c\u529b\u3002\u201d<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4f1a\u4e0a\u5c55\u793a\u7684\u6570\u636e\u8868\u660e\uff0cSAT-3247 \u5728 1a\/b \u671f\u7814\u7a76\u4e2d\u8868\u73b0\u51fa\u5b89\u5168\u6027\u548c\u826f\u597d\u7684\u8010\u53d7\u6027\uff0c\u5e76\u5177\u6709\u7406\u60f3\u7684\u836f\u4ee3\u52a8\u529b\u5b66 (PK) \u7279\u5f81\u3002\u62a5\u544a\u8fd8\u6db5\u76d6\u4e86\u5bf9\u65e9\u671f\u836f\u7269\u6548\u5e94\u63a2\u7d22\u6027\u6307\u6807\u7684\u65b0\u5206\u6790\u3002<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"increase-in-grip-strength\">\u589e\u52a0\u63e1\u529b<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u63a5\u53d7 SAT-3247 \u6cbb\u7597\u8d85\u8fc7 28 \u5929\u7684\u4e2a\u4f53\u7684\u63e1\u529b\u589e\u5f3a\u7a0b\u5ea6\u8fdc\u8fdc\u8d85\u8fc7\u8be5\u5e74\u9f84\u7ec4\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u81ea\u7136\u75c5\u7a0b\u3002<\/strong> \u5177\u4f53\u800c\u8a00\uff0c\u4f18\u52bf\u624b\u7684\u6700\u5927\u63e1\u529b\u5e73\u5747\u63d0\u9ad8\u4e86 118.6%\uff0c\u975e\u4f18\u52bf\u624b\u7684\u6700\u5927\u63e1\u529b\u5e73\u5747\u63d0\u9ad8\u4e86 97.9%\uff0c\u8fd9\u610f\u5473\u7740\u63e1\u529b\u5927\u7ea6\u7ffb\u4e86\u4e00\u756a\uff0c\u4ece\u7ea6 2 \u516c\u65a4\u589e\u52a0\u5230\u7ea6 4 \u516c\u65a4\u3002\u8fd9\u4e9b\u6539\u5584\u4e0e\u5df2\u53d1\u8868\u7684\u81ea\u7136\u75c5\u7a0b1\u4e0d\u4e00\u81f4\uff0c\u5e76\u4e14\u4e0e\u7b2c 15 \u5929\u66f4\u9ad8\u7684\u836f\u7269\u6d53\u5ea6\u548c\u66f4\u9ad8\u7684\u57fa\u7ebf\u808c\u9150\uff08\u808c\u8089\u8d28\u91cf\u589e\u52a0\u7684\u66ff\u4ee3\u6307\u6807\uff09\u76f8\u5173\uff0c\u6211\u4eec\u8ba4\u4e3a\u8fd9\u8868\u660e\u6211\u4eec\u7684\u836f\u7269\u5bf9\u808c\u8089\u4ea7\u751f\u4e86\u9884\u671f\u7684\u6548\u679c\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u6b64\u5916\uff0c\u53c2\u4e0e\u8005\u7684\u9884\u6d4b\u7528\u529b\u80ba\u6d3b\u91cf\u5e73\u5747\u63d0\u9ad8\u4e865.8%\uff1b\u8fd9\u6837\u7684\u63d0\u9ad8\u4e5f\u4e0e\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u6210\u5e74\u60a3\u8005\u6bcf\u5e74\u7ea6\u4e0b\u964d5%\u7684\u81ea\u7136\u75c5\u7a0b\u4e0d\u7b26\u3002\u7814\u7a76\u671f\u95f4\uff0c\u6240\u6709\u5176\u4ed6\u6307\u6807\u5747\u4fdd\u6301\u7a33\u5b9a\u3002\u4e24\u9879\u7814\u7a76\u5747\u672a\u89c2\u5bdf\u5230\u4e2d\u5ea6\u6216\u4ee5\u4e0a\u4e25\u91cd\u7a0b\u5ea6\u7684\u836f\u7269\u76f8\u5173\u4e0d\u826f\u4e8b\u4ef6\uff0c\u4e5f\u672a\u53d1\u751f\u5242\u91cf\u9650\u5236\u6027\u6bd2\u6027\u3002<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"regardless-specific-dystrophin-mutation\">\u72ec\u7acb\u4e8e\u7279\u5b9a\u5916\u663e\u5b50\u7a81\u53d8<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Satellos \u9996\u5e2d\u533b\u7597\u5b98 Wildon Farwell \u533b\u5b66\u535a\u58eb\u8868\u793a\uff1a\u201cSatellos \u7684\u79d1\u5b66\u8054\u5408\u521b\u59cb\u4eba\u7387\u5148\u8ba4\u8bc6\u5230\uff0c\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u4f53\u5185\u56fa\u6709\u7684\u808c\u8089\u518d\u751f\u8fc7\u7a0b\u4e25\u91cd\u53d7\u635f\u3002\u4ed6\u4eec\u53d1\u660e\u4e86 SAT-3247\uff0c\u65e8\u5728\u91cd\u542f\u8fd9\u4e00\u53d7\u635f\u7684\u518d\u751f\u8fc7\u7a0b\uff0c\u4f7f\u8eab\u4f53\u80fd\u591f\u518d\u6b21\u4fee\u590d\u548c\u91cd\u5efa\u808c\u8089\u3002\u8fd9\u4e9b\u5bf9\u665a\u671f\u6210\u5e74\u60a3\u8005\u6709\u6548\u7684\u65e9\u671f\u8ff9\u8c61\u4ee4\u4eba\u9f13\u821e\uff0c\u5e76\u652f\u6301\u6211\u4eec\u5c06\u4e34\u5e8a\u9879\u76ee\u6269\u5c55\u5230\u66f4\u5e7f\u6cdb\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7fa4\u4f53\u3002SAT-3247 \u65e8\u5728\u6210\u4e3a\u4e00\u79cd\u4fbf\u6377\u7684\u53e3\u670d\u7597\u6cd5\uff0c\u65e0\u8bba\u4e2a\u4f53\u5177\u4f53\u7684\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u7a81\u53d8\u60c5\u51b5\u5982\u4f55\uff0c\u90fd\u6709\u53ef\u80fd\u6539\u5584\u7597\u6548\u3002\u201d<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"future-clinical-trial-plans\">\u672a\u6765\u7684\u4e34\u5e8a\u8bd5\u9a8c\u8ba1\u5212<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u53c2\u4e0e1b\u671f\u4e34\u5e8a\u8bd5\u9a8c\u7684\u4e94\u540d\u5e74\u9f84\u572820-27\u5c81\u4e4b\u95f4\u7684\u6210\u5e74\u60a3\u8005\u73b0\u53d7\u9080\u53c2\u52a0\u4e00\u9879\u4e3a\u671f11\u4e2a\u6708\u7684SAT-3247\u5f00\u653e\u6807\u7b7e\u968f\u8bbf\u7814\u7a76\uff0c\u8be5\u7814\u7a76\u8fd8\u5c06\u62db\u52df\u66f4\u591a\u5e74\u9f84\u572816-25\u5c81\u4e4b\u95f4\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u7537\u6027\u60a3\u8005\u3002\u672c\u7814\u7a76\u7684\u4e3b\u8981\u7ec8\u70b9\u662f\u8bc4\u4f30SAT-3247\u7684\u957f\u671f\u5b89\u5168\u6027\u548c\u8010\u53d7\u6027\uff0c\u4ee5\u53ca\u5176\u5bf9\u80b1\u4e8c\u5934\u808c\u8102\u80aa\u5206\u6570\u7684\u5f71\u54cd\u3002\u6b21\u8981\u7ec8\u70b9\u5305\u62ecSAT-3247\u5bf9\u8102\u80aa\u5206\u6570\u7684\u5f71\u54cd\uff0c\u4ee5\u53ca\u5bf9\u808c\u8089\u529b\u91cf\u548c\u529f\u80fd\u7684\u5f71\u54cd\u3002\u53c2\u4e0e\u8005\u5b8c\u62103\u4e2a\u6708\u7684\u968f\u8bbf\u540e\uff0c\u516c\u53f8\u5c06\u63d0\u4f9b\u521d\u6b65\u7684\u4e2d\u671f\u7ed3\u679c\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u57fa\u4e8e1a\/b\u671f\u8bd5\u9a8c\u7684\u521d\u6b65\u5b89\u5168\u6027\u548c\u6709\u6548\u6027\u6570\u636e\uff0cSatellos\u8fd8\u8ba1\u5212\u5f00\u5c55\u4e00\u9879\u9488\u5bf9\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u7684\u95e8\u8bca\u513f\u7ae5\u76842\u671f\u968f\u673a\u3001\u53cc\u76f2\u3001\u5b89\u6170\u5242\u5bf9\u7167\u3001\u5168\u7403\u6982\u5ff5\u9a8c\u8bc1\u6027\u7814\u7a76\uff0c\u4ee5\u8bc4\u4f30SAT-3247\u7684\u7597\u6548\u3002\u4e3b\u8981\u7ec8\u70b9\u5c06\u8bc4\u4f30SAT-3247\u7684\u5b89\u5168\u6027\u548c\u8010\u53d7\u6027\u4ee5\u53ca\u5bf9\u808c\u8089\u529b\u91cf\u7684\u5f71\u54cd\u3002\u6b21\u8981\u7ec8\u70b9\u5c06\u8bc4\u4f30SAT-3247\u5bf9\u808c\u8089\u8d28\u91cf\u3001\u529f\u80fd\u548c\u518d\u751f\u7684\u5f71\u54cd\u3002\u8be5\u516c\u53f8\u8fd1\u671f\u5df2\u5728\u7f8e\u56fd\u548c\u5168\u7403\u63d0\u4ea4\u4e86\u76d1\u7ba1\u6587\u4ef6\uff0c\u4ee5\u63a8\u8fdb\u8fd9\u9879\u7814\u7a76\u3002<\/p>","protected":false},"excerpt":{"rendered":"<p>Satellos Bioscience announced new data further demonstrating tolerability and initial efficacy of SAT-3247 in adults (aged 20-27 years) with Duchenne muscular dystrophy (Duchenne or DMD) at the 30th Annual Congress of the World Muscle Society in Vienna, Austria. Key Findings \u201cSatellos\u2019 new and updated clinical results from the 28-day clinical study in adults with Duchenne [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4777,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[254,251,252,253],"class_list":["post-4776","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-frank-gleeson","tag-sat-3247","tag-satellos","tag-satellos-bioscience"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4776","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=4776"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4776\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/4777"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=4776"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=4776"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=4776"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}