{"id":4735,"date":"2025-10-07T11:45:03","date_gmt":"2025-10-07T08:45:03","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4735"},"modified":"2025-11-03T20:19:16","modified_gmt":"2025-11-03T17:19:16","slug":"form-bio-and-cure-rare-disease-partnership-for-duchenne-muscular-dystrophy-program","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/form-bio-and-cure-rare-disease-partnership-for-duchenne-muscular-dystrophy-program\/","title":{"rendered":"Form Bio \u4e0e Cure Rare Disease \u5408\u4f5c\u52a0\u901f\u57fa\u56e0\u836f\u7269\u5f00\u53d1\uff0c\u63a8\u8fdb CRD \u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u9879\u76ee"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Form Bio \u662f\u4e00\u5bb6\u4eba\u5de5\u667a\u80fd\u9a71\u52a8\u7684\u57fa\u56e0\u533b\u5b66\u5f00\u53d1\u548c\u57fa\u56e0\u7ec4\u5de5\u7a0b\u9886\u57df\u7684\u9886\u5bfc\u8005\uff0c\u8be5\u516c\u53f8\u5ba3\u5e03\u4e0e Cure Rare Disease (CRD) \u5efa\u7acb\u6218\u7565\u5408\u4f5c\u4f19\u4f34\u5173\u7cfb\u3002CRD \u662f\u4e00\u5bb6\u975e\u8425\u5229\u6027\u751f\u7269\u6280\u672f\u516c\u53f8\uff0c\u81f4\u529b\u4e8e\u5f00\u53d1\u7528\u4e8e\u6cbb\u7597\u7f55\u89c1\u548c\u6781\u7f55\u89c1\u795e\u7ecf\u808c\u8089\u75be\u75c5\u548c\u795e\u7ecf\u9000\u884c\u6027\u75be\u75c5\u7684\u57fa\u56e0\u7597\u6cd5\u3002\u53cc\u65b9\u5c06\u643a\u624b\u52a0\u901f\u5f00\u5c55\u9879\u76ee\uff0c\u4ee5\u8bc6\u522b\u548c\u4f18\u5316\u591a\u79cd\u5148\u5bfc\u9002\u5e94\u75c7\uff0c\u9996\u5148\u662f\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD)\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u901a\u8fc7\u6b64\u6b21\u5408\u4f5c\uff0cForm Bio \u5c06\u5229\u7528\u5176\u4e13\u6709\u7684\u8ba1\u7b97\u673a\u6a21\u62df\u5e73\u53f0\u5f00\u5c55\u4eba\u5de5\u667a\u80fd\u7814\u7a76\uff0c\u652f\u6301 CRD \u5f00\u53d1\u9488\u5bf9\u5305\u88c5\u3001\u8868\u8fbe\u3001\u5b89\u5168\u6027\u548c\u53ef\u5236\u9020\u6027\u8fdb\u884c\u4f18\u5316\u7684\u57fa\u56e0\u6cbb\u7597\u5019\u9009\u836f\u7269\uff0c\u8fd9\u4e9b\u662f\u786e\u4fdd\u4e34\u5e8a\u6210\u529f\u548c\u964d\u4f4e\u6210\u672c\u7684\u5173\u952e\u56e0\u7d20\u3002<\/strong> \u8be5\u8ba1\u5212\u65e8\u5728\u7b80\u5316\u4e3b\u8981\u5019\u9009\u836f\u7269\u7684\u9009\u62e9\uff0c\u52a0\u5feb\u5f00\u53d1\u65f6\u95f4\u8868\uff0c\u5e76\u6539\u5584\u76ee\u524d\u7f3a\u4e4f\u6cbb\u7597\u9009\u62e9\u7684\u4e25\u91cd\u795e\u7ecf\u808c\u8089\u75be\u75c5\u60a3\u8005\u7684\u6cbb\u7597\u6548\u679c\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">CRD \u6700\u521d\u4e0e Form Bio \u5408\u4f5c\uff0c\u65e8\u5728\u6539\u8fdb\u4e00\u79cd\u5c1a\u672a\u9488\u5bf9\u751f\u4ea7\u6216\u964d\u4f4e\u514d\u75ab\u539f\u6027\u8fdb\u884c\u4f18\u5316\u7684 DMD \u5019\u9009\u836f\u7269\u3002Form Bio \u5229\u7528\u957f\u8bfb\u6d4b\u5e8f\u3001\u57fa\u56e0\u7ec4\u5b8c\u6574\u6027\u5206\u6790\u3001\u5408\u7406\u8bbe\u8ba1\u4ee5\u53ca AI\/ML \u6a21\u578b\uff0c\u53d1\u73b0\u4e86\u53ef\u80fd\u963b\u788d\u4e34\u5e8a\u6210\u529f\u7684\u5305\u88c5\u6548\u7387\u4f4e\u4e0b\u95ee\u9898\u3002 <strong>\u901a\u8fc7\u4fee\u6539\u542f\u52a8\u5b50\u548c\u4f18\u5316\u6838\u9178\u9176\uff0cForm Bio\u5c06AAV\u5168\u57fa\u56e0\u7ec4\u7684\u6bd4\u4f8b\u4ece13%\u63d0\u9ad8\u523059%\uff0c\u5728\u77ed\u77ed\u4e00\u4e2a\u6708\u5185\u5b9e\u73b0\u4e86\u6cbb\u7597\u4ea7\u91cf\u76844.4\u500d\u63d0\u9ad8\u3002<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c\u5bf9\u4e8e\u9762\u4e34\u7f55\u89c1\u795e\u7ecf\u808c\u8089\u75be\u75c5\u548c\u795e\u7ecf\u9000\u884c\u6027\u75be\u75c5\u7684\u60a3\u8005\u53ca\u5176\u5bb6\u5ead\u6765\u8bf4\uff0c\u65f6\u95f4\u81f3\u5173\u91cd\u8981\uff0c\u201dCure Rare Disease \u521b\u59cb\u4eba\u517c\u9996\u5e2d\u6267\u884c\u5b98 Richard Horgan \u8868\u793a\u3002\u201cForm Bio \u7684\u4e13\u4e1a\u77e5\u8bc6\u548c\u6280\u672f\u5df2\u7ecf\u4e3a\u6211\u4eec\u7684 DMD \u9879\u76ee\u5e26\u6765\u4e86\u663e\u8457\u7684\u6539\u8fdb\uff0c\u4f7f\u5176\u80fd\u591f\u4ee5\u663e\u8457\u66f4\u9ad8\u7684\u53ef\u751f\u4ea7\u6027\u548c\u6548\u7387\u63a8\u8fdb\u5230\u4f53\u5185\u4e34\u5e8a\u524d\u7814\u7a76\u9636\u6bb5\u3002\u6b64\u6b21\u5408\u4f5c\u662f\u4e00\u4e2a\u5f3a\u6709\u529b\u7684\u8303\u4f8b\uff0c\u5c55\u73b0\u4e86\u975e\u8425\u5229\u7ec4\u7ec7\u548c\u6280\u672f\u9886\u8896\u5982\u4f55\u643a\u624b\u52a0\u901f\u5f00\u53d1\u6539\u53d8\u88ab\u5ffd\u89c6\u4eba\u7fa4\u547d\u8fd0\u7684\u7597\u6cd5\u3002\u201d<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Form Bio \u603b\u88c1\u517c\u9996\u5e2d\u6267\u884c\u5b98\u9648\u6653\u71d5\u535a\u58eb\u8868\u793a\uff1a\u201cForm Bio \u7684\u4f7f\u547d\u662f\u8d4b\u80fd Cure Rare Disease \u7b49\u5408\u4f5c\u4f19\u4f34\uff0c\u5229\u7528\u6211\u4eec\u57fa\u4e8e\u4eba\u5de5\u667a\u80fd\u7684\u6d1e\u5bdf\uff0c\u5c06\u751f\u7269\u5b66\u8f6c\u5316\u4e3a\u5de5\u7a0b\u5316\u7684\u53ef\u7f16\u7a0b\u7cfb\u7edf\u3002\u901a\u8fc7\u9884\u5148\u4f18\u5316 AAV \u8f7d\u4f53\u8bbe\u8ba1\uff0c\u6211\u4eec\u53ef\u4ee5\u964d\u4f4e\u6574\u4e2a\u57fa\u56e0\u6cbb\u7597\u5f00\u53d1\u6d41\u7a0b\u7684\u65f6\u95f4\u3001\u6210\u672c\u548c\u98ce\u9669\u3002\u6211\u4eec\u5f88\u8363\u5e78\u80fd\u591f\u52a9\u529b CRD \u4e3a\u76ee\u524d\u522b\u65e0\u9009\u62e9\u7684\u60a3\u8005\u63d0\u4f9b\u6025\u9700\u7684\u6cbb\u7597\u65b9\u6848\u3002\u201d<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c\uff08\u6240\u6709\u7814\u7a76\u5217\u8868\uff09<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Form Bio \u548c CRD \u5171\u540c\u5c55\u793a\u4e86\u5148\u8fdb\u7684\u8ba1\u7b97\u5de5\u5177\u548c\u4ee5\u60a3\u8005\u4e3a\u4e2d\u5fc3\u7684\u751f\u7269\u6280\u672f\u521b\u65b0\u5982\u4f55\u52a0\u901f\u7a81\u7834\u3001\u964d\u4f4e\u6210\u672c\u5e76\u4e3a\u8feb\u5207\u672a\u6ee1\u8db3\u9700\u6c42\u7684\u60a3\u8005\u5e26\u6765\u66f4\u5b89\u5168\u3001\u66f4\u6709\u6548\u7684\u6cbb\u7597\u65b9\u6cd5\u3002<\/p>","protected":false},"excerpt":{"rendered":"<p>Form Bio, a leader in AI-powered genetic medicine development and genome engineering, announced a strategic partnership with Cure Rare Disease (CRD), a nonprofit biotechnology company developing genetic therapies for the treatment of rare and ultra-rare neuromuscular and neurodegenerative diseases. Together, the organizations will accelerate programs to identify and optimize multiple lead indications, beginning with Duchenne [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4737,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[431,430],"class_list":["post-4735","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-cure-rare-disease","tag-form-bio"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4735","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=4735"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4735\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/4737"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=4735"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=4735"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=4735"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}