{"id":4428,"date":"2025-09-07T13:07:26","date_gmt":"2025-09-07T10:07:26","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4428"},"modified":"2025-11-03T20:20:56","modified_gmt":"2025-11-03T17:20:56","slug":"gnr-097-duchenne-gene-therapy-phase-1-2-study-started-by-generium","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/gnr-097-duchenne-gene-therapy-phase-1-2-study-started-by-generium\/","title":{"rendered":"GNR-097\uff1a\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u57fa\u56e0\u6cbb\u75971\/2\u671f\u7814\u7a76\u7531Generium\u542f\u52a8"},"content":{"rendered":"

Generium\u662f\u4e00\u5bb6\u4fc4\u7f57\u65af\u521b\u65b0\u751f\u7269\u6280\u672f\u516c\u53f8\uff0c\u5df2\u83b7\u5f97\u6279\u51c6\u8fdb\u884cGNR-097\u57fa\u56e0\u6cbb\u7597\u836f\u7269\u7684\u4e34\u5e8a\u8bd5\u9a8c\uff0c\u7528\u4e8e\u6cbb\u7597\u8fdb\u884c\u6027\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u3002<\/strong><\/p>\n\n\n\n

\u8fd9\u9879\u591a\u4e2d\u5fc3\u3001\u5355\u76f2\u3001\u968f\u673a\u3001\u5b89\u6170\u5242\u5bf9\u7167\u8bd5\u9a8c\u6d89\u53ca\u5bf9\u60a3\u6709\u8fdb\u884c\u6027\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u513f\u79d1\u60a3\u8005\u8fdb\u884c\u5355\u6b21\u9759\u8109\u6ce8\u5c04\u57fa\u56e0\u6cbb\u7597\u836f\u7269\u3002\u8fd9\u98791\/2\u671f\u7814\u7a76\u65e8\u5728\u8bc4\u4f30GNR-097\u836f\u7269\u7684\u8010\u53d7\u6027\u3001\u5b89\u5168\u6027\u548c\u6709\u6548\u6027\u3002<\/p>\n\n\n\n

GNR-097 \u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u57fa\u56e0\u6cbb\u7597<\/h2>\n\n\n\n

GNR-097 \u662f\u8840\u6e05\u578b 9 \u7684\u91cd\u7ec4\u817a\u76f8\u5173\u75c5\u6bd2\u8f7d\u4f53\uff0c\u7f16\u7801\u622a\u77ed\u7684\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u57fa\u56e0\u3002<\/strong><\/p>\n\n\n\n

GENERIUM \u9996\u5e2d\u6267\u884c\u5b98\u4e39\u5c3c\u5c14\u00b7\u5854\u5229\u626c\u65af\u57fa (Daniil Talyansky)\uff1a<\/h2>\n\n\n\n

\u57fa\u56e0\u6cbb\u7597\u662f\u5168\u7403\u5236\u836f\u548c\u533b\u5b66\u9886\u57df\u6700\u5e74\u8f7b\u3001\u6700\u5177\u7a81\u7834\u6027\u7684\u9886\u57df\u3002\u4fc4\u7f57\u65af\u79d1\u5b66\u5bb6\u51ed\u501f\u5176\u72ec\u7279\u7684\u4e13\u4e1a\u77e5\u8bc6\uff0c\u6210\u529f\u5f00\u53d1\u51fa\u4e00\u79cd\u7f16\u7801\u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u57fa\u56e0\u7684\u91cd\u7ec4\u817a\u76f8\u5173\u75c5\u6bd2\u8f7d\u4f53\u3002\u6211\u4eec\u76ee\u524d\u6b63\u5728\u542f\u52a8\u8fd9\u79cd\u5177\u6709\u5de8\u5927\u524d\u666f\u7684\u539f\u521b\u836f\u7269\u7684\u4e34\u5e8a\u8bd5\u9a8c\u3002<\/p>\n\n\n\n

GNR-097\u57fa\u56e0\u6cbb\u7597\u4e34\u5e8a\u8bd5\u9a8c<\/h2>\n\n\n\n

\u8fd9\u6b3e\u521b\u65b0\u836f\u7269\u7684\u8bd5\u9a8c\u662f\u56fd\u9645\u6027\u7684\uff0c\u5c06\u5728\u4fc4\u7f57\u65af\u8054\u90a6\u548c\u767d\u4fc4\u7f57\u65af\u5171\u548c\u56fd\u8fdb\u884c\u3002\u5728\u4fc4\u7f57\u65af\uff0c\u8be5\u7814\u7a76\u5c06\u5728\u4e94\u5bb6\u533b\u7597\u4e2d\u5fc3\u8fdb\u884c\uff1a\u5c24\u00b7\u4f0a\u00b7\u7ef4\u5c14\u5b63\u8c22\u592b\u9662\u58eb\u513f\u79d1\u548c\u513f\u79d1\u5916\u79d1\u4e34\u5e8a\u7814\u7a76\u6240\u3001\u76ae\u7f57\u6208\u592b\u4fc4\u7f57\u65af\u56fd\u7acb\u7814\u7a76\u533b\u79d1\u5927\u5b66\u3001\u5723\u5f7c\u5f97\u5821\u56fd\u7acb\u513f\u79d1\u5927\u5b66\u3001\u53f6\u5361\u6377\u7433\u5821\u5730\u533a\u513f\u7ae5\u4e34\u5e8a\u533b\u9662\u548c\u56fd\u5bb6\u513f\u7ae5\u5065\u5eb7\u533b\u5b66\u7814\u7a76\u4e2d\u5fc3\u3002\u5728\u767d\u4fc4\u7f57\u65af\uff0c\u8be5\u8bd5\u9a8c\u5c06\u5728\u5171\u548c\u56fd\u79d1\u5b66\u5b9e\u8df5\u4e2d\u5fc3\u201c\u6bcd\u5a74\u201d\u8fdb\u884c\u3002<\/p>\n\n\n\n

\u9605\u8bfb\u66f4\u591a<\/strong>:\u00a0\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c\uff08\u6240\u6709\u7814\u7a76\u5217\u8868\uff09<\/a><\/p>","protected":false},"excerpt":{"rendered":"

Generium is a Russian innovative biotechnology company has received approval to conduct a clinical trial of GNR-097 gene therapy drug for the treatment of progressive Duchenne muscular dystrophy (DMD). The multicenter, single-blind, randomized placebo-controlled trial involves a single intravenous administration of the gene therapy drug to pediatric patients with progressive Duchenne muscular dystrophy. This Phase […]<\/p>\n","protected":false},"author":1,"featured_media":4430,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[137,415,61,241,414,135],"class_list":["post-4428","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-clinical-trial","tag-daniil-talyansky","tag-gene-therapy","tag-generium","tag-gnr-097","tag-russia"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4428","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=4428"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4428\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/4430"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=4428"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=4428"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=4428"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}