{"id":4350,"date":"2025-08-19T14:31:34","date_gmt":"2025-08-19T11:31:34","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4350"},"modified":"2025-08-19T15:44:33","modified_gmt":"2025-08-19T12:44:33","slug":"itf-therapeutics-launching-a-study-to-evaluate-the-real-world-experience-of-duvyzat-givinostat-in-patients-with-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/itf-therapeutics-launching-a-study-to-evaluate-the-real-world-experience-of-duvyzat-givinostat-in-patients-with-duchenne-muscular-dystrophy\/","title":{"rendered":"ITF Therapeutics \u542f\u52a8\u4e00\u9879\u7814\u7a76\uff0c\u8bc4\u4f30 Duvyzat\uff08Givinostat\uff09\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u771f\u5b9e\u4e16\u754c\u4f53\u9a8c"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u8fd9\u9879\u524d\u77bb\u6027\u89c2\u5bdf\u6027\u7814\u7a76 (NCT07127978) \u65e8\u5728\u8bc4\u4f30\u9996\u6b21\u53e3\u670d Duvyzat\uff08Givinostat\uff09\u6216\u5df2\u5728\u7f8e\u56fd\u6807\u51c6\u4e34\u5e8a\u6cbb\u7597\u4e2d\u63a5\u53d7\u6cbb\u7597\uff086 \u4e2a\u6708\u5185\uff09\u7684 DMD \u60a3\u8005\u7684\u5b89\u5168\u6027\u3001\u8010\u53d7\u6027\u548c\u529f\u80fd\u6027\u7ed3\u679c\u3002\u8be5\u8bd5\u9a8c\u7684\u5165\u7ec4\u671f\u4e3a 24 \u4e2a\u6708\uff0c\u968f\u8bbf\u671f\u81f3\u5c11\u4e3a 2 \u5e74\uff0c\u9884\u8ba1\u521d\u59cb\u62db\u52df\u7684\u60a3\u8005\u5c06\u6301\u7eed\u957f\u8fbe 5 \u5e74\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e86\u89e3\u66f4\u591a<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/zh\/duvyzat-givinostat-nonsteroidal-drug\/\" target=\"_blank\" rel=\"noreferrer noopener\">Duvyzat (Givinostat) \u662f\u4ec0\u4e48\uff1f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u7814\u7a76\u5c06\u62db\u52df300\u540d\u53c2\u4e0e\u8005\uff08180\u540d\u975e\u5367\u5e8a\u60a3\u8005\u548c\u6700\u591a120\u540d\u5367\u5e8a\u60a3\u8005\uff09\u3002\u53c2\u4e0e\u8005\u5c06\u63a5\u53d7\u81f3\u5c11\u4e24\u5e74\u7684\u968f\u8bbf\uff0c\u5e76\u5728\u5e38\u89c4\u4e34\u5e8a\u8bbf\u89c6\u671f\u95f4\u6536\u96c6\u6570\u636e\u3002\u8bc4\u4f30\u5305\u62ec\u5b9e\u9a8c\u5ba4\u53c2\u6570\uff08\u4f8b\u5982\u8840\u5c0f\u677f\u8ba1\u6570\u3001\u7518\u6cb9\u4e09\u916f\uff09\u3001\u5fc3\u80ba\u529f\u80fd\u3001\u60a3\u8005\u62a5\u544a\u7ed3\u679c\u4ee5\u53ca\u8fd0\u52a8\u529f\u80fd\u91cf\u8868\uff0c\u4f8b\u5982\u5317\u6781\u661f\u5367\u5e8a\u8bc4\u4f30\u91cf\u8868 (NSAA) \u548c\u4e0a\u80a2\u8868\u73b0\u91cf\u8868 (PUL)\u3002<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Duvyzat\uff08Givinostat\uff09\u7814\u7a76 - NCT07127978 -<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u672c\u7814\u7a76\u8bc4\u4f30\u4e86 Givinostat \u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u771f\u5b9e\u4f53\u9a8c\u3002 <\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5b66\u4e60\u5f00\u59cb\u65f6\u95f4\uff08\u9884\u8ba1\uff09<\/strong>: 2025-09-15<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5c0f\u5b66\u5b8c\u6210\u60c5\u51b5\uff08\u9884\u8ba1\uff09\uff1a<\/strong> 2030-06-30<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7814\u7a76\u5b8c\u6210\u60c5\u51b5\uff08\u9884\u8ba1\uff09<\/strong>: 2030-07-30<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u53c2\u4e0e\u4eba\u6570\uff08\u9884\u8ba1\uff09<\/strong>: 300<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5b66\u4e60\u7c7b\u578b<\/strong>\uff1a\u89c2\u5bdf<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4f4d\u7f6e<\/strong>\uff1a\u5c1a\u65e0\u4f4d\u7f6e\u6570\u636e\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9002\u5408\u5b66\u4e60\u7684\u5e74\u9f84<\/strong>\uff1a6\u5c81\u4ee5\u4e0a\uff08\u513f\u7ae5\u3001\u6210\u4eba\u3001\u8001\u5e74\u4eba\uff09<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4e3b\u8981\u7eb3\u5165\u548c\u6392\u9664\u6807\u51c6\u3002\u2013 <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT07127978\" target=\"_blank\" rel=\"noreferrer noopener\">NCT07127978<\/a> \u2013<\/p>","protected":false},"excerpt":{"rendered":"<p>The purpose of this prospective observational study (NCT07127978) is to assess the safety, tolerability, and functional results of DMD patients who are starting oral Duvyzat (Givinostat) for the first time or who have already begun therapy within six months as part of standard clinical care in the United States. With a 24-month enrollment period and [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4353,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[46,47],"class_list":["post-4350","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-duvyzat","tag-givinostat"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4350","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=4350"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4350\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/4353"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=4350"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=4350"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=4350"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}