{"id":4142,"date":"2025-07-17T12:11:19","date_gmt":"2025-07-17T09:11:19","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4142"},"modified":"2025-11-03T20:21:36","modified_gmt":"2025-11-03T17:21:36","slug":"insmed-ins1201-gene-therapy-phase-1-clinical-trial-nct06817382","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/insmed-ins1201-gene-therapy-phase-1-clinical-trial-nct06817382\/","title":{"rendered":"INS1201\u57fa\u56e0\u7597\u6cd51\u671f\u4e34\u5e8a\u8bd5\u9a8c\u5f00\u59cb"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Insmed\u5728ClinicalTrials.gov\u4e0a\u53d1\u5e03\u7684ID\u4e3aNCT06817382\u7684\u9875\u9762\u4e0a\u5ba3\u5e03\uff0c\u5c06\u542f\u52a8\u9488\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u5f00\u53d1\u7684INS1201\u57fa\u56e0\u7597\u6cd5\u76841\u671f\u8bd5\u9a8c\u3002<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u76ee\u5f55<\/h2><nav><ul><li><a href=\"#bbm-d-101-gene-therapy-phase-1-2-clinical-trial\">INS1201\u57fa\u56e0\u6cbb\u75971\u671f\u4e34\u5e8a\u8bd5\u9a8c<\/a><\/li><li><a href=\"#what-is-insmed-ins-1201-gene-therapy\">\u4ec0\u4e48\u662f Insmed INS1201 \u57fa\u56e0\u6cbb\u7597\uff1f<\/a><\/li><li><a href=\"#bbm-d-101-clinical-trial-nct-07058662\">INS1201\u4e34\u5e8a\u8bd5\u9a8c \u2013 NCT06817382<\/a><\/li><li><a href=\"#bbm-d-101-phase-1-2-participation-criteria\">INS1201 \u7b2c\u4e00\u9636\u6bb5\u53c2\u4e0e\u6807\u51c6<\/a><\/li><li><a href=\"#how-can-i-contact-with-belief-bio-med\">\u6211\u5982\u4f55\u8054\u7cfb Insmed\uff1f<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-gene-therapy-phase-1-2-clinical-trial\">INS1201\u57fa\u56e0\u6cbb\u75971\u671f\u4e34\u5e8a\u8bd5\u9a8c<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u672c\u7814\u7a76\u7684\u4e3b\u8981\u76ee\u7684\u662f\u8bc4\u4f30\u5bf9\u60a3\u6709 DMD \u7684\u7537\u6027\u95e8\u8bca\u60a3\u8005\u901a\u8fc7 IT \u7ed9\u836f\u5355\u5242\u91cf INS1201 \u7684\u5b89\u5168\u6027\u548c\u8010\u53d7\u6027\u3002<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-is-insmed-ins-1201-gene-therapy\">\u4ec0\u4e48\u662f Insmed INS1201 \u57fa\u56e0\u6cbb\u7597\uff1f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">INS1201 \u76f4\u63a5\u4f5c\u7528\u4e8e\u4e2d\u67a2\u795e\u7ecf\u7cfb\u7edf\uff0c\u901a\u8fc7\u9798\u5185\u7ed9\u836f\uff0c\u800c Elevidys \u5219\u9700\u8981\u5168\u8eab\u9759\u8109\u6ce8\u5c04\u3002\u8fd9\u79cd\u6709\u9488\u5bf9\u6027\u7684\u7ed9\u836f\u7b56\u7565\u65e8\u5728\u89e3\u51b3\u5168\u8eab\u57fa\u56e0\u6cbb\u7597\u7684\u5b89\u5168\u6027\u548c\u6709\u6548\u6027\u95ee\u9898\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u9798\u5185\u7ed9\u836f\u53ef\u5c06\u6240\u9700\u5242\u91cf\u5927\u5e45\u964d\u4f4e 10 \u81f3 50 \u500d\uff0c\u901a\u8fc7\u5c06\u836f\u7269\u96c6\u4e2d\u5728\u9700\u8981\u7684\u5730\u65b9\uff0c\u53ef\u9632\u6b62\u5168\u8eab\u6bd2\u6027\u548c\u8131\u9776\u6548\u5e94\u3002\u5c3d\u7ba1\u5b58\u5728\u810a\u9ad3\u635f\u4f24\u3001\u795e\u7ecf\u635f\u4f24\u548c\u611f\u67d3\u98ce\u9669\u7b49\u969c\u788d\uff0c\u4f46\u8fd9\u53ef\u80fd\u4e3a\u60a3\u8005\u63d0\u4f9b\u66f4\u5b89\u5168\u3001\u66f4\u6210\u529f\u7684\u9009\u62e9\uff0c\u5c24\u5176\u662f\u8003\u8651\u5230\u9759\u8109\u6cbb\u7597\u4e2d\u4f7f\u7528\u7684\u5927\u5242\u91cf\u75c5\u6bd2\u8f7d\u4f53\u7684\u5b89\u5168\u95ee\u9898\u3002<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-clinical-trial-nct-07058662\">INS1201\u4e34\u5e8a\u8bd5\u9a8c \u2013 NCT06817382<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5b66\u4e60\u5f00\u59cb\u65f6\u95f4\uff08\u9884\u8ba1\uff09<\/strong>: 2025-05-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u5c0f\u5b66\u5b8c\u6210\u60c5\u51b5\uff08\u9884\u8ba1\uff09<\/strong>: 2028-01-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7814\u7a76\u5b8c\u6210\u60c5\u51b5\uff08\u9884\u8ba1\uff09<\/strong>: 2028-03-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u53c2\u4e0e\u4eba\u6570\uff08\u9884\u8ba1\uff09<\/strong>\uff1a12\uff08\u7537\u6027\uff09<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4f4d\u7f6e<\/strong>\uff1a\u7f8e\u56fd<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9002\u5408\u5b66\u4e60\u7684\u5e74\u9f84<\/strong>\uff1a2\u5c81\u81f34\u5c81\uff08\u513f\u7ae5\uff09<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-phase-1-2-participation-criteria\">INS1201 \u7b2c\u4e00\u9636\u6bb5\u53c2\u4e0e\u6807\u51c6<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u53d7\u8bd5\u8005\u5fc5\u987b\u7b26\u5408\u7eb3\u5165\u6807\u51c6\u624d\u6709\u8d44\u683c\u53c2\u4e0e\u3002\u5982\u679c\u53d7\u8bd5\u8005\u60a3\u6709\u5176\u4ed6\u75be\u75c5\u6216\u6b63\u5728\u63a5\u53d7\u5176\u4ed6\u6cbb\u7597\uff0c\u5bfc\u81f4\u65e0\u6cd5\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\uff0c\u5219\u53ef\u80fd\u65e0\u6cd5\u53c2\u4e0e\u3002\u70b9\u51fb\u6b64\u7814\u7a76\u94fe\u63a5\uff0c\u5373\u53ef\u67e5\u770b\u5b8c\u6574\u7684\u7eb3\u5165\u548c\u6392\u9664\u6807\u51c6\uff1a <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06817382\" target=\"_blank\" rel=\"noreferrer noopener\">NCT06817382<\/a> \u2013\u3002<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"how-can-i-contact-with-belief-bio-med\">\u6211\u5982\u4f55\u8054\u7cfb Insmed\uff1f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u59d3\u540d<\/strong>: Insmed \u533b\u7597\u4fe1\u606f<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7535\u8bdd\u53f7\u7801<\/strong>: 18444467633<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7535\u5b50\u90ae\u4ef6<\/strong>\u90ae\u7bb1\uff1amedicalinformation@insmed.com<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c\uff08\u6240\u6709\u7814\u7a76\u5217\u8868\uff09<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Insmed was announced on the page published on ClinicalTrials.gov with the ID NCT06817382 that the phase 1 trials of INS1201 gene therapy developed for Duchenne Muscular Dystrophy will be initiated. INS1201 Gene Therapy Phase 1 Clinical Trial The primary objective of this study is to evaluate the safety and tolerability of a single dose of [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4148,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[137,61,173,174,172],"class_list":["post-4142","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-clinical-trial","tag-gene-therapy","tag-ins1201","tag-ins1201-gene-therapy","tag-insmed"],"subtitle":"Insmed\u5ba3\u5e03\u5176\u6b63\u5728\u7814\u53d1\u7684\u57fa\u56e0\u7597\u6cd5INS1201\u542f\u52a81\u671f\u4e34\u5e8a\u8bd5\u9a8c\uff08NCT06817382\uff09\u3002\u76ee\u524d\u6b63\u5728\u8fdb\u884c\u4e34\u5e8a\u8bd5\u9a8c\u3002\u7acb\u5373\u4e86\u89e3\u5982\u4f55\u53c2\u4e0eINS1201\u57fa\u56e0\u7597\u6cd5\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u4e34\u5e8a\u8bd5\u9a8c\u3002","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4142","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=4142"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4142\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/4148"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=4142"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=4142"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=4142"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}