{"id":4108,"date":"2025-07-16T10:53:45","date_gmt":"2025-07-16T07:53:45","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4108"},"modified":"2025-07-16T10:53:47","modified_gmt":"2025-07-16T07:53:47","slug":"sarepta-therapeutics-halts-elevidys-shipments-for-non-ambulatory-dmd-patients","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/sarepta-therapeutics-halts-elevidys-shipments-for-non-ambulatory-dmd-patients\/","title":{"rendered":"Sarepta Therapeutics \u505c\u6b62\u5411\u975e\u5367\u5e8a\u6027 DMD \u60a3\u8005\u53d1\u8d27 ELEVIDYS"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u7531\u4e8e\u6709\u4e24\u8d77\u5bfc\u81f4\u6b7b\u4ea1\u7684\u4e25\u91cd\u809d\u529f\u80fd\u8870\u7aed\u4e8b\u4ef6\uff0cSarepta Therapeutics \u5df2\u505c\u6b62\u5411\u60a3\u6709\u975e\u6b65\u884c\u6027\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u60a3\u8005\u8fd0\u9001\u5176\u57fa\u56e0\u6cbb\u7597\u836f\u7269 ELEVIDYS\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u6700\u8fd1\u53bb\u4e16\u7684\u60a3\u8005\u5e74\u4ec515\u5c81\u3002\u4e3a\u4e86\u8c03\u6574\u65b9\u6848\u5e76\u8003\u8651\u76d1\u7ba1\u65b9\u9762\u7684\u56e0\u7d20\uff0cSarepta \u51b3\u5b9a\u56e0\u8fd9\u4e9b\u4e25\u91cd\u4e0d\u826f\u4e8b\u4ef6\u800c\u6682\u505c ENVISION \u4e09\u671f\u9a8c\u8bc1\u6027\u8bd5\u9a8c (SRP-9001-303)\uff0c\u8be5\u8bd5\u9a8c\u6d89\u53ca\u53ef\u884c\u8d70\u548c\u65e0\u6cd5\u884c\u8d70\u7684\u6210\u5e74\u60a3\u8005\u3002 <strong>\u9605\u8bfb\u66f4\u591a<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/zh\/three-ongoing-clinical-trials-of-elevidys-gene-therapy-temporarily-halted-in-europe\/\">\u6b27\u6d32\u6682\u505c\u4e09\u9879\u6b63\u5728\u8fdb\u884c\u7684 Elevidys \u57fa\u56e0\u7597\u6cd5\u4e34\u5e8a\u8bd5\u9a8c<\/a> \u2013<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4e24\u4f8b\u6b7b\u4ea1\u75c5\u4f8b\u4e8e2025\u5e746\u6708\u62a5\u544a\uff0cFDA\u4e8e2025\u5e746\u670824\u65e5\u53d1\u5e03\u5b89\u5168\u901a\u62a5\uff0c\u4ee5\u8c03\u67e5\u4e0eELEVIDYS\u76f8\u5173\u7684\u6025\u6027\u809d\u8870\u7aed\u6f5c\u5728\u98ce\u9669\u3002\u4e3a\u6b64\uff0cSarepta\u6682\u505c\u4e86\u5176ENVISION 3\u671f\u8bd5\u9a8c\uff0c\u4ee5\u66f4\u65b0\u65b9\u6848\u5e76\u54a8\u8be2\u76d1\u7ba1\u673a\u6784\u3002\u8be5\u516c\u53f8\u8fd8\u6682\u505c\u4e86ELEVIDYS\u5bf9\u975e\u5367\u5e8a\u60a3\u8005\u7684\u9500\u552e\uff0c\u76f4\u81f3\u65b0\u7684\u514d\u75ab\u6291\u5236\u65b9\u6848\u83b7\u5f97\u6279\u51c6\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e86\u89e3\u66f4\u591a<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/zh\/aan-report-reviews-the-state-of-evidence-on-elevidys-gene-therapy-cure-for-duchenne-muscular-dystrophy\/\">\u7b2c\u4e8c\u540d\u60a3\u8005\u6b7b\u4ea1\u540e\uff0c\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7fa4\u4f53\u5e0c\u671b\u4e86\u89e3Elevidys\u57fa\u56e0\u7597\u6cd5\u7684\u7597\u6548<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Due to two documented incidents of severe liver failure that resulted in death, Sarepta Therapeutics has stopped shipping its gene treatment ELEVIDYS for individuals with non-ambulatory Duchenne muscular dystrophy. The patient who died most recently was 15 years old. In order to allow for protocol changes and regulatory considerations, Sarepta has decided to halt the [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4109,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[33,65],"class_list":["post-4108","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-elevidys","tag-sarepta"],"subtitle":"\u636e\u62a5\u9053\uff0c\u4e24\u540d\u60a3\u8005\u5728\u670d\u7528 ELEVIDYS \u6cbb\u7597\u540e\u51fa\u73b0\u6025\u6027\u809d\u529f\u80fd\u8870\u7aed\u5e76\u6b7b\u4ea1\uff0c\u6b64\u540e Sarepta \u5df2\u6682\u505c\u5411\u65e0\u6cd5\u884c\u8d70\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u60a3\u8005\u8fd0\u9001\u8be5\u836f\u7269\u3002","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4108","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=4108"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/4108\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/4109"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=4108"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=4108"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=4108"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}