{"id":3846,"date":"2025-05-13T17:38:41","date_gmt":"2025-05-13T14:38:41","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3846"},"modified":"2025-05-13T17:47:11","modified_gmt":"2025-05-13T14:47:11","slug":"elevidys-gene-therapy-approved-in-japan","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/elevidys-gene-therapy-approved-in-japan\/","title":{"rendered":"Sarepta Therapeutics\u5ba3\u5e03\u65e5\u672c\u6279\u51c6\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u57fa\u56e0\u7597\u6cd5ELEVIDYS"},"content":{"rendered":"<p class=\"wp-block-paragraph\">3\u5c81\u81f38\u5c81\u4ee5\u4e0b\uff0cDMD\u57fa\u56e0\u5916\u663e\u5b508\u548c\/\u62169\u672a\u7f3a\u5931\uff0c\u4e14\u6297AAVrh74\u6297\u4f53\u68c0\u6d4b\u5448\u9634\u6027\u7684\u4eba\u7fa4\uff0c\u53ef\u4f7f\u7528ELEVIDYS\u3002\u8fd9\u662f\u5168\u7403\u9996\u4e2a\u8986\u76d64\u5c81\u4ee5\u4e0b\u4eba\u7fa4\u7684\u83b7\u6279\u836f\u7269\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e86\u89e3\u66f4\u591a\uff1a<\/strong> <a href=\"https:\/\/dmdwarrior.com\/zh\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u5173\u4e8e Elevidys \u7528\u4e8e\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u5e38\u89c1\u95ee\u9898<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">ELEVIDYS\u57fa\u56e0\u7597\u6cd5\u5728\u65e5\u672c\u83b7\u6279<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Sarepta Therapeutics \u662f\u7f55\u89c1\u75be\u75c5\u7cbe\u51c6\u57fa\u56e0\u533b\u5b66\u9886\u57df\u7684\u9886\u5bfc\u8005\uff0c\u4eca\u5929\u5ba3\u5e03\u65e5\u672c\u539a\u751f\u52b3\u52a8\u7701 (MHLW) \u5df2\u6279\u51c6 ELEVIDYS (delandistrogene moxeparvovec) \u6839\u636e\u65e5\u672c\u6709\u6761\u4ef6\u548c\u6709\u65f6\u95f4\u9650\u5236\u7684\u6279\u51c6\u9014\u5f84\u7528\u4e8e\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD)\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a\uff1a<\/strong> <a href=\"https:\/\/dmdwarrior.com\/zh\/will-elevidys-receive-approval-from-the-european-medicines-agency-ema\/\">Elevidys \u4f1a\u83b7\u5f97\u6b27\u6d32\u836f\u54c1\u7ba1\u7406\u5c40 (EMA) \u7684\u6279\u51c6\u5417\uff1f<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>People aged 3 to under 8 who do not have deletions in exons 8 and\/or 9 of the DMD gene and who test negative for anti-AAVrh74 antibodies are eligible to use ELEVIDYS. This is the first worldwide approval that covers people under the age of four. Learn More: Frequently Asked Questions About Elevidys Used for [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3847,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[33,61,142],"class_list":["post-3846","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-elevidys","tag-gene-therapy","tag-japan"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/3846","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=3846"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/3846\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/3847"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=3846"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=3846"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=3846"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}