{"id":3307,"date":"2025-03-19T19:20:55","date_gmt":"2025-03-19T16:20:55","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3307"},"modified":"2025-03-19T19:20:57","modified_gmt":"2025-03-19T16:20:57","slug":"regenxbio-reports-positive-biomarker-data-from-affinity-duchenne-trial-of-rgx-202-gene-therapy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/regenxbio-reports-positive-biomarker-data-from-affinity-duchenne-trial-of-rgx-202-gene-therapy\/","title":{"rendered":"Regenxbio \u62a5\u544a Rgx-202 \u57fa\u56e0\u6cbb\u7597 Affinity Duchenne \u8bd5\u9a8c\u7684\u9633\u6027\u751f\u7269\u6807\u5fd7\u7269\u6570\u636e"},"content":{"rendered":"<p class=\"wp-block-paragraph\">REGENXBIO \u62a5\u544a\u4e86 RGX-202 AFFINITY DUCHENNE\u00ae \u8bd5\u9a8c I\/II \u671f\u90e8\u5206\u4e2d\u6765\u81ea\u53e6\u5916\u4e24\u540d\u60a3\u8005\u7684\u65b0\u7684\u9633\u6027\u4e2d\u671f\u6570\u636e\uff0cRGX-202 \u662f\u4e00\u79cd\u9488\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (Duchenne) \u7684\u5dee\u5f02\u5316\u8bd5\u9a8c\u57fa\u56e0\u7597\u6cd5\u3002\u7ed3\u679c\u5728 2025 \u5e74\u808c\u8089\u8425\u517b\u4e0d\u826f\u75c7\u534f\u4f1a (MDA) \u4e34\u5e8a\u548c\u79d1\u5b66\u4f1a\u8bae\u4e0a\u8fdb\u884c\u4e86\u5c55\u793a\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Rgx-202 \u7684\u4e3b\u8981\u53d1\u73b0\u5305\u62ec\uff1a<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>MDA \u5c55\u793a\u4e86\u4e24\u540d\u63a5\u53d7\u5173\u952e\u5242\u91cf RGX-202 \u7684\u60a3\u8005\u7684\u65b0\u751f\u7269\u6807\u5fd7\u7269\u6570\u636e\uff0c\u5e76\u7ee7\u7eed\u652f\u6301 RGX-202 \u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u5728\u6240\u6709\u5e74\u9f84\u6bb5\u7684\u8868\u8fbe\u548c\u8f6c\u5bfc\u4e00\u81f4\u3001\u5f3a\u52b2\u3002<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u5728\u4e00\u540d 3 \u5c81\u60a3\u8005\u670d\u836f\u65f6\uff0c\u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u8868\u8fbe\u91cf\u4e0e\u5bf9\u7167\u7ec4\u76f8\u6bd4\u4e3a 122.3%\u30024 \u5c81\u4ee5\u4e0b\u60a3\u8005\u65e0\u6cd5\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\uff0cREGENXBIO \u662f\u7f8e\u56fd\u552f\u4e00\u4e00\u5bb6\u62db\u52df\u8be5\u5e74\u9f84\u6bb5\u60a3\u8005\u7684\u57fa\u56e0\u6cbb\u7597\u8d5e\u52a9\u5546<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u5728\u4e00\u540d 7 \u5c81\u60a3\u8005\u4e2d\uff0c\u4e0e\u5bf9\u7167\u7ec4\u76f8\u6bd4\uff0cRGX-202 \u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u8868\u8fbe\u6d4b\u91cf\u7ed3\u679c\u4e3a 31.5%\u3002<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u5728\u6240\u6709\u60a3\u8005\u4e2d\uff0cRGX-202 \u90fd\u9002\u5f53\u5730\u5b9a\u4f4d\u4e8e\u808c\u819c\uff0c\u8868\u660e\u5177\u6709 CT \u57df\u7684\u5206\u5316\u6784\u5efa\u4f53\u9002\u5f53\u5730\u9776\u5411\u808c\u8089\u3002<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>RGX-202 \u5728 8 \u5c81\u4ee5\u4e0a\u95e8\u8bca\u60a3\u8005\u4e2d\u7684\u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u8868\u8fbe\u7ed3\u679c\u662f\u5df2\u83b7\u6279\u51c6\u6216\u6b63\u5728\u7814\u7a76\u4e2d\u7684\u57fa\u56e0\u7597\u6cd5\u4e2d\u62a5\u544a\u7684\u6700\u9ad8\u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u6c34\u5e73\u3002<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u4e3a\u4e86\u652f\u6301\u4f7f\u7528\u52a0\u901f\u5ba1\u6279\u9014\u5f84\u7684\u751f\u7269\u5236\u54c1\u8bb8\u53ef\u7533\u8bf7 (BLA)\uff0cAFFINITY DUCHENNE \u5173\u952e\u9636\u6bb5\u7684\u4e3b\u8981\u7ec8\u70b9\u662f\u7b2c 12 \u5468 RGX-202 \u5fae\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u8868\u8fbe\u226510% \u7684\u53c2\u4e0e\u8005\u6bd4\u4f8b\u3002<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>RGX-202 \u8fd8\u7ee7\u7eed\u663e\u793a\u51fa\u5728\u5df2\u6279\u51c6\u6216\u7814\u7a76\u7684\u57fa\u56e0\u7597\u6cd5\u4e2d\u901a\u8fc7 qPCR \u6d4b\u91cf\u7684\u6700\u9ad8\u62a5\u544a\u8f7d\u4f53\u57fa\u56e0\u7ec4\u62f7\u8d1d\u6570\uff084.9-55.4\uff09\u3002<\/li>\n<\/ul>","protected":false},"excerpt":{"rendered":"<p>REGENXBIO \u516c\u5e03\u4e86 RGX-202 AFFINITY DUCHENNE\u00ae \u4e34\u5e8a\u8bd5\u9a8c I\/II \u671f\u9636\u6bb5\u65b0\u589e\u4e24\u4f8b\u60a3\u8005\u7684\u79ef\u6781\u4e2d\u671f\u6570\u636e\u3002RGX-202 \u662f\u4e00\u79cd\u9488\u5bf9\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08Duchenne \u578b\uff09\u7684\u5dee\u5f02\u5316\u7814\u7a76\u57fa\u56e0\u7597\u6cd5\u3002\u7814\u7a76\u7ed3\u679c\u5df2\u5728 2025 \u5e74\u808c\u8089\u840e\u7f29\u75c7\u534f\u4f1a (MDA) \u4e34\u5e8a\u4e0e\u79d1\u5b66\u4f1a\u8bae\u4e0a\u516c\u5e03\u3002RGX-202 \u7684\u4e3b\u8981\u53d1\u73b0\u5305\u62ec\uff1a<\/p>","protected":false},"author":1,"featured_media":3308,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[61,297,107,108],"class_list":["post-3307","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-gene-therapy","tag-muscular-dystrophy-association","tag-regenxbio","tag-rgx-202"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/3307","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=3307"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/3307\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/3308"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=3307"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=3307"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=3307"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}