{"id":3027,"date":"2026-08-06T17:27:14","date_gmt":"2026-08-06T14:27:14","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3027"},"modified":"2026-08-06T17:27:17","modified_gmt":"2026-08-06T14:27:17","slug":"ips-heart-full-length-dystrophin-duchenne","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/ips-heart-full-length-dystrophin-duchenne\/","title":{"rendered":"IPS HEART \u65e8\u5728\u901a\u8fc7\u4e24\u79cd\u518d\u751f\u7ec6\u80de\u7597\u6cd5\u6062\u590d\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d"},"content":{"rendered":"<p class=\"wp-block-paragraph\">IPS HEART \u5ba3\u5e03\u5176\u7528\u4e8e\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u7684\u5728\u7814\u5fc3\u808c\u7597\u6cd5 ISX9-CPC \u83b7\u5f97 FDA \u7f55\u89c1\u513f\u79d1\u75be\u75c5\u8ba4\u5b9a\uff0c\u8fd9\u662f\u53c8\u4e00\u4e2a\u91cd\u8981\u7684\u76d1\u7ba1\u91cc\u7a0b\u7891\u3002. <strong>\u8be5\u516c\u53f8\u6b63\u4e0e GIVI-MPCs\uff08\u4e00\u79cd\u65e8\u5728\u751f\u6210\u65b0\u808c\u8089\u5e76\u6062\u590d\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u7684\u5b9e\u9a8c\u6027\u9aa8\u9abc\u808c\u7597\u6cd5\uff09\u4e00\u8d77\uff0c\u63a2\u7d22\u4e00\u79cd\u65e8\u5728\u89e3\u51b3\u5fc3\u810f\u548c\u9aa8\u9abc\u808c\u635f\u4f24\u7684\u518d\u751f\u65b9\u6cd5\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4e0e\u76ee\u524d\u8bb8\u591a\u4e3b\u8981\u4fa7\u91cd\u4e8e\u51cf\u7f13\u75be\u75c5\u8fdb\u5c55\u7684\u6cbb\u7597\u65b9\u6cd5\u4e0d\u540c\uff0cIPS HEART \u8868\u793a\uff0c\u5176\u518d\u751f\u533b\u5b66\u5e73\u53f0\u65e8\u5728\u521b\u9020\u80fd\u591f\u4ea7\u751f\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u7684\u5168\u65b0\u4eba\u7c7b\u808c\u8089\u7ec6\u80de\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u4e0e\u73b0\u6709DMD\u7597\u6cd5\u4e0d\u540c\u7684\u7b56\u7565<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u76ee\u524d\u8bb8\u591a\u53ef\u7528\u7684\u6216\u5b9e\u9a8c\u6027\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u6cbb\u7597\u65b9\u6cd5\uff08\u5305\u62ec\u5916\u663e\u5b50\u8df3\u8dc3\u7597\u6cd5\u548c\u5fae\u578b\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u57fa\u56e0\u7597\u6cd5\uff09\u4ec5\u5bf9\u7279\u5b9a\u60a3\u8005\u7fa4\u4f53\u6709\u5e2e\u52a9\uff0c\u5e76\u4e14\u901a\u5e38\u4e0d\u80fd\u6062\u590d\u5b8c\u6574\u7684\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">IPS HEART \u5728\u65b0\u95fb\u7a3f\u4e2d\u6307\u51fa\uff0c\u8fd9\u4e9b\u65b9\u6cd5\u5b58\u5728\u4e34\u5e8a\u5c40\u9650\u6027\uff0c\u65e0\u6cd5\u6062\u590d\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\uff0c\u800c\u5176\u8bf1\u5bfc\u591a\u80fd\u5e72\u7ec6\u80de (iPSC) \u5e73\u53f0\u65e8\u5728\u4e34\u5e8a\u524d\u7814\u7a76\u4e2d\u751f\u6210\u8868\u8fbe\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u7684\u65b0\u578b\u529f\u80fd\u6027\u808c\u8089\u7ec6\u80de\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u516c\u53f8\u6b63\u5728\u5f00\u53d1\u4e24\u79cd\u4e0d\u540c\u7684\u518d\u751f\u7597\u6cd5\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>ISX9-CPC \u7528\u4e8e\u5fc3\u808c<\/strong><\/li>\n\n\n\n<li><strong>GIVI-MPCs \u7528\u4e8e\u9aa8\u9abc\u808c<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u4e9b\u7597\u6cd5\u5171\u540c\u7684\u76ee\u6807\u662f\u518d\u751f\u53d7\u635f\u808c\u8089\uff0c\u800c\u4e0d\u4ec5\u4ec5\u662f\u51cf\u7f13\u5176\u8870\u9000\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">ISX9-CPC\uff1a\u518d\u751f\u5fc3\u808c<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u5fc3\u810f\u75c5\u662f\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u4e3b\u8981\u6b7b\u56e0\u4e4b\u4e00\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u636eIPS HEART\u62a5\u9053\uff0cISX9-CPC\u65e8\u5728\u7528\u65b0\u751f\u6210\u7684\u6536\u7f29\u6027\u5fc3\u808c\u7ec4\u7ec7\u66ff\u4ee3\u5fc3\u810f\u4e2d\u7684\u7ea4\u7ef4\u5316\u7622\u75d5\u7ec4\u7ec7\u3002\u4e34\u5e8a\u524d\u7814\u7a76\u8868\u660e\uff0c\u6cbb\u7597\u540e\u5fc3\u810f\u529f\u80fd\u5f97\u5230\u6539\u5584\uff0c\u5c04\u8840\u5206\u6570\u589e\u52a0\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8be5\u516c\u53f8\u8fd8\u5728\u5176\u5b98\u65b9\u7f51\u7ad9\u4e0a\u91cd\u70b9\u4ecb\u7ecd\u4e86\u5176\u4ed6\u4e34\u5e8a\u524d\u7814\u7a76\u7ed3\u679c\uff0c\u58f0\u660e\u5982\u4e0b\uff1a<\/p>\n\n\n\n<blockquote class=\"wp-block-quote is-layout-flow wp-block-quote-is-layout-flow\">\n<p class=\"wp-block-paragraph\">\u201c\u5728\u4e00\u9879\u7ecf\u8fc7\u540c\u884c\u8bc4\u5ba1\u7684\u4f53\u5185\u6982\u5ff5\u9a8c\u8bc1\u7814\u7a76\u4e2d\uff0c\u6211\u4eec\u83b7\u5f97\u4e13\u5229\u7684 ISX9-CPC \u5355\u6b21\u6cbb\u7597\u53ef\u51cf\u5c11 70% \u4e2a\u574f\u6b7b\u7622\u75d5\u7ec4\u7ec7\uff0c\u5e76\u5728\u5fc3\u810f\u75c5\u53d1\u4f5c\u540e 90 \u5929\u4f7f\u5fc3\u810f\u529f\u80fd\u6062\u590d 60% \u4e2a\u4ee5\u4e0a\uff08\u4e0e\u5bf9\u7167\u7ec4\u76f8\u6bd4\uff09\u3002\u201d<\/p>\n<\/blockquote>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u4e9b\u53d1\u73b0\u4e0e\u5fc3\u810f\u75c5\u53d1\u4f5c\u6a21\u578b\u6709\u5173\uff0c\u800c\u4e0d\u662f\u4e0e\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u6709\u5173\uff0c\u4f46 IPS HEART \u5c06\u5176\u4f5c\u4e3a\u8bc1\u636e\uff0c\u652f\u6301\u5176\u5fc3\u810f\u7ec6\u80de\u7597\u6cd5\u7684\u518d\u751f\u6f5c\u529b\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">GIVI-MPCs\uff1a\u5229\u7528\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u6784\u5efa\u65b0\u7684\u9aa8\u9abc\u808c<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u8be5\u516c\u53f8\u7684\u7b2c\u4e8c\u4e2a\u9879\u76ee GIVI-MPCs \u4e13\u6ce8\u4e8e\u518d\u751f\u53d7\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u5f71\u54cd\u7684\u9aa8\u9abc\u808c\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u6839\u636e\u65b0\u95fb\u7a3f\uff0cGIVI-MPCs \u65e8\u5728\u751f\u6210\u65b0\u7684\u4eba\u7c7b\u9aa8\u9abc\u808c\u7ec4\u7ec7\uff0c\u540c\u65f6\u5728\u591a\u79cd\u8425\u517b\u4e0d\u826f\u52a8\u7269\u6a21\u578b\u4e2d\u6062\u590d\u5168\u957f\u7684\u4eba\u7c7b\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">IPS HEART\u5728\u5176\u5b98\u65b9\u7f51\u7ad9\u4e0a\u8fdb\u4e00\u6b65\u9610\u8ff0\u4e86\u8fd9\u4e00\u8bf4\u6cd5\uff0c\u58f0\u660e\u5982\u4e0b\uff1a<\/p>\n\n\n\n<blockquote class=\"wp-block-quote is-layout-flow wp-block-quote-is-layout-flow\">\n<p class=\"wp-block-paragraph\">\u201c\u5229\u7528 GIVI-MPC\uff0c\u6211\u4eec\u5728 mdx \u5c0f\u9f20\u548c\u8425\u517b\u4e0d\u826f\u732a\u4f53\u5185\u6210\u529f\u6784\u5efa\u4e86\u91cd\u8981\u7684\u5168\u65b0\u4eba\u7c7b\u9aa8\u9abc\u808c\uff0c\u4ee5\u53ca 100% \u5168\u957f\u4eba\u7c7b\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u3002\u201d<\/p>\n<\/blockquote>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u8fd9\u662f\u8be5\u516c\u53f8\u76ee\u524d\u5f3a\u8c03\u7684\u6700\u6709\u529b\u4e3b\u5f20\u4e4b\u4e00\uff0c\u56e0\u4e3a\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u4e0e\u5065\u5eb7\u808c\u8089\u4e2d\u5929\u7136\u5b58\u5728\u7684\u86cb\u767d\u8d28\u975e\u5e38\u76f8\u4f3c\uff0c\u8fd9\u4e0e\u76ee\u524d\u57fa\u56e0\u6cbb\u7597\u65b9\u6cd5\u4ea7\u751f\u7684\u7f29\u77ed\u7684\u5fae\u578b\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u4e0d\u540c\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4f46\u9700\u8981\u6ce8\u610f\u7684\u662f\uff0c\u8fd9\u4e9b\u7ed3\u679c\u5c1a\u5c5e\u4e34\u5e8a\u524d\u7814\u7a76\uff0c\u5c1a\u672a\u5728\u4eba\u4f53\u4e34\u5e8a\u8bd5\u9a8c\u4e2d\u5f97\u5230\u8bc1\u5b9e\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u8ba1\u5212\u4e8e2027\u5e74\u5f00\u5c55\u4eba\u4f53\u4e34\u5e8a\u8bd5\u9a8c<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>IPS HEART \u8868\u793a\uff0c\u8ba1\u5212\u5411\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40\u63d0\u4ea4\u7814\u7a76\u6027\u65b0\u836f (IND) \u7533\u8bf7\uff0c\u5e76\u5728\u83b7\u5f97\u76d1\u7ba1\u90e8\u95e8\u6279\u51c6\u540e\uff0c\u4e8e 2027 \u5e74\u5f00\u59cb GIVI-MPCs \u7684\u9996\u6b21\u4eba\u4f53\u4e34\u5e8a\u8bd5\u9a8c\u3002.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u5982\u679c\u83b7\u5f97\u6279\u51c6\uff0c\u8fd9\u5c06\u662f\u8bc4\u4f30\u8be5\u516c\u53f8\u518d\u751f\u7b56\u7565\u80fd\u5426\u5b89\u5168\u5730\u6062\u590d\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u9aa8\u9abc\u808c\u548c\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u7684\u9996\u6b21\u673a\u4f1a\u3002.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u4e3a\u4ec0\u4e48\u8fd9\u5f88\u91cd\u8981<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7814\u7a76\u4e2d\u6700\u5927\u7684\u79d1\u5b66\u6311\u6218\u4e4b\u4e00\u662f\u627e\u5230\u4e00\u79cd\u65b9\u6cd5\u6765\u66ff\u4ee3\u5931\u53bb\u7684\u808c\u8089\uff0c\u540c\u65f6\u6062\u590d\u5b8c\u6574\u7684\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">IPS HEART \u8ba4\u4e3a\u5176\u518d\u751f\u7ec6\u80de\u7597\u6cd5\u5e73\u53f0\u6700\u7ec8\u53ef\u80fd\u540c\u65f6\u5b9e\u73b0\u8fd9\u4e24\u4e2a\u76ee\u6807\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u4fee\u590d\u53d7\u635f\u5fc3\u808c<\/strong><\/li>\n\n\n\n<li><strong>\u751f\u6210\u65b0\u7684\u9aa8\u9abc\u808c<\/strong><\/li>\n\n\n\n<li><strong>\u6062\u590d\u5168\u957f\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d<\/strong><\/li>\n\n\n\n<li><strong>\u4e0e\u9488\u5bf9\u7279\u5b9a\u7a81\u53d8\u7684\u7597\u6cd5\u76f8\u6bd4\uff0c\u53ef\u80fd\u5177\u6709\u66f4\u5e7f\u6cdb\u7684\u9002\u7528\u6027\u3002<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u4e9b\u4ee4\u4eba\u9f13\u821e\u7684\u4e34\u5e8a\u524d\u7814\u7a76\u7ed3\u679c\u80fd\u5426\u8f6c\u5316\u4e3a\u6709\u610f\u4e49\u7684\u4e34\u5e8a\u76ca\u5904\uff0c\u8fd8\u6709\u5f85\u901a\u8fc7\u7cbe\u5fc3\u8bbe\u8ba1\u7684\u4eba\u4f53\u8bd5\u9a8c\u6765\u786e\u5b9a\u3002.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u7acb\u5373\u63a2\u7d22<\/strong>:&nbsp;<a href=\"https:\/\/dmdwarrior.com\/clinical-trials\/\" target=\"_blank\" rel=\"noreferrer noopener\">DMDWarrioR \u4e34\u5e8a\u8bd5\u9a8c\u4e2d\u5fc3<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>IPS HEART has announced another important regulatory milestone after receiving FDA Rare Pediatric Disease Designation for ISX9-CPC, its investigational cardiac muscle therapy for Duchenne muscular dystrophy (DMD). Together with GIVI-MPCs, an experimental skeletal muscle therapy designed to generate new muscle and restore full-length dystrophin, the company is pursuing a regenerative approach that aims to address [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":8332,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[817,359,857,856,858,259],"class_list":["post-3027","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-dmd-treatment","tag-full-length-dystrophin","tag-givi-mpcs","tag-isx9-cpc","tag-muscle-regeneration","tag-stem-cell-therapy"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/3027","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=3027"}],"version-history":[{"count":10,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/3027\/revisions"}],"predecessor-version":[{"id":8333,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/3027\/revisions\/8333"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/8332"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=3027"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=3027"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=3027"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}