{"id":2570,"date":"2025-01-24T11:20:01","date_gmt":"2025-01-24T08:20:01","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2570"},"modified":"2025-03-07T13:21:44","modified_gmt":"2025-03-07T10:21:44","slug":"will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies\/","title":{"rendered":"Genethon \u548c Eukar \u7684\u5408\u4f5c\u4f1a\u964d\u4f4e\u57fa\u56e0\u6cbb\u7597\u7684\u6210\u672c\u5417\uff1f"},"content":{"rendered":"<p class=\"wp-block-paragraph\">FDA \u662f\u552f\u4e00\u83b7\u6279\u7684\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u57fa\u56e0\u7597\u6cd5\uff0c\u5176\u4ef7\u683c\u5bf9\u4e8e\u666e\u901a\u5bb6\u5ead\u6765\u8bf4\u592a\u9ad8\u4e86\u3002\u666e\u901a\u5bb6\u5ead\u6839\u672c\u8d1f\u62c5\u4e0d\u8d77\u8fd9\u79cd\u9ad8\u6602\u7684\u4ef7\u683c\u3002\u5236\u9020\u5546\u5e94\u8be5\u91cd\u65b0\u8003\u8651\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u57fa\u56e0\u7597\u6cd5\u7684\u4ef7\u683c\u3002\u6839\u636e Genethon 1 \u6708 23 \u65e5\u7684\u516c\u544a\uff0c\u4e0e Eukar\u00ffs \u7684\u5408\u4f5c\u53ef\u80fd\u4f1a\u5c06\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u57fa\u56e0\u7597\u6cd5\u7684\u4ef7\u683c\u964d\u81f3\u5408\u7406\u6c34\u5e73\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u4eca\u5929\uff0cEukar\u00ffs \u548c Genethon \u5ba3\u5e03\u8fbe\u6210\u6218\u7565\u534f\u8bae\u3002Eukar\u00ffs \u662f\u4e00\u5bb6\u751f\u7269\u6280\u672f\u516c\u53f8\uff0c\u8be5\u516c\u53f8\u5f00\u53d1\u4e86\u4e00\u9879\u6539\u53d8\u6e38\u620f\u89c4\u5219\u7684\u6280\u672f\uff0c\u53ef\u5927\u5e45\u63d0\u9ad8\u751f\u7269\u5236\u9020\u4ea7\u91cf\u3002Genethon \u662f\u7f55\u89c1\u75be\u75c5\u57fa\u56e0\u6cbb\u7597\u7814\u7a76\u548c\u5f00\u53d1\u7684\u5148\u9a71\u548c\u9886\u5bfc\u8005\u3002\u6b64\u6b21\u5408\u4f5c\u5229\u7528 Eukar\u00ffs \u72ec\u7279\u7684 C3P3 \u6280\u672f\uff08\u4e00\u79cd\u5728\u54fa\u4e73\u52a8\u7269\u7ec6\u80de\u4e2d\u8868\u8fbe\u65b0\u578b\u4fe1\u4f7f RNA (mRNA) \u7684\u65b9\u6cd5\uff09\u6765\u964d\u4f4e\u751f\u4ea7\u57fa\u56e0\u6cbb\u7597\u836f\u7269\u7684\u6210\u672c\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e86\u89e3\u66f4\u591a\uff1a<\/strong>\u00a0<a href=\"https:\/\/dmdwarrior.com\/zh\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u6f5c\u5728\u65b0\u57fa\u56e0\u7597\u6cd5<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a\uff1a<\/strong> <a href=\"https:\/\/dmdwarrior.com\/zh\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\">\u5173\u4e8e Elevidys \u7684\u5e38\u89c1\u95ee\u9898\u89e3\u7b54<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The FDA-approved only gene therapy for Duchenne muscular dystrophy is costing far too much for families to afford. Families simply cannot afford this prohibitive price. Manufacturers should reconsider the price of DMD gene therapies. According to an announcement by Genethon on January 23, the collaboration with Eukar\u00ffs could bring the price of DMD gene therapies [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2572,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[201,66,200,72,61,105,202],"class_list":["post-2570","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-c3p3-technology","tag-duchenne-muscular-dystrophy","tag-eukarys","tag-gene-editing","tag-gene-therapy","tag-genethon","tag-mrna"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/2570","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=2570"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/2570\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/2572"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=2570"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=2570"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=2570"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}