{"id":2547,"date":"2025-01-23T14:50:06","date_gmt":"2025-01-23T11:50:06","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2547"},"modified":"2025-11-03T20:31:05","modified_gmt":"2025-11-03T17:31:05","slug":"fda-grants-rare-pediatric-disease-designation-to-nippon-shinyakus-exon-51-skipping-study-ns-051-ncnp-04","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/fda-grants-rare-pediatric-disease-designation-to-nippon-shinyakus-exon-51-skipping-study-ns-051-ncnp-04\/","title":{"rendered":"FDA \u6388\u4e88\u65e5\u672c\u65b0\u836f\u5916\u663e\u5b50 51 \u8df3\u8dc3\u7814\u7a76 (NS-051\/NCNP-04) \u7f55\u89c1\u513f\u79d1\u75be\u75c5\u8ba4\u5b9a"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u65e5\u672c\u65b0\u836f\u682a\u5f0f\u4f1a\u793e\u548c\u56fd\u7acb\u795e\u7ecf\u7cbe\u795e\u75c5\u5b66\u7814\u7a76\u4e2d\u5fc3\u5171\u540c\u53d1\u73b0\u4e86\u53cd\u4e49\u5be1\u6838\u82f7\u9178 NS-051\/NCNP-04\u3002NS-051\/NCNP-04 \u901a\u8fc7\u5220\u9664\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u57fa\u56e0\u7684\u4e00\u90e8\u5206\u9057\u4f20\u7269\u8d28\uff0c\u751f\u6210\u94fe\u957f\u7565\u77ed\u7684\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\uff0c\u4ece\u800c\u9632\u6b62\u808c\u8089\u529f\u80fd\u4e0b\u964d\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u65e5\u672c\u65b0\u836f\u682a\u5f0f\u4f1a\u793e\u6000\u7740\u5f3a\u70c8\u7684\u4f7f\u547d\u611f\uff0c\u79ef\u6781\u5f00\u53d1\u6cbb\u7597\u7f55\u89c1\u53ca\u96be\u6cbb\u6027\u75be\u75c5\u7684\u836f\u7269\uff0c\u4ee5\u4fbf\u4e3aDMD\u60a3\u8005\u8fc5\u901f\u627e\u5230\u89e3\u51b3\u65b9\u6848\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u9605\u8bfb\u66f4\u591a<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/zh\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u4e34\u5e8a\u8bd5\u9a8c\uff08\u6240\u6709\u7814\u7a76\u5217\u8868\uff09<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Nippon Shinyaku and the National Center of Neurology and Psychiatry jointly discovered the antisense oligonucleotide NS-051\/NCNP-04. By omitting a portion of the dystrophin gene&#8217;s genetic material, NS-051\/NCNP-04 creates a functioning dystrophin protein with a little shorter chain length, which should prevent the decline in muscle function. With a strong sense of purpose, Nippon Shinyaku has [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2550,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[193,194,88,136,192],"class_list":["post-2547","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-exon-51-skipping","tag-exon-51-treatment","tag-fda","tag-nippon-shinyaku","tag-ns-051-ncnp-04"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/2547","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=2547"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/2547\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/2550"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=2547"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=2547"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=2547"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}