{"id":2226,"date":"2025-01-02T23:09:53","date_gmt":"2025-01-02T20:09:53","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2226"},"modified":"2025-11-03T19:23:00","modified_gmt":"2025-11-03T16:23:00","slug":"what-is-deramiocel","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/what-is-deramiocel\/","title":{"rendered":"\u4ec0\u4e48\u662f Deramiocel\uff1fCAP-1002 \u6709\u4ec0\u4e48\u4f5c\u7528\uff1f"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Capricor Therapeutics \u662f\u4e00\u5bb6\u751f\u7269\u6280\u672f\u516c\u53f8\uff0c\u81f4\u529b\u4e8e\u5f00\u53d1\u7528\u4e8e\u6cbb\u7597\u7f55\u89c1\u75be\u75c5\u7684\u8f6c\u5316\u7ec6\u80de\u548c\u5916\u6ccc\u4f53\u7597\u6cd5\uff0c\u4eca\u5929\u5ba3\u5e03\u5df2\u5b8c\u6210\u5411\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40\uff08FDA\uff09\u63d0\u4ea4\u7684\u751f\u7269\u5236\u54c1\u8bb8\u53ef\u7533\u8bf7\uff08BLA\uff09\uff08FDA\uff09\uff0c\u5bfb\u6c42\u5168\u9762\u6279\u51c6 deramiocel\uff0c\u4e00\u79cd\u7814\u7a76\u6027\u7ec6\u80de\u7597\u6cd5\uff0c\u7528\u4e8e\u6cbb\u7597\u88ab\u8bca\u65ad\u4e3a\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08DMD\uff09\u5fc3\u808c\u75c5\u7684\u60a3\u8005\u3002 <strong>\u90a3\u4e48 Deramiocel \u662f\u4ec0\u4e48\u4ee5\u53ca\u5b83\u6709\u4ec0\u4e48\u4f5c\u7528\uff1f<\/strong><\/p>\n\n\n\n<h2 class=\"wp-block-heading\"><strong>Deramiocel \u662f\u4ec0\u4e48\uff1f<\/strong><\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Deramiocel (CAP-1002) \u7531 Capricor Therapeutics \u5f00\u53d1\uff0c\u662f\u4e00\u79cd\u6b63\u5728\u7814\u7a76\u4e2d\u7684\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7 (DMD) \u7684\u6709\u524d\u666f\u7684\u7597\u6cd5\uff0c\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u662f\u4e00\u79cd\u4ee5\u808c\u8089\u9000\u5316\u548c\u65e0\u529b\u4e3a\u7279\u5f81\u7684\u4e25\u91cd\u8fdb\u884c\u6027\u9057\u4f20\u6027\u75be\u75c5\u3002<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u4f5c\u7528\u673a\u5236<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">Deramiocel \u662f\u4e00\u79cd\u57fa\u4e8e\u7ec6\u80de\u7684\u7597\u6cd5\uff0c\u6e90\u81ea\u5fc3\u810f\u95f4\u5145\u8d28\u5e72\u7ec6\u80de (MSC)\u3002\u8fd9\u4e9b\u5e72\u7ec6\u80de\u80fd\u591f\u5206\u6ccc\u652f\u6301\u808c\u8089\u4fee\u590d\u548c\u518d\u751f\u7684\u56e0\u5b50\u3002Deramiocel \u7684\u76ee\u6807\u662f\u5229\u7528\u8fd9\u4e9b\u5e72\u7ec6\u80de\u7684\u518d\u751f\u7279\u6027\u6765\u51cf\u5c11\u708e\u75c7\u3001\u4fc3\u8fdb\u7ec4\u7ec7\u4fee\u590d\uff0c\u5e76\u53ef\u80fd\u518d\u751f\u60a3\u6709 DMD \u7684\u4e2a\u4f53\u53d7\u635f\u7684\u808c\u8089\u7ec4\u7ec7\u3002<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">Deramiocel \u5728 DMD \u4e2d\u6f5c\u5728\u7528\u9014\u7684\u5173\u952e\u70b9\uff1a<\/h3>\n\n\n\n<ol class=\"wp-block-list\">\n<li><strong>\u7ec6\u80de\u7597\u6cd5<\/strong>\uff1aDeramiocel \u4f7f\u7528\u4ece\u5fc3\u810f\u7ec4\u7ec7\u4e2d\u5206\u79bb\u51fa\u6765\u7684\u5e72\u7ec6\u80de\uff0c\u7136\u540e\u5bf9\u5176\u8fdb\u884c\u52a0\u5de5\u5e76\u6ce8\u5165\u60a3\u8005\u4f53\u5185\u3002\u95f4\u5145\u8d28\u5e72\u7ec6\u80de\u88ab\u8ba4\u4e3a\u53ef\u4ee5\u901a\u8fc7\u91ca\u653e\u86cb\u767d\u8d28\u548c\u7ec6\u80de\u56e0\u5b50\u6765\u4fc3\u8fdb\u6108\u5408\uff0c\u4ece\u800c\u51cf\u5c11\u708e\u75c7\u5e76\u523a\u6fc0\u808c\u8089\u518d\u751f\u3002<\/li>\n\n\n\n<li><strong>\u9488\u5bf9\u808c\u8089\u518d\u751f<\/strong>\uff1aDMD \u4f1a\u5bfc\u81f4\u9aa8\u9abc\u808c\u9010\u6e10\u53d7\u635f\u548c\u865a\u5f31\u3002Deramiocel \u53ef\u901a\u8fc7\u523a\u6fc0\u8eab\u4f53\u7684\u81ea\u7136\u6108\u5408\u8fc7\u7a0b\u548c\u521b\u9020\u4fc3\u8fdb\u808c\u8089\u7ec6\u80de\u5b58\u6d3b\u548c\u751f\u957f\u7684\u73af\u5883\u6765\u5e2e\u52a9\u808c\u8089\u7ec4\u7ec7\u518d\u751f\u3002<\/li>\n\n\n\n<li><strong>\u51cf\u7f13\u75be\u75c5\u8fdb\u5c55\u7684\u6f5c\u529b<\/strong>\uff1a\u901a\u8fc7\u89e3\u51b3\u708e\u75c7\u548c\u652f\u6301\u808c\u8089\u7ec4\u7ec7\u7684\u4fee\u590d\uff0cDeramiocel \u53ef\u4ee5\u5e2e\u52a9\u51cf\u7f13 DMD \u4e2d\u808c\u8089\u9000\u5316\u7684\u8fdb\u5c55\uff0c\u4ece\u800c\u6709\u53ef\u80fd\u6539\u5584\u60a3\u8005\u7684\u6d3b\u52a8\u80fd\u529b\u548c\u751f\u6d3b\u8d28\u91cf\u3002<\/li>\n\n\n\n<li><strong>\u9001\u8d27\u65b9\u5f0f<\/strong>\uff1a\u7ec6\u80de\u901a\u5e38\u901a\u8fc7\u6ce8\u5c04\u7684\u65b9\u5f0f\u7ed9\u836f\uff0c\u4f7f\u5b83\u4eec\u5230\u8fbe\u53d7\u635f\u7684\u808c\u8089\u7ec4\u7ec7\u5e76\u91ca\u653e\u4fee\u590d\u56e0\u5b50\u3002<\/li>\n<\/ol>\n\n\n\n<h3 class=\"wp-block-heading\">Capricor Therapeutics \u5b8c\u6210\u5411\u7f8e\u56fd\u63d0\u4ea4 Deramiocel \u751f\u7269\u5236\u54c1\u8bb8\u53ef\u7533\u8bf7 FDA\uff0c\u7528\u4e8e\u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u622a\u81f3\u6700\u65b0\u6d88\u606f\uff0cCapricor Therapeutics \u4e00\u76f4\u5728\u8fdb\u884c\u4e34\u5e8a\u8bd5\u9a8c\uff0c\u4ee5\u8bc4\u4f30 Deramiocel \u6cbb\u7597\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u5b89\u5168\u6027\u548c\u6709\u6548\u6027\u3002\u8fd9\u4e9b\u8bd5\u9a8c\u7684\u7ed3\u679c\u5c06\u51b3\u5b9a\u8fd9\u79cd\u6cbb\u7597\u65b9\u6cd5\u662f\u5426\u80fd\u6210\u4e3a\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u53ef\u884c\u6cbb\u7597\u9009\u62e9\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u5982\u679c\u8bc1\u660e\u6709\u6548\uff0cDeramiocel \u5c06\u6210\u4e3a DMD \u6cbb\u7597\u7684\u91cd\u5927\u8fdb\u6b65\uff0c\u4e3a\u53d7\u8fd9\u79cd\u68d8\u624b\u75be\u75c5\u5f71\u54cd\u7684\u60a3\u8005\u548c\u5bb6\u5ead\u5e26\u6765\u65b0\u7684\u5e0c\u671b\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u4e86\u89e3\u66f4\u591a\uff1a<\/strong> <a href=\"https:\/\/dmdwarrior.com\/zh\/capricor-therapeutics-publishes-peer-reviewed-study-about-cell-therapy-deramiocel\/\">Capricor Therapeutics \u53d1\u8868\u5173\u4e8e Deramiocel \u7ec6\u80de\u7597\u6cd5\u7684\u540c\u884c\u8bc4\u5ba1\u7814\u7a76<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Capricor Therapeutics, a biotechnology company developing transformative cell and exosome-based therapeutics for the treatment of rare diseases, today announced the completion of the submission of its Biologics License Application (BLA) to the U.S. Food and Drug Administration (FDA) seeking full approval for deramiocel, an investigational cell therapy, to treat patients diagnosed with Duchenne muscular dystrophy [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2228,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[90,86,87,89,85,88],"class_list":["post-2226","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-cap-1002","tag-capricor","tag-capricor-therapeutics","tag-cardiomyopathy","tag-deramiocel","tag-fda"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/2226","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=2226"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/2226\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/2228"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=2226"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=2226"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=2226"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}