{"id":1458,"date":"2024-10-04T10:49:58","date_gmt":"2024-10-04T10:49:58","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=1458"},"modified":"2024-10-04T10:49:59","modified_gmt":"2024-10-04T10:49:59","slug":"satellos-produced-near-normal-levels-of-dystrophin-in-experiment-with-dogs-with-dmd-with-sat-3247","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/zh\/satellos-produced-near-normal-levels-of-dystrophin-in-experiment-with-dogs-with-dmd-with-sat-3247\/","title":{"rendered":"Satellos \u4f7f\u7528 SAT-3247 \u5bf9\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u72d7\u8fdb\u884c\u5b9e\u9a8c\uff0c\u7ed3\u679c\u663e\u793a\u5176\u808c\u8425\u517b\u4e0d\u826f\u86cb\u767d\u6c34\u5e73\u63a5\u8fd1\u6b63\u5e38\u6c34\u5e73"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u636eSatellos Bioscience\u516c\u53f8\u5ba3\u5e03\uff0c\u5728\u5bf9\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u72d7\u8fdb\u884c\u7684\u5b9e\u9a8c\u4e2d\uff0c\u53d1\u73b0\u63a5\u53d7\u540d\u4e3aSAT-3247\u7684\u7597\u6cd5\u7684\u53d7\u8bd5\u8005\u4f53\u5185\u7684\u6297\u808c\u840e\u7f29\u86cb\u767d\u751f\u6210\u91cf\u63a5\u8fd1\u6b63\u5e38\u6c34\u5e73\u3002\u8fd9\u4e00\u8fdb\u5c55\u7ed9\u56e0\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u800c\u5ea6\u8fc7\u538b\u529b\u91cd\u91cd\u65e5\u5b50\u7684\u5bb6\u5ead\u5e26\u6765\u4e86\u5e0c\u671b\u3002<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u5206\u6790\u663e\u793a\u808c\u8089\u5f62\u6001\u5f97\u5230\u6539\u5584\uff0c\u808c\u8089\u7fa4\uff08\u5305\u62ec\u6a2a\u8188\u819c\u3001\u80a1\u56db\u5934\u808c\u548c\u5c0f\u817f\uff09\u7684\u518d\u751f\u6c34\u5e73\u5f97\u5230\u63d0\u9ad8<\/li>\n\n\n\n<li>\u7ecf\u8fc7\u56db\u4e2a\u6708\u7684\u6bcf\u65e5\u53e3\u670d SAT-3247\uff08Satellos \u7684\u4e13\u6709\u5c0f\u5206\u5b50\uff09\u6cbb\u7597\u540e\uff0c\u672a\u89c2\u5bdf\u5230\u4efb\u4f55\u4e0d\u826f\u4e8b\u4ef6\uff0c\u8840\u6db2\u5b66\u6216\u4e34\u5e8a\u5316\u5b66\u65b9\u9762\u4e5f\u672a\u51fa\u73b0\u663e\u8457\u53d8\u5316<\/li>\n\n\n\n<li>\u5c06\u5728 2024 \u5e74\u4e16\u754c\u808c\u8089\u534f\u4f1a\u5e74\u5ea6\u5927\u4f1a\u4e0a\u5c55\u793a\u7684\u6570\u636e<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">Satellos Bioscience Inc.\uff08\u201cSatellos\u201d\u6216\u201c\u516c\u53f8\u201d\uff09\uff08TSX\uff1aMSCL\uff0cOTCQB\uff1aMSCLF\uff09\u662f\u4e00\u5bb6\u4e0a\u5e02\u751f\u7269\u79d1\u6280\u516c\u53f8\uff0c\u81f4\u529b\u4e8e\u5f00\u53d1\u65b0\u7684\u5c0f\u5206\u5b50\u6cbb\u7597\u65b9\u6cd5\u4ee5\u6539\u5584\u808c\u8089\u75be\u75c5\u548c\u75c5\u75c7\u7684\u6cbb\u7597\uff0c\u8be5\u516c\u53f8\u4eca\u5929\u5ba3\u5e03\u5c06\u5728 2024 \u5e74 10 \u6708 8 \u65e5\u81f3 12 \u65e5\u5728\u5e03\u62c9\u683c\u4e3e\u884c\u7684\u7b2c 29 \u5c4a\u4e16\u754c\u808c\u8089\u534f\u4f1a\u5e74\u4f1a\u4e0a\u5c55\u793a\u6570\u636e\u3002\u8be5\u62a5\u544a\u5c06\u6982\u8ff0\u5728\u72ac\u7c7b\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\uff08\u201c\u675c\u6c0f\u201d\u6216\u201cDMD\u201d\uff09\u6a21\u578b\u4e2d\u5bf9 SAT-3247 \u8fdb\u884c\u5f00\u653e\u6807\u7b7e\u8bd5\u70b9\u7814\u7a76\u671f\u95f4\u6536\u96c6\u7684\u5173\u952e\u6570\u636e\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u6570\u636e\u7684\u521d\u6b65\u603b\u7ed3\u5982\u4e0b\u3002\u4f7f\u7528 SAT-3247 \u6cbb\u7597\u56db\u4e2a\u6708\u540e\uff1a<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u4e0e\u5386\u53f2\u6bd4\u8f83\u6570\u636e\u76f8\u6bd4\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u52a8\u7269\u7684\u808c\u8089\u529f\u80fd\u6062\u590d\u5230\u63a5\u8fd1\u5065\u5eb7\u3001\u672a\u60a3\u75c5\u3001\u5e74\u9f84\u5339\u914d\u7684\u52a8\u7269\u6c34\u5e73\u3002<\/li>\n\n\n\n<li>\u8fd9\u4e9b\u52a8\u7269\u7684\u8188\u808c\u3001\u8153\u80a0\u808c\u5185\u4fa7\u808c\uff08\u5c0f\u817f\uff09\u548c\u80a1\u5916\u4fa7\u808c\uff08\u80a1\u56db\u5934\u808c\uff09\u7684\u518d\u751f\u6307\u6570 (RI) \u6709\u6240\u589e\u52a0\u3002\u8fd9\u662f\u4e4b\u524d\u62a5\u9053\u8fc7\u7684\u80a1\u4e8c\u5934\u808c\u518d\u751f\u6307\u6570\u6539\u5584\u7684\u8865\u5145\u3002<\/li>\n\n\n\n<li>\u6ca1\u6709\u89c2\u5bdf\u5230\u4e0d\u826f\u4e8b\u4ef6\uff0c\u4e5f\u6ca1\u6709\u89c2\u5bdf\u5230\u8840\u6db2\u5b66\u6216\u4e34\u5e8a\u5316\u5b66\u65b9\u9762\u7684\u663e\u8457\u53d8\u5316\u3002<\/li>\n\n\n\n<li>\u7814\u7a76\u53d1\u73b0\u808c\u9178\u6fc0\u9176\u6c34\u5e73\u6709\u964d\u4f4e\u7684\u8d8b\u52bf\uff0c\u8fd9\u4e00\u53d1\u73b0\u53ef\u80fd\u4e0e\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u6539\u826f\u6cbb\u7597\u4e00\u81f4\u3002<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">Satellos Bioscience \u8054\u5408\u521b\u59cb\u4eba\u517c\u9996\u5e2d\u6267\u884c\u5b98 Frank Gleeson \u8868\u793a\uff1a\u201c\u6211\u4eec\u8ba4\u4e3a\uff0c\u4e0e\u5df2\u53d1\u8868\u7684\u81ea\u7136\u53f2\u6570\u636e\u548c\u72ac\u7c7b DMD \u6a21\u578b\u4e2d\u7684\u5176\u4ed6\u6cbb\u7597\u5e72\u9884\u63aa\u65bd\u76f8\u6bd4\uff0c\u5728\u6cbb\u7597\u56db\u4e2a\u6708\u5185\u89c2\u5bdf\u5230\u7684\u518d\u751f\u548c\u808c\u8089\u529b\u91cf\u6539\u5584\u63a5\u8fd1\u5065\u5eb7\u6c34\u5e73\uff0c\u5177\u6709\u5f00\u521b\u6027\u610f\u4e49\u3002\u201d\u201c\u72ac\u7c7b\u6a21\u578b\u88ab\u8ba4\u4e3a\u6bd4\u5c0f\u9f20\u6a21\u578b\u66f4\u4e3a\u4e25\u91cd\uff0c\u5e76\u4e14\u53ef\u80fd\u4ee3\u8868\u4e86\u5bf9\u6cbb\u7597\u8f6c\u5316\u4e3a\u4eba\u7c7b\u7684\u6548\u7528\u7684\u66f4\u5927\u8003\u9a8c\u3002\u6211\u4eec\u5f88\u9ad8\u5174\u6211\u4eec\u7684\u53e3\u670d\u5c0f\u5206\u5b50 SAT-3247 \u6cbb\u7597\u663e\u793a\u51fa\u5982\u6b64\u663e\u8457\u7684\u6539\u5584\u3002\u8fd9\u4e9b\u975e\u5e38\u6709\u5e0c\u671b\u7684\u7ed3\u679c\u52a0\u5f3a\u4e86\u6211\u4eec\u5bf9 SAT-3247 \u6f5c\u529b\u7684\u4fe1\u5ff5\uff0c\u5373\u63d0\u4f9b\u4e00\u79cd\u6709\u610f\u4e49\u7684\u75be\u75c5\u4fee\u9970\u836f\u7269\uff0c\u5e2e\u52a9\u60a3\u6709\u675c\u6c0f\u808c\u8425\u517b\u4e0d\u826f\u75c7\u7684\u60a3\u8005\u3002\u201d<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u72ac\u7c7b\u808c\u8425\u517b\u4e0d\u826f\u75c7\u6a21\u578b\u4ee3\u8868\u4e86\u66f4\u4e25\u91cd\u7684\u4e34\u5e8a\u8868\u578b\uff0c\u53cd\u6620\u4e86 DMD \u60a3\u8005\u4e2d\u89c2\u5bdf\u5230\u7684\u75be\u75c5\u8fdb\u5c55\u3002\u5728\u8fd9\u9879\u521d\u6b65\u7814\u7a76\u4e2d\uff0c\u6bcf\u53ea\u52a8\u7269 (n=2) \u63a5\u53d7\u56db\u4e2a\u6708\u7684\u6bcf\u65e5\u53e3\u670d SAT-3247 \u6cbb\u7597\u3002\u8fd9\u9879\u591a\u53c2\u6570\u521d\u6b65\u7814\u7a76\u6d4b\u91cf\u4e86\u4e34\u5e8a\u5316\u5b66\u3001\u8840\u6db2\u5b66\u3001\u808c\u8089\u529f\u80fd\uff0c\u5e76\u5305\u62ec\u5927\u89c4\u6a21\u808c\u8089\u7ec4\u7ec7\u5b66\u68c0\u67e5\u3002\u6839\u636e\u808c\u8089\u7ec4\u7ec7\u5b66\uff0c\u8ba1\u7b97\u4e86\u518d\u751f\u6307\u6570 (RI)\uff0c\u8fd9\u662f\u8861\u91cf\u65b0\u518d\u751f\u808c\u8089\u7ea4\u7ef4\u6570\u91cf\u4e0e\u53d7\u635f\u548c\u6b7b\u4ea1\u808c\u8089\u7ea4\u7ef4\u6570\u91cf\u7684\u6307\u6807\u3002<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u8fd9\u9879\u7814\u7a76\u7684\u6570\u636e\u5c06\u4ee5\u6d77\u62a5\u5f62\u5f0f\u5c55\u793a\uff0c\u6d77\u62a5\u9898\u4e3a\u201cSAT-3247\uff1a\u4e00\u79cd\u9488\u5bf9\u9aa8\u9abc\u808c\u518d\u751f\u5173\u952e\u6548\u5e94\u7269 AAK1 \u7684\u53e3\u670d\u5c0f\u5206\u5b50\u6291\u5236\u5242\u201d\u3002\u6d77\u62a5\u53ef\u5728 Satellos \u7f51\u7ad9\u7684\u201c\u6d3b\u52a8\u548c\u6f14\u793a\u201d\u9875\u9762\u4e0a\u627e\u5230\uff0c\u7f51\u5740\u4e3a ir.satellos.com\u3002<\/p>","protected":false},"excerpt":{"rendered":"<p>According to the announcement made by Satellos Bioscience Inc., in an experiment conducted on dogs with DMD, it was seen that dystrophin was produced at near normal levels in the subjects with the therapy called SAT-3247. This development gave hope to families going through stressful days with Duchenne disease. Satellos Bioscience Inc. (\u201cSatellos\u201d or the [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":1459,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[],"class_list":["post-1458","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research"],"subtitle":"","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/1458","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/comments?post=1458"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/posts\/1458\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media\/1459"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/media?parent=1458"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/categories?post=1458"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/zh\/wp-json\/wp\/v2\/tags?post=1458"}],"curies":[{"name":"\u53ef\u6e7f\u6027\u7c89\u5242","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}